                         SEQUENCE LISTING

<110>  Research Institute at Nationwide Childrens Hospital
       The Trustees of Columbia University in the City of New York
 
<120>  PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DYNAMIN-1 
       VARIANTS

<130>  28335/56694/PC

<150>  US 17/231,963
<151>  2021-04-15

<160>  61    

<170>  PatentIn version 3.5

<210>  1
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1a-1 Full-length mouse miRNA sequence

<400>  1
ctcgagtgag cgatgtgtgg acatggtagt cagtctgtaa agccacagat gggactgact       60

accatgtcca cacactgcct actaga                                            86


<210>  2
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1a-4 Full-length mouse miRNA sequence

<400>  2
ctcgagtgag cgaaccatca gaaagtgtag tgaactgtaa agccacagat gggttcacta       60

cactttctga tggtgtgcct actaga                                            86


<210>  3
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  Humanized miDNM1-10a-4 Full-length human miRNA sequence

<400>  3
ctcgagtgag cgaaccatca gaaagtgtag cgaactgtaa agccacagat gggttcgcta       60

cactttctga tggtgtgcct actaga                                            86


<210>  4
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-71 Full-length human miRNA sequence

<400>  4
ctcgagtgag cgaccagtat caagtgtgtg gatactgtaa agccacagat gggtatccac       60

acacttgata ctgggtgcct actaga                                            86


<210>  5
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-72 Full-length human miRNA sequence

<400>  5
ctcgagtgag cgacagtatc aagtgtgtgg atatctgtaa agccacagat gggatatcca       60

cacacttgat actggtgcct actaga                                            86


<210>  6
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-104 Full-length human miRNA sequence

<400>  6
ctcgagtgag cgaagctcac agccaccatc agaactgtaa agccacagat gggttctgat       60

ggtggctgtg agctctgcct actaga                                            86


<210>  7
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-106 Full-length human miRNA sequence

<400>  7
ctcgagtgag cgactcacag ccaccatcag aaagctgtaa agccacagat gggctttctg       60

atggtggctg tgagctgcct actaga                                            86


<210>  8
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-3 Full-length human miRNA sequence

<400>  8
ctcgagtgag cgaggggctg tttaccccag acatctgtaa agccacagat gggatgtctg       60

gggtaaacag ccccgtgcct actaga                                            86


<210>  9
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-24 Full-length human miRNA sequence

<400>  9
ctcgagtgag cgcggccttt gagaccattg tgaactgtaa agccacagat gggttcacaa       60

tggtctcaaa ggccatgcct actaga                                            86


<210>  10
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-25 Full-length human miRNA sequence

<400>  10
ctcgagtgag cgagcctttg agaccattgt gaaactgtaa agccacagat gggtttcaca       60

atggtctcaa aggcctgcct actaga                                            86


<210>  11
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-49 Full-length human miRNA sequence

<400>  11
ctcgagtgag cgacaggtga agaagatccg agaactgtaa agccacagat gggttctcgg       60

atcttcttca cctgctgcct actaga                                            86


<210>  12
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-72 Full-length human miRNA sequence

<400>  12
ctcgagtgag cgagtgtctc aagtgtgtgg acatctgtaa agccacagat gggatgtcca       60

cacacttgag acacgtgcct actaga                                            86


<210>  13
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-101 Full-length human miRNA sequence

<400>  13
ctcgagtgag cgccggagct aatcagcacc gttactgtaa agccacagat gggtaacggt       60

gctgattagc tccgatgcct actaga                                            86


<210>  14
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-102 Full-length human miRNA sequence

<400>  14
ctcgagtgag cgaggagcta atcagcaccg ttagctgtaa agccacagat gggctaacgg       60

tgctgattag ctccgtgcct actaga                                            86


<210>  15
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-103 Full-length human miRNA sequence

<400>  15
ctcgagtgag cgagagctaa tcagcaccgt tagactgtaa agccacagat gggtctaacg       60

gtgctgatta gctcctgcct actaga                                            86


<210>  16
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-116 Full-length human miRNA sequence

<400>  16
ctcgagtgag cgcccgttag acagtgcacc aagactgtaa agccacagat gggtcttggt       60

gcactgtcta acggttgcct actaga                                            86


<210>  17
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-117 Full-length human miRNA sequence

<400>  17
ctcgagtgag cgacgttaga cagtgcacca agaactgtaa agccacagat gggttcttgg       60

tgcactgtct aacggtgcct actaga                                            86


<210>  18
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1a-1 Full-length mouse miRNA sequence

<400>  18
cucgagugag cgaugugugg acaugguagu cagucuguaa agccacagau gggacugacu       60

accaugucca cacacugccu acuaga                                            86


<210>  19
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1a-4 Full-length mouse miRNA sequence

<400>  19
cucgagugag cgaaccauca gaaaguguag ugaacuguaa agccacagau ggguucacua       60

cacuuucuga uggugugccu acuaga                                            86


<210>  20
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  Humanized miDNM1-10a-4 Full-length human miRNA sequence

<400>  20
cucgagugag cgaaccauca gaaaguguag cgaacuguaa agccacagau ggguucgcua       60

cacuuucuga uggugugccu acuaga                                            86


<210>  21
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-71 Full-length human miRNA sequence

<400>  21
cucgagugag cgaccaguau caagugugug gauacuguaa agccacagau ggguauccac       60

acacuugaua cugggugccu acuaga                                            86


<210>  22
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-72 Full-length human miRNA sequence

<400>  22
cucgagugag cgacaguauc aagugugugg auaucuguaa agccacagau gggauaucca       60

cacacuugau acuggugccu acuaga                                            86


<210>  23
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-104 Full-length human miRNA sequence

<400>  23
cucgagugag cgaagcucac agccaccauc agaacuguaa agccacagau ggguucugau       60

gguggcugug agcucugccu acuaga                                            86


<210>  24
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-106 Full-length human miRNA sequence

<400>  24
cucgagugag cgacucacag ccaccaucag aaagcuguaa agccacagau gggcuuucug       60

augguggcug ugagcugccu acuaga                                            86


<210>  25
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-3 Full-length human miRNA sequence

<400>  25
cucgagugag cgaggggcug uuuaccccag acaucuguaa agccacagau gggaugucug       60

ggguaaacag ccccgugccu acuaga                                            86


<210>  26
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-24 Full-length human miRNA sequence

<400>  26
cucgagugag cgcggccuuu gagaccauug ugaacuguaa agccacagau ggguucacaa       60

uggucucaaa ggccaugccu acuaga                                            86


<210>  27
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-25 Full-length human miRNA sequence

<400>  27
cucgagugag cgagccuuug agaccauugu gaaacuguaa agccacagau ggguuucaca       60

auggucucaa aggccugccu acuaga                                            86


<210>  28
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-49 Full-length human miRNA sequence

<400>  28
cucgagugag cgacagguga agaagauccg agaacuguaa agccacagau ggguucucgg       60

aucuucuuca ccugcugccu acuaga                                            86


<210>  29
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-72 Full-length human miRNA sequence

<400>  29
cucgagugag cgagugucuc aagugugugg acaucuguaa agccacagau gggaugucca       60

cacacuugag acacgugccu acuaga                                            86


<210>  30
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-101 Full-length human miRNA sequence

<400>  30
cucgagugag cgccggagcu aaucagcacc guuacuguaa agccacagau ggguaacggu       60

gcugauuagc uccgaugccu acuaga                                            86


<210>  31
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-102 Full-length human miRNA sequence

<400>  31
cucgagugag cgaggagcua aucagcaccg uuagcuguaa agccacagau gggcuaacgg       60

ugcugauuag cuccgugccu acuaga                                            86


<210>  32
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-103 Full-length human miRNA sequence

<400>  32
cucgagugag cgagagcuaa ucagcaccgu uagacuguaa agccacagau gggucuaacg       60

gugcugauua gcuccugccu acuaga                                            86


<210>  33
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-116 Full-length human miRNA sequence

<400>  33
cucgagugag cgcccguuag acagugcacc aagacuguaa agccacagau gggucuuggu       60

gcacugucua acgguugccu acuaga                                            86


<210>  34
<211>  86
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-117 Full-length human miRNA sequence

<400>  34
cucgagugag cgacguuaga cagugcacca agaacuguaa agccacagau ggguucuugg       60

ugcacugucu aacggugccu acuaga                                            86


<210>  35
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1a-1 Mature antisense sequence

<400>  35
acugacuacc auguccacac ac                                                22


<210>  36
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1a-4 Mature antisense sequence

<400>  36
uucacuacac uuucugaugg ug                                                22


<210>  37
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  Humanized miDNM1-10a-4 Mature antisense sequence

<400>  37
uucgcuacac uuucugaugg ug                                                22


<210>  38
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-71 Mature antisense sequence

<400>  38
uauccacaca cuugauacug gg                                                22


<210>  39
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-72 Mature antisense sequence

<400>  39
auauccacac acuugauacu gg                                                22


<210>  40
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-104 Mature antisense sequence

<400>  40
uucugauggu ggcugugagc uc                                                22


<210>  41
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10a-106 Mature antisense sequence

<400>  41
cuuucugaug guggcuguga gc                                                22


<210>  42
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-3 Mature antisense sequence

<400>  42
augucugggg uaaacagccc cg                                                22


<210>  43
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-24 Mature antisense sequence

<400>  43
uucacaaugg ucucaaaggc ca                                                22


<210>  44
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-25 Mature antisense sequence

<400>  44
uuucacaaug gucucaaagg cc                                                22


<210>  45
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-49 Mature antisense sequence

<400>  45
uucucggauc uucuucaccu gc                                                22


<210>  46
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-72 Mature antisense sequence

<400>  46
auguccacac acuugagaca cg                                                22


<210>  47
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-101 Mature antisense sequence

<400>  47
uaacggugcu gauuagcucc ga                                                22


<210>  48
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-102 Mature antisense sequence

<400>  48
cuaacggugc ugauuagcuc cg                                                22


<210>  49
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-103 Mature antisense sequence

<400>  49
ucuaacggug cugauuagcu cc                                                22


<210>  50
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-116 Mature antisense sequence

<400>  50
ucuuggugca cugucuaacg gu                                                22


<210>  51
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  synthetic


<220>
<221>  misc_feature
<223>  miDNM1-10b-117 Mature antisense sequence

<400>  51
uucuuggugc acugucuaac gg                                                22


<210>  52
<211>  139
<212>  DNA
<213>  Homo sapiens

<400>  52
gacgggcctc ttcacacctg acctcgcttt tgaagccaca gtgaaaaagc aggtgcagaa       60

gctcaaagag cccagtatca agtgtgtgga tatggtagtc agtgagctca cagccaccat      120

cagaaagtgt agcgaaaag                                                   139


<210>  53
<211>  139
<212>  DNA
<213>  Homo sapiens

<400>  53
aacggggctg tttaccccag acatggcctt tgagaccatt gtgaaaaagc aggtgaagaa       60

gatccgagaa ccgtgtctca agtgtgtgga catggttatc tcggagctaa tcagcaccgt      120

tagacagtgc accaagaag                                                   139


<210>  54
<211>  138
<212>  DNA
<213>  Mus musculus

<400>  54
gacgggcctc ttcacacctg acctcgcttt tgaagccaca gtgaaaaagc aggtgcagaa       60

gctcaaagag cccagtatca agtgtgtgga catggtagtc agtgaactca cgtccaccat      120

cagaaagtgt agtgaaaa                                                    138


<210>  55
<211>  139
<212>  DNA
<213>  Mus musculus

<400>  55
aacggggctc tttaccccag acatggcctt tgaaaccatt gtgaaaaagc aggtgaagaa       60

gattcgagag ccgtgtctca agtgtgtgga catggttatc tcggagctaa tcagcacggt      120

tagacagtgc accaagaag                                                   139


<210>  56
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic

<400>  56
ctcgcttttg aagccacagt                                                   20


<210>  57
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic

<400>  57
gagtgcaggt ggtagtcttt                                                   20


<210>  58
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic

<400>  58
ggcctttgaa accattgtga                                                   20


<210>  59
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic

<400>  59
agtcgtgcca atctgtcacg                                                   20


<210>  60
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic

<400>  60
cctctctgtc cacttgtagc catt                                              24


<210>  61
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic

<400>  61
tccaagatca ctcgtagtgg gtca                                              24


