                         SEQUENCE LISTING

<110>  APPLIED GENETIC TECHNOLOGIES CORPORATION
 
<120>  METHODS FOR THE TREATMENT OF ACHROMATOPSIA AND OTHER CNGB3 
       ASSOCIATED DISEASES

<130>  119561-02520

<140>  PCT/US2022/034781
<141>  2022-06-23

<150>  US 63/214,710
<151>  2021-06-24

<160>  100   

<170>  PatentIn version 3.5

<210>  1
<211>  2430
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic: hCNGB3co

<400>  1
atgttcaaga gcctgacaaa agtgaacaaa gtgaagccca tcggcgagaa caacgagaac       60

gagcagagca gccggcggaa cgaggaaggc agccacccca gcaaccagag ccagcagacc      120

accgcccagg aagagaacaa gggcgaggaa aagtccctga aaacaaagtc cacccccgtg      180

accagcgagg aaccccacac caacatccag gacaagctga gcaagaagaa cagcagcggc      240

gacctgacca ccaaccccga ccctcagaat gccgccgagc ctaccggcac cgtgcccgag      300

cagaaagaga tggaccccgg caaagagggc cccaacagcc cccagaacaa gccccctgcc      360

gcccctgtga tcaacgagta cgccgacgcc cagctgcaca acctggtcaa gcggatgcgg      420

cagcggaccg ccctgtacaa gaaaaagctg gtggaaggcg acctgagcag ccccgaggcc      480

agccctcaga cagccaagcc tacagccgtg ccccccgtga aagagagcga cgacaagccc      540

accgagcact actaccggct gctgtggttc aaagtgaaga agatgcccct gaccgagtac      600

ctgaagcgga tcaagctgcc caacagcatc gacagctaca ccgaccggct gtacctgctg      660

tggctgctgc tggtcaccct ggcctacaac tggaactgct ggttcatccc cctgcggctg      720

gtgttcccat accagaccgc cgacaacatc cactactggc tgatcgccga catcatctgc      780

gatatcatct acctgtacga catgctgttc atccagcccc ggctgcagtt cgtgcgggga      840

ggcgacatca tcgtggacag caacgagctg cggaagcact accggaccag ccccaagttc      900

cagctggacg tggccagcat catccccttc gacatctgct acctgttctt cggcttcaac      960

cccatgttcc gggccaaccg gatgctgaag tataccagct tcttcgagtt caaccaccac     1020

ctggaatcca tcatggacaa ggcctacatc tacagagtga tccggaccac cggctacctg     1080

ctgtttatcc tgcacatcaa cgcctgcgtg tactactggg ccagcaacta cgagggcatc     1140

ggcaccacca gatgggtgta cgacggcgag ggcaacgagt acctgcggtg ctactattgg     1200

gccgtgcgga ccctgatcac catcggcgga ctgcccgagc cccagaccct gttcgagatc     1260

gtgttccagc tgctgaactt cttcagcggc gtgttcgtgt tcagcagcct gatcggccag     1320

atgcgggacg tgatcggagc cgccaccgcc aaccagaact acttccgggc ctgcatggac     1380

gacacaatcg cctacatgaa caactacagc atccccaagc tggtgcagaa aagagtgcgg     1440

acttggtacg agtacacctg ggacagccag cggatgctgg acgagagcga cctgctgaaa     1500

accctgccca ccaccgtgca gctggccctg gccatcgacg tgaacttcag catcatcagc     1560

aaggtggacc tgttcaaggg ctgcgacacc cagatgatct acgatatgct gctgcggctg     1620

aagtccgtgc tgtatctgcc cggcgacttc gtgtgcaaga agggcgagat cggcaaagag     1680

atgtacatca tcaagcacgg cgaggtgcag gtcctgggcg gacccgatgg caccaaggtg     1740

ctcgtgacac tgaaggccgg cagcgtgttc ggcgagatca gcctgctggc cgctggcggc     1800

ggaaacagac ggacagccaa tgtggtggcc cacggcttcg ccaacctgct gaccctggac     1860

aaaaagaccc tgcaggaaat cctggtccac taccccgaca gcgagaggat cctcatgaag     1920

aaagcccggg tgctgctgaa gcagaaggcc aagaccgccg aggccacccc ccccagaaaa     1980

gacctggccc tgctgttccc cccaaaagag gaaaccccca agctgttcaa gaccctgctg     2040

ggcggcaccg gcaaggccag cctggccaga ctgctgaagc tgaaaagaga gcaggccgcc     2100

cagaagaaag agaacagcga gggcggcgag gaagagggca aagagaacga ggacaaacag     2160

aaagagaatg aagataagca gaaagaaaac gaggataagg gaaaagaaaa tgaggacaag     2220

gacaagggca gagagcccga agagaagccc ctggacagac ccgagtgcac cgccagccct     2280

atcgccgtgg aagaggaacc tcacagcgtg cggcggaccg tgctgcccag aggcacaagc     2340

cggcagagcc tgatcatcag catggcccct agcgccgagg gcggagaaga ggtgctgacc     2400

atcgaagtga aagaaaaggc caagcagtga                                      2430


<210>  2
<211>  1727
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic: PR1.7 (promoter)

<400>  2
ggaggctgag gggtggggaa agggcatggg tgtttcatga ggacagagct tccgtttcat       60

gcaatgaaaa gagtttggag acggatggtg gtgactggac tatacactta cacacggtag      120

cgatggtaca ctttgtatta tgtatatttt accacgatct ttttaaagtg tcaaaggcaa      180

atggccaaat ggttccttgt cctatagctg tagcagccat cggctgttag tgacaaagcc      240

cctgagtcaa gatgacagca gcccccataa ctcctaatcg gctctcccgc gtggagtcat      300

ttaggagtag tcgcattaga gacaagtcca acatctaatc ttccaccctg gccagggccc      360

cagctggcag cgagggtggg agactccggg cagagcagag ggcgctgaca ttggggcccg      420

gcctggcttg ggtccctctg gcctttcccc aggggccctc tttccttggg gctttcttgg      480

gccgccactg ctcccgctcc tctcccccca tcccaccccc tcaccccctc gttcttcata      540

tccttctcta gtgctccctc cactttcatc cacccttctg caagagtgtg ggaccacaaa      600

tgagttttca cctggcctgg ggacacacgt gcccccacag gtgctgagtg actttctagg      660

acagtaatct gctttaggct aaaatgggac ttgatcttct gttagcccta atcatcaatt      720

agcagagccg gtgaaggtgc agaacctacc gcctttccag gcctcctccc acctctgcca      780

cctccactct ccttcctggg atgtgggggc tggcacacgt gtggcccagg gcattggtgg      840

gattgcactg agctgggtca ttagcgtaat cctggacaag ggcagacagg gcgagcggag      900

ggccagctcc ggggctcagg caaggctggg ggcttccccc agacacccca ctcctcctct      960

gctggacccc cacttcatag ggcacttcgt gttctcaaag ggcttccaaa tagcatggtg     1020

gccttggatg cccagggaag cctcagagtt gcttatctcc ctctagacag aaggggaatc     1080

tcggtcaaga gggagaggtc gccctgttca aggccaccca gccagctcat ggcggtaatg     1140

ggacaaggct ggccagccat cccaccctca gaagggaccc ggtggggcag gtgatctcag     1200

aggaggctca cttctgggtc tcacattctt ggatccggtt ccaggcctcg gccctaaata     1260

gtctccctgg gctttcaaga gaaccacatg agaaaggagg attcgggctc tgagcagttt     1320

caccacccac cccccagtct gcaaatcctg acccgtgggt ccacctgccc caaaggcgga     1380

cgcaggacag tagaagggaa cagagaacac ataaacacag agagggccac agcggctccc     1440

acagtcaccg ccaccttcct ggcggggatg ggtggggcgt ctgagtttgg ttcccagcaa     1500

atccctctga gccgcccttg cgggctcgcc tcaggagcag gggagcaaga ggtgggagga     1560

ggaggtctaa gtcccaggcc caattaagag atcaggtagt gtagggtttg ggagctttta     1620

aggtgaagag gcccgggctg atcccacagg ccagtataaa gcgccgtgac cctcaggtga     1680

tgcgccaggg ccggctgccg tcggggacag ggctttccat agccatg                   1727


<210>  3
<211>  143
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic: TR

<400>  3
ttggccactc cctctctgcg cgctcgctcg ctcactgagg ccgggcgacc aaaggtcgcc       60

cgacgcccgg gctttgcccg ggcggcctca gtgagcgagc gagcgcgcag agagggagtg      120

gccaactcca tcactagggg ttc                                              143


<210>  4
<211>  143
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic: TR

<400>  4
aacccctagt gatggagttg gccactccct ctctgcgcgc tcgctcgctc actgaggccg       60

cccgggcaaa gcccgggcgt cgggcgacct ttggtcgccc ggcctcagtg agcgagcgag      120

cgcgcagaga gggagtggcc aac                                              143


<210>  5

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<400>  60
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<400>  63
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<210>  64

<400>  64
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<400>  65
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<400>  66
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<400>  68
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<210>  89

<400>  89
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<210>  90

<400>  90
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<400>  91
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<210>  92

<400>  92
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<210>  93

<400>  93
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<210>  94

<400>  94
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<210>  95

<400>  95
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<210>  96

<400>  96
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<210>  97

<400>  97
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<210>  98

<400>  98
000

<210>  99

<400>  99
000

<210>  100
<211>  4896
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic: TR-PR1.7-hCNGB3co-TR; rAAV2tYF-PR1.7-hCNGB3co

<400>  100
ttggccactc cctctctgcg cgctcgctcg ctcactgagg ccgggcgacc aaaggtcgcc       60

cgacgcccgg gctttgcccg ggcggcctca gtgagcgagc gagcgcgcag agagggagtg      120

gccaactcca tcactagggg ttcctcagat ctgaattcgg taccggaggc tgaggggtgg      180

ggaaagggca tgggtgtttc atgaggacag agcttccgtt tcatgcaatg aaaagagttt      240

ggagacggat ggtggtgact ggactataca cttacacacg gtagcgatgg tacactttgt      300

attatgtata ttttaccacg atctttttaa agtgtcaaag gcaaatggcc aaatggttcc      360

ttgtcctata gctgtagcag ccatcggctg ttagtgacaa agcccctgag tcaagatgac      420

agcagccccc ataactccta atcggctctc ccgcgtggag tcatttagga gtagtcgcat      480

tagagacaag tccaacatct aatcttccac cctggccagg gccccagctg gcagcgaggg      540

tgggagactc cgggcagagc agagggcgct gacattgggg cccggcctgg cttgggtccc      600

tctggccttt ccccaggggc cctctttcct tggggctttc ttgggccgcc actgctcccg      660

ctcctctccc cccatcccac cccctcaccc cctcgttctt catatccttc tctagtgctc      720

cctccacttt catccaccct tctgcaagag tgtgggacca caaatgagtt ttcacctggc      780

ctggggacac acgtgccccc acaggtgctg agtgactttc taggacagta atctgcttta      840

ggctaaaatg ggacttgatc ttctgttagc cctaatcatc aattagcaga gccggtgaag      900

gtgcagaacc taccgccttt ccaggcctcc tcccacctct gccacctcca ctctccttcc      960

tgggatgtgg gggctggcac acgtgtggcc cagggcattg gtgggattgc actgagctgg     1020

gtcattagcg taatcctgga caagggcaga cagggcgagc ggagggccag ctccggggct     1080

caggcaaggc tgggggcttc ccccagacac cccactcctc ctctgctgga cccccacttc     1140

atagggcact tcgtgttctc aaagggcttc caaatagcat ggtggccttg gatgcccagg     1200

gaagcctcag agttgcttat ctccctctag acagaagggg aatctcggtc aagagggaga     1260

ggtcgccctg ttcaaggcca cccagccagc tcatggcggt aatgggacaa ggctggccag     1320

ccatcccacc ctcagaaggg acccggtggg gcaggtgatc tcagaggagg ctcacttctg     1380

ggtctcacat tcttggatcc ggttccaggc ctcggcccta aatagtctcc ctgggctttc     1440

aagagaacca catgagaaag gaggattcgg gctctgagca gtttcaccac ccacccccca     1500

gtctgcaaat cctgacccgt gggtccacct gccccaaagg cggacgcagg acagtagaag     1560

ggaacagaga acacataaac acagagaggg ccacagcggc tcccacagtc accgccacct     1620

tcctggcggg gatgggtggg gcgtctgagt ttggttccca gcaaatccct ctgagccgcc     1680

cttgcgggct cgcctcagga gcaggggagc aagaggtggg aggaggaggt ctaagtccca     1740

ggcccaatta agagatcagg tagtgtaggg tttgggagct tttaaggtga agaggcccgg     1800

gctgatccca caggccagta taaagcgccg tgaccctcag gtgatgcgcc agggccggct     1860

gccgtcgggg acagggcttt ccatagccat gctagaggat ccggtactcg aggaactgaa     1920

aaaccagaaa gttaactggt aagtttagtc tttttgtctt ttatttcagg tcccggatcc     1980

ggtggtggtg caaatcaaag aactgctcct cagtggatgt tgcctttact tctaggcctg     2040

tacggaagtg ttacttctgc tctaaaagct gcggaattgt acccgcggcc gcatgttcaa     2100

gagcctgaca aaagtgaaca aagtgaagcc catcggcgag aacaacgaga acgagcagag     2160

cagccggcgg aacgaggaag gcagccaccc cagcaaccag agccagcaga ccaccgccca     2220

ggaagagaac aagggcgagg aaaagtccct gaaaacaaag tccacccccg tgaccagcga     2280

ggaaccccac accaacatcc aggacaagct gagcaagaag aacagcagcg gcgacctgac     2340

caccaacccc gaccctcaga atgccgccga gcctaccggc accgtgcccg agcagaaaga     2400

gatggacccc ggcaaagagg gccccaacag cccccagaac aagccccctg ccgcccctgt     2460

gatcaacgag tacgccgacg cccagctgca caacctggtc aagcggatgc ggcagcggac     2520

cgccctgtac aagaaaaagc tggtggaagg cgacctgagc agccccgagg ccagccctca     2580

gacagccaag cctacagccg tgccccccgt gaaagagagc gacgacaagc ccaccgagca     2640

ctactaccgg ctgctgtggt tcaaagtgaa gaagatgccc ctgaccgagt acctgaagcg     2700

gatcaagctg cccaacagca tcgacagcta caccgaccgg ctgtacctgc tgtggctgct     2760

gctggtcacc ctggcctaca actggaactg ctggttcatc cccctgcggc tggtgttccc     2820

ataccagacc gccgacaaca tccactactg gctgatcgcc gacatcatct gcgatatcat     2880

ctacctgtac gacatgctgt tcatccagcc ccggctgcag ttcgtgcggg gaggcgacat     2940

catcgtggac agcaacgagc tgcggaagca ctaccggacc agccccaagt tccagctgga     3000

cgtggccagc atcatcccct tcgacatctg ctacctgttc ttcggcttca accccatgtt     3060

ccgggccaac cggatgctga agtataccag cttcttcgag ttcaaccacc acctggaatc     3120

catcatggac aaggcctaca tctacagagt gatccggacc accggctacc tgctgtttat     3180

cctgcacatc aacgcctgcg tgtactactg ggccagcaac tacgagggca tcggcaccac     3240

cagatgggtg tacgacggcg agggcaacga gtacctgcgg tgctactatt gggccgtgcg     3300

gaccctgatc accatcggcg gactgcccga gccccagacc ctgttcgaga tcgtgttcca     3360

gctgctgaac ttcttcagcg gcgtgttcgt gttcagcagc ctgatcggcc agatgcggga     3420

cgtgatcgga gccgccaccg ccaaccagaa ctacttccgg gcctgcatgg acgacacaat     3480

cgcctacatg aacaactaca gcatccccaa gctggtgcag aaaagagtgc ggacttggta     3540

cgagtacacc tgggacagcc agcggatgct ggacgagagc gacctgctga aaaccctgcc     3600

caccaccgtg cagctggccc tggccatcga cgtgaacttc agcatcatca gcaaggtgga     3660

cctgttcaag ggctgcgaca cccagatgat ctacgatatg ctgctgcggc tgaagtccgt     3720

gctgtatctg cccggcgact tcgtgtgcaa gaagggcgag atcggcaaag agatgtacat     3780

catcaagcac ggcgaggtgc aggtcctggg cggacccgat ggcaccaagg tgctcgtgac     3840

actgaaggcc ggcagcgtgt tcggcgagat cagcctgctg gccgctggcg gcggaaacag     3900

acggacagcc aatgtggtgg cccacggctt cgccaacctg ctgaccctgg acaaaaagac     3960

cctgcaggaa atcctggtcc actaccccga cagcgagagg atcctcatga agaaagcccg     4020

ggtgctgctg aagcagaagg ccaagaccgc cgaggccacc ccccccagaa aagacctggc     4080

cctgctgttc cccccaaaag aggaaacccc caagctgttc aagaccctgc tgggcggcac     4140

cggcaaggcc agcctggcca gactgctgaa gctgaaaaga gagcaggccg cccagaagaa     4200

agagaacagc gagggcggcg aggaagaggg caaagagaac gaggacaaac agaaagagaa     4260

tgaagataag cagaaagaaa acgaggataa gggaaaagaa aatgaggaca aggacaaggg     4320

cagagagccc gaagagaagc ccctggacag acccgagtgc accgccagcc ctatcgccgt     4380

ggaagaggaa cctcacagcg tgcggcggac cgtgctgccc agaggcacaa gccggcagag     4440

cctgatcatc agcatggccc ctagcgccga gggcggagaa gaggtgctga ccatcgaagt     4500

gaaagaaaag gccaagcagt gagcggccgc gcggatccag acatgataag atacattgat     4560

gagtttggac aaaccacaac tagaatgcag tgaaaaaaat gctttatttg tgaaatttgt     4620

gatgctattg ctttatttgt aaccattata agctgcaata aacaagttaa caacaacaat     4680

tgcattcatt ttatgtttca ggttcagggg gaggtgtggg aggtttttta gtcgactggg     4740

gagagatctg aggaacccct agtgatggag ttggccactc cctctctgcg cgctcgctcg     4800

ctcactgagg ccgcccgggc aaagcccggg cgtcgggcga cctttggtcg cccggcctca     4860

gtgagcgagc gagcgcgcag agagggagtg gccaac                               4896


