                         SEQUENCE LISTING

<110>  The Trustees of Columbia University in the City of New York
 
<120>  RESCUE STRATEGIES FOR BEST1 LOSS- AND GAIN-OF-FUNCTION MUTATIONS

<130>  COLUM-40036.601

<150>  US 63/174,090
<151>  2021-04-13

<160>  9     

<170>  PatentIn version 3.5

<210>  1
<211>  20
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  1
ctcacccagc acgaaggaaa                                                   20


<210>  2
<211>  20
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  2
ccatggtggc gcatccgtac                                                   20


<210>  3
<211>  20
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  3
gctggcctgc gcggtcccac                                                   20


<210>  4
<211>  20
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  4
tccttggtga cccacttaca                                                   20


<210>  5
<211>  20
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  5
tctggagcag gatagggtcc                                                   20


<210>  6
<211>  20
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  6
tgtatacaca ggtgaggact                                                   20


<210>  7
<211>  20
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  7
gcaggctctg gagcaggata                                                   20


<210>  8
<211>  120
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  8
gccctgggtg tggtttgcca acctgtcaat gaaggcgtgg cttggaggtc gaattcggga       60

ccctaccctg ctccagagcc tgctgaacgt gagcccactg tacagacagg gctgccgcag      120


<210>  9
<211>  120
<212>  DNA
<213>  artificial sequence

<220>
<223>  Synthetic

<400>  9
tcagtgtgga cacctgtatg cctacgactg gattagtatc ccactggtgt gtacacaggt       60

gaggactagt ctggtgaggc tgcccttttg ggaaactgag gctagaagga ccaaggaagc      120


