                               SEQUENCE LISTING

<110> NOVARTIS AG

<120> THE USE OF A SPLICING MODULATOR FOR A TREATMENT SLOWING 
      PROGRESSION OF HUNTINGTON'S DISEASE

<130> PAT059073-WO-PCT

<140>
<141>

<150> 63/263149
<151> 2021-10-27

<150> 63/250109
<151> 2021-09-29

<150> 63/233538
<151> 2021-08-16

<150> 63/167285
<151> 2021-03-29

<160> 26    

<170> PatentIn version 3.5

<210> 1
<211> 20
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 1
gtcatttgca ccttcctcct                                                   20


<210> 2
<211> 20
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 2
tggatcaaat gccaggacag                                                   20


<210> 3
<211> 23
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 3
tcctgagaaa gagaaggaca ttg                                               23


<210> 4
<211> 21
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 4
ctgtgggctc ctgtagaaat c                                                 21


<210> 5
<211> 18
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 5
gcccgtagtg cttcagtt                                                     18


<210> 6
<211> 21
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 6
gatttggcta caaaaacagc a                                                 21


<210> 7
<211> 15
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      probe"

<400> 7
tggcaaccct tgaga                                                        15


<210> 8
<211> 15
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      probe"

<400> 8
tcgtggtggc aaccc                                                        15


<210> 9
<211> 439
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      polynucleotide"

<400> 9
gggatgctgc actgtatcag tccctgccca ctctggcccg ggccctggca cagtacctgg       60

tggtggtctc caaactgccc agtcatttgc accttcctcc tgagaaagag aaggacattg      120

tgaaattcgt ggtggcaacc cttgagaggc aagccctggt gctgtgggag ccccaaggaa      180

gagcctctgg cctggtggcc acgtagccca ggagagattt ctacaggagc ccacagcgct      240

gaaggagaga gaggcagcag agccctgtcc tggcatttga tccatgagca gatcccgctg      300

agtctggatc tccaggcagg gctggactgc tgctgcctgg ccctgcagct gcctggcctc      360

tggagcgtgg tctcctccac agagtttgtg acccacgcct gctccctcat ctactgtgtg      420

cacttcatcc tggaggccg                                                   439


<210> 10
<211> 22
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 10
gagactcatc cagtaccatc ag                                                22


<210> 11
<211> 22
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 11
gatgtcagct atctgtcgag ac                                                22


<210> 12
<211> 19
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      probe"

<400> 12
ttgtcttcat tctccttgt                                                    19


<210> 13
<211> 24
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 13
gtagaacttc agaccctaat cctg                                              24


<210> 14
<211> 19
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 14
caccactctg gcttcacaa                                                    19


<210> 15
<211> 15
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      probe"

<400> 15
gagtcagtga ttgtt                                                        15


<210> 16
<211> 24
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 16
tcactgaaga gtaccagaaa agtc                                              24


<210> 17
<211> 21
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      primer"

<400> 17
ttttattccc cagcactctc g                                                 21


<210> 18
<211> 17
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      probe"

<400> 18
atacgtggtt ggagagc                                                      17


<210> 19
<211> 20
<212> DNA
<213> Artificial Sequence

<220>
<221> source
<223> /note="Description of Artificial Sequence: Synthetic
      probe"

<400> 19
caaggacttc atgatccagg                                                   20


<210> 20
<211> 105
<212> DNA
<213> Homo sapiens


<220>
<221> misc_feature
<222> (1)..(105) 
<223> /note="This sequence may encompass 6-35 'cag' repeating units"

<400> 20
cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca gcagcagcag       60

cagcagcagc agcagcagca gcagcagcag cagcagcagc agcag                      105


<210> 21
<211> 117
<212> DNA
<213> Homo sapiens


<220>
<221> misc_feature
<222> (1)..(117) 
<223> /note="This sequence may encompass 36-39 'cga' repeating units"

<400> 21
cgacgacgac gacgacgacg acgacgacga cgacgacgac gacgacgacg acgacgacga       60

cgacgacgac gacgacgacg acgacgacga cgacgacgac gacgacgacg acgacga         117


<210> 22
<211> 120
<212> DNA
<213> Homo sapiens


<220> 
<221> source
<223> /note="See specification as filed for detailed description of
      substitutions and preferred embodiments"

<400> 22
cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca gcagcagcag       60

cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca gcagcagcag      120


<210> 23
<211> 108
<212> DNA
<213> Homo sapiens


<220> 
<221> source
<223> /note="See specification as filed for detailed description of
      substitutions and preferred embodiments"

<400> 23
cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca gcagcagcag       60

cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcag                   108




<210> 24
<211> 291
<212> DNA
<213> Homo sapiens

<400> 24
cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca gcagcagcag       60

cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca gcagcagcag      120

cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca gcagcagcag      180

cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca gcagcagcag      240

cagcagcagc agcagcagca gcagcagcag cagcagcagc agcagcagca g               291
