                         SEQUENCE LISTING

<110>  THE UNITED STATES OF AMERICA, AS REPRESENTED BY THE 
       SECRETARY, DEPARTMENT OF HEALTH AND HUMAN SERVICES
       Gudmundsdottir, Bjorg
       Tisdale, John Fitzgerald
       Tumburu, Laxminath
 
<120>  COMPOSITIONS AND METHODS FOR TREATING SICKLE CELL DISEASES

<130>  3000093-006977

<160>  5     

<170>  PatentIn version 3.5

<210>  1
<211>  3574
<212>  DNA
<213>  Homo sapiens

<400>  1
agttccggac gcggccgccg ccgtcgccgc catctgtcac ctccactccg gcatcagcag       60

ccagtcgccc gtgtcccgcc tgtctcctcg gcggagcctg ctgcccgtcc tgccacctct      120

ctgctctgtt cttgtctctg ccttcattcc cgaatggatc tggtaggagt ggcatcgcct      180

gagcccggga cggcagcggc ctggggaccc agcaagtgtc catgggctat tcctcaaaat      240

acaatatctt gttctttggc tgatgtaatg agtgaacagc tggccaaaga attgcagtta      300

gaagaagaag ctgccgtttt tcctgaagtt gctgttgctg aaggaccatt tattactgga      360

gaaaacattg atacttccag tgaccttatg ctggctcaga tgctacagat ggaatatgac      420

agagaatatg atgcacagct taggcgtgaa gaaaaaaaat tcaatggaga tagcaaagtt      480

tccatttcct ttgaaaatta tcgaaaagtg catccttatg aagacagcga tagctctgaa      540

gatgaggttg actggcagga tactcgtgat gatccctaca gaccagcaaa accggttccc      600

actcctaaaa agggctttat tggaaaagga aaagatatca ccaccaaaca tgatgaagta      660

gtatgtggga gaaagaacac agcaagaatg gaaaattttg cacctgagtt tcaggtagga      720

gatggaattg gaatggattt aaaactatca aaccatgttt tcaatgcttt aaaacaacat      780

gcctactcag aagaacgtcg aagtgcccgc ctacatgaga aaaaggagca ttctacagca      840

gaaaaagcag ttgatcctaa gacacgttta cttatgtata aaatggtcaa ctctggaatg      900

ttggagacaa tcactggctg tattagtaca ggaaaggagt ctgttgtctt tcatgcatat      960

ggagggagca tggaggatga aaaggaagat agtaaagtta tacctacaga atgtgccatc     1020

aaggtattta aaacaaccct taatgaattt aagaatcgtg acaaatatat taaagatgat     1080

ttcaggttta aagatcgctt cagtaaacta aatccacgta agatcatccg catgtgggca     1140

gaaaaagaaa tgcacaatct cgcaagaatg cagagagctg gaattccttg tccaacagtt     1200

gtactactga agaaacacat tttagttatg tcttttattg gccatgatca agttccagcc     1260

cctaaattaa aagaagtaaa gctcaatagt gaagaaatga aagaagccta ctatcaaact     1320

cttcatttga tgcggcagtt atatcatgaa tgtacgcttg tccatgctga cctcagtgag     1380

tataacatgc tgtggcatgc tggaaaggtc tggttgatcg atgtcagtca gtcagtagaa     1440

cctacccacc ctcacggcct ggagttcttg ttccgggact gcaggaatgt ctcgcagttt     1500

ttccagaaag gaggagtcaa ggaagccctt agtgaacgag aactcttcaa tgctgtttca     1560

ggcttaaaca tcacagcaga taatgaagct gattttttag ctgagataga agctttggag     1620

aaaatgaatg aagatcacgt tcagaagaat ggaaggaaag ctgcttcatt tttgaaagat     1680

gatggagacc caccactact atatgatgaa tagcactaat acccactgct tcagtgttaa     1740

cacagcagtg attgtcagct gccaatagca aatgaagtta tgggtgactt gaaataccaa     1800

aacctgagga gtgggcaatg gtgcttctgt gcttttcccc cttgtaaccc atgtgccaga     1860

tgtgtggaat ttttagctca gcattgagag aataaaatgt cactacctct catcttatga     1920

acaggataat ataattcttt aacagctata ggttatctgg ctgaagtaga cctaatttta     1980

tgtgacttgt ggtgtaaaat gtcttgatga taatttttaa aacttgggta acacttccaa     2040

atatgggagg aaaggacaga tgtgtttaca agggaggatt ttacaacata cttgctttat     2100

tcacctccct gttttgtgtt gcgtctttcc ttgaatattt tattggccca gagttagcct     2160

ttctcaatta tgtttccaga ctgtggccgt gattctaaag gaaaatgtgt gctctttagt     2220

gggtagaaca aatggaaatt tggtttcaga atggctgaca gaaatcgaca taagtcatgt     2280

aatttttgtt gatatatcat gaaaatgaac agaattcttt ttccatactt atatctaaga     2340

aaaggcatca taggtttctg aaagagataa ctatataaca gctttttaac tatccagtca     2400

actttcagct tttctacatt taggtaaaat ggttaggata taactcatgg tgtggctaat     2460

ctacatttat caataaaatg taaattatct gaaaggacag aatataagat ttaaccatgt     2520

ttgacgtatt ttaatttagt taatgaagca aaattcagtt tatatttcac tagaactgtg     2580

tacttgattg attttcagag aaatatcaca aattagaaat attaaatcta aggatgaaag     2640

gtatatataa aacaatttgg gggccaggca cgatggctca aacctgtaat cccagcactt     2700

tgggagacca aggcgggtgg atcacttgag gtcaggagtt caagaccagc ctgggcaaca     2760

tggcgaaacc ctgtctctac taaaaataca aaaattagcc gggtgtggtg gcacttctct     2820

gtaatctcag cttctcagga ggctgagaca ggagaatcgc ttgaacccgg gaggcagagg     2880

ttgcagtgag ctgagatcat gccactgcac tccggcctag gtgacagagg gaaactccat     2940

ctccaggaaa aaaaaaaaaa aacccaattt ggataccaaa ttaatcaact aatttgagct     3000

atctggcctt actcttagta gtttttagta cgtgctggac accactttta aaaagcaatc     3060

actgtgctag aaaagtatat tggctttgtt aggattaaag ttcattaact tcaatgtaat     3120

catgcctcct attactgaag tcagattgga accactaaag atccaaactt tctgtctggt     3180

aatagaaagt aaaaatctag acatcattta catttgagaa agctgttttt aacattattt     3240

taaaatgcca aatatgttct ttctagaaaa atatttattt ttgtttttgt tggatagctt     3300

ttaattacat ttcagagagg tgtaattttg ggtagatgct cattacattt ttgaaaggtt     3360

tatgattcca aaataaagat ttatatgact ggtgatactg gctttacaga aatttcagag     3420

aactaatttt taaaatcttt agcatttaaa actttttttg ttttgttttc tgacatattc     3480

tgacaaagag cagcaaacca ctgctgtgtg gcattcttgg agtgtgctgt gaatgtgctt     3540

tttaagaaat taaaaagaga tcattttaaa attg                                 3574


<210>  2
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic oligonucleotide

<400>  2
gctcagcatt gagagaataa a                                                 21


<210>  3
<211>  58
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA forward sequence

<400>  3
ccgggctcag cattgagaga ataaactcga gtttattctc tcaatgctga gctttttg         58


<210>  4
<211>  58
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA reverse sequence

<400>  4
aattcaaaaa gctcagcatt gagagaataa actcgagttt attctctcaa tgctgagc         58


<210>  5
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic oligonucleotide reverse sequence

<400>  5
tttattctct caatgctgag c                                                 21


