﻿SEQUENCE LISTING

<110>  Charite Universitätsmedizin Berlin; Max-Delbrück-Centrum
für Molekulare Medizin

<120>  Method for gene repair in primary human muscle stem cells
(satellite cells) in viitro and genetically repaired human muscle
stem cells

<130>  CHT111WO

<140>  PCT/EP2022/052214
<141>  2022-03-28

<160>  6

<170>  PatentIn version 3.5

<210>  1
<211>  20
<212>  DNA
<213>  Homo sapiens


<220>
<221>  sgRNA_SGCAex2mut
<222>  (1)..(20)

<400>  1
atgtcagtga gcggcctgac                                                   20


<210>  2
<211>  20
<212>  DNA
<213>  Homo sapiens


<220>
<221>  sgRNA_CBE_1
<222>  (1)..(20)

<400>  2
gacttgtcgc gcagccggac                                                   20


<210>  3
<211>  21
<212>  DNA
<213>  Homo sapiens


<220>
<221>  sgRNA_CBE_1+G
<222>  (1)..(21)

<400>  3
ggacttgtcg cgcagccgga c                                                 21


<210>  4
<211>  20
<212>  DNA
<213>  Homo sapiens


<220>
<221>  sgRNA_CBE_2
<222>  (1)..(20)

<400>  4
ggacttgtcg cgcagccgga                                                   20


<210>  5
<211>  20
<212>  DNA
<213>  Homo sapiens


<220>
<221>  sgRNA_DYSFex44
<222>  (1)..(20)

<400>  5
aaataggggt ccagcgtgca                                                   20


<210>  6
<211>  20
<212>  DNA
<213>  Homo sapiens


<220>
<221>  sgRNA_NCAM1ex7
<222>  (1)..(20)

<400>  6
ccctaccaaa gactttgagg                                                   20


