                         SEQUENCE LISTING

<110>  Svaren, John
 
<120>  REGULATORY ELEMENTS FOR SCHWANN CELL-SPECIFIC GENE EXPRESSION

<130>  09824.283

<140>  xx/yyy,zzz
<141>  2021-12-22

<150>  63/129,080
<151>  2020-12-22

<160>  20    

<170>  PatentIn version 3.5

<210>  1
<211>  769
<212>  DNA
<213>  mouse

<400>  1
agcaaagatt gacgatatca taggaggaat agaaatccaa agaaataagt aaccctctgt       60

gttacactgg ggattcccaa gaaggctctc agacagaatt cccaggaggt aagtaaaaga      120

tatggcatgc taagatggga gattcgggac aatgaggggg gagtgggtgt ggtatgagcc      180

cccaacattg gctagacaat gggattttgt ttggttgcct cctcctaaag aacagaaaag      240

tctataattg ttcctaccca gagccacccc acccacatag actgcctggg atgactctcc      300

atgggtgggg ggcttagagg ggtggcactg ggccaagatg accaagaaga gggtgaggat      360

ggatggtcgg accacagagg tccacatgca gaggcacctg ggtgctggac tcggcatctt      420

tcctatatct agctttcctt gacaatgagt ccttcctccc ctagatcccc agtcatggta      480

acctagggta gggggaggtc agtatacaca aagccctctg tgtaaggggt ggtatgtgtc      540

cccccacccc tccacccagc gtatacaatg ccccttctgc tccatgcccc ctgccaccct      600

ccccaccacc tctccattgc acatgccagg ctgcaattgg tcactggctc aggacagccc      660

cctcatgctg gggatccagg ggattttaag caggttccag aaaacacagc tcagttcctt      720

gtcccccgct ctctccaccc cacagacact ctgggccttt gccctaccc                  769


<210>  2
<211>  177
<212>  DNA
<213>  Homo sapiens

<400>  2
ccccgaggga acaggactct tttgtaccgg ggaccagctt ctggtgaggg tgcggacacc       60

aggggccgtc tgtggggtgg gagagggcgg caggaattca cgcggcatgt cgggaatgct      120

gatactgtga aacccagtca ttgatggctc tgggtccctg cccgccaccc ccaggcc         177


<210>  3
<211>  379
<212>  DNA
<213>  mouse

<400>  3
cctaggaggt ctctaggatg gggcacccac acccccaaag gaacagggct cttttgtatt       60

ggctactggc ctctggtgag ggtggggaca ccctgagcct gctgcgggtg ggagagggcg      120

gcaggaattc acacggcatg ctgggaatgc tgatgttgtg aaacccagtc attgatgggg      180

ctgggtcctt gcctgcctgc cacccccagg cctcatctgc tcatggactc accactttct      240

gttcccctca tcttagagct accattccct tccttcccca tggcactccc acgccccagc      300

tggggcgtgg ggtgttgtgg tggtacagta tctttgaagc tgtgtgggag catcctgggt      360

atccacgggt tctagctcg                                                   379


<210>  4
<211>  174
<212>  DNA
<213>  rat

<400>  4
ccagcagggg ctaacactag ctgacacgga gctgacacca tggggtgctc ccttgatggt       60

ggattgtgga actgaaagac agcattgtgt ggggcccgat tgctattctc tgccagacat      120

ttgacaccat tgtccctgtg gtatccaggc acagtaagtg ctgcacacag atct            174


<210>  5
<211>  1092
<212>  DNA
<213>  Homo sapiens

<400>  5
gtacctagcc ccgcctctac attctctggg tctccaggcc ctggaaggag ccccctcccc       60

ctgggctctc ctggcagcca ggctcagacc caggcctgtc agccctctgg gcagttgacg      120

tgggagcaga attcggggaa tccctcgggg cgtgggcagg catgagtggg ctctgccagc      180

gctggcccct tcgtcccggg cctcactgac ccttcctccc gctgacctca cccggcctgg      240

ccctcgggga gaatgggcca gtgtgctccg tgcggggccg tgccaagcag cccccaacaa      300

aggagccttt ggtgcgcccg gcgtgggatg ccagcctgcg gcagggtggg ggtgggccgc      360

tccagtgccc tctctgtgcc gtggccccag cctcttgctc agccacactg cctgcctggt      420

gcagcccatg tgacgggtcg agctccgggc cctgctgtcc ctggccgggc tatcccagtg      480

gcttcaggca ccttctccag acctacccag aaagatgccc ggatggatcc tgcagctccg      540

tggcttttct gggaagcagc ggcccctgct ctcaagagac cctggctcct gatggtggcc      600

ccaaggttgc cagctggtgc tagggactca ggacagtttc ccagaaaagg ccaagcgggc      660

agcccctcca ggggccgggt gaggaagctg gggggtgcgg aggccacact gggtccctga      720

accccctgct tggttacagt gcagctcctc aagtccacag acgtgggccg gcacagcctc      780

ctgtacctga aggaaatcgg ccgtggctgg ttcgggaagg tacgtgtccc gcctgggagg      840

gaggactccc gcctgggagg cagaagggac acagggctgc agacctgctc ctcctaggag      900

ccaccccagc cccgacggtc ccttcttcag tctctgggcc ctgctggacc cttccccagg      960

gaggtcctca gcatctggct gcatcccctt ctccctaggg ggtcctgggg tcagaggtac     1020

ctggggaggg gccctgggag ggagaggagc agcctcttgc tcatggcctt cccctgacct     1080

tggcctaaac ga                                                         1092


<210>  6
<211>  519
<212>  DNA
<213>  Homo sapiens

<400>  6
agccccgcct ctacattctc tgggtctcca ggccctggaa ggagccccct ccccctgggc       60

tctcctggca gccaggctca gacccaggcc tgtcagccct ctgggcagtt gacgtgggag      120

cagaattcgg ggaatccctc ggggcgtggg caggcatgag tgggctctgc cagcgctggc      180

cccttcgtcc cgggcctcac tgacccttcc tcccgctgac ctcacccggc ctggccctcg      240

gggagaatgg gccagtgtgc tccgtgcggg gccgtgccaa gcagccccca acaaaggagc      300

ctttggtgcg cccggcgtgg gatgccagcc tgcggcaggg tgggggtggg ccgctccagt      360

gccctctctg tgccgtggcc ccagcctctt gctcagccac actgcctgcc tggtgcagcc      420

catgtgacgg gtcgagctcc gggccctgct gtccctggcc gggctatccc agtggcttca      480

ggcaccttct ccagacctac ccagaaagat gcccggatg                             519


<210>  7
<211>  898
<212>  DNA
<213>  Homo sapiens

<400>  7
acctaaatat gccataactt cctttacttc cctctccaag aatttccaat tgctcttcca       60

gcctattctg cctgacaggt tagaaagttt tcaatagttt tcaatagagg ttcgtttact      120

tgcattgaat tatctcatga aggtcagctt gattcgggca cattaaagac agagtcggaa      180

gaacacattt ccctaagttt tattctaatg tacaacacat gtgatcattt gcgatggggt      240

ctaggcagac aaggcaggta acagggagtc cttccaacca ggggttggaa caaaggaggc      300

ttgatttggt gactcttgag acatttggct cactgctgtg atgctgtgag agattagctg      360

tgcaatgttt gggctcctta aaaggaagtt tatttaaaat aaaacttacc tgcacgtatg      420

taacactgta gacacagatc cttcccacag tatatttaat ctctgcagaa ttcactggga      480

ggggagggga gccagtggga cctcttggct attacacagg ttggcacttc cagagagaac      540

agtcttggca tcacaggctt caggcatact caaagctctt ctcccttctg attccagttt      600

ctccatgccc tgcagggcct cttgggatta ttgtattctg gaaagcaaac aaagttggac      660

actgtctctt taaataatag aggctgagaa cctctcaggc caccatgaca tatcccagca      720

ttggaccagc ccctgaataa actggaaaga cgcctggtct ggcttcagtt acagggagca      780

ccaccaggga acatctcggg gagcctggtt ggaagctgca ggcttagtct gtcggctgcg      840

ggtctctgac tgccctgtgg ggagggtctt gccttaacat cccttgcatt tggctgca        898


<210>  8
<211>  287
<212>  DNA
<213>  Homo sapiens

<400>  8
gggcctcttg ggattattgt attctggaaa gcaaacaaag ttggacactg tctctttaaa       60

taatagaggc tgagaacctc tcaggccacc atgacatatc ccagcattgg accagcccct      120

gaataaactg gaaagacgcc tggtctggct tcagttacag ggagcaccac cagggaacat      180

ctcggggagc ctggttggaa gctgcaggct tagtctgtcg gctgcgggtc tctgactgcc      240

ctgtggggag ggtcttgcct taacatccct tgcatttggc tgcaaag                    287


<210>  9
<211>  104
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  rPmp22 sh1

<400>  9
gatctctgtt gacagtgagc gaccattcaa cctcatagga taatagtgaa gccacagatg       60

tattatccta tgaggttgaa tgggtgccta ctgcctcgga ccgg                       104


<210>  10
<211>  99
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  rPmp22 sh2

<400>  10
gatctgctgt tgacagtgag ctgttatcct atgaggttga atggttttgg ccactgactg       60

actccattcc ctcataggat aagagcctac tgccaccgg                              99


<210>  11
<211>  121
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  mPmp22 sh1

<400>  11
ggaaaggacg aaacaccgga ttcttgctgg tctgtgcgtg atgagtgcct cgaggcactc       60

atcacgcaca gaccagcaag aattttttgg atcccaagtt tgtacaaaaa agcaggctta      120

a                                                                      121


<210>  12
<211>  50
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA targeting exon 1A of hPmp22 (target site 1)

<400>  12
caccgggtta cgctgtttgg ccgggcgaac ccggccaaac agcgtaaccc                  50


<210>  13
<211>  49
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA targeting exon 1A of hPmp22 (target site 2)

<400>  13
caccacgctg tttggccggg cagaacgaat tctgcccggc caaacagcg                   49


<210>  14
<211>  50
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA targeting exon 1A of hPmp22 (target site 3)

<400>  14
caccgctgtt tggccgggca gaaaccgaag tttctgcccg gccaaacagc                  50


<210>  15
<211>  90
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA with 5' UTR no. 1 for PMP22 (sh51)

<400>  15
cgcgtatccg tctttgcagc caaatgcaag ggatgtagtg aaatatatat taaacatccc       60

ttgcatttgg ctgcaattac ggtaacgcgc                                        90


<210>  16
<211>  90
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA with 5' UTR no. 2 for PMP22 (sh52)

<400>  16
cgcgtatccg tcttccaagc agatttcttt gcaggtagtg aaatatatat taaacctgca       60

aagaaatctg cttggattac ggtaacgcgc                                        90


<210>  17
<211>  90
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA with 5' UTR no. 3 for PMP22 (sh53)

<400>  17
cgcgtatccg tctgttaagg caagaccctc cccagtagtg aaatatatat taaactgggg       60

agggtcttgc cttaacttac ggtaacgcgc                                        90


<210>  18
<211>  86
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  shRNA-1 for PMP22 coding region

<400>  18
cgcgtatccg tctgcactca tcacgcacag acgtagtgaa atatatatta aacgtctgtg       60

cgtgatgagt gcttacggta acgcgc                                            86


<210>  19
<211>  88
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Scrambled shRNA (scr)

<400>  19
cgcgtatccg tctcctaagg ttaagtcgcc ctcgtagtga aatatatatt aaacgagggc       60

gacttaacct taggttacgg taacgcgc                                          88


<210>  20
<211>  82
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Micro RNA (miR) flanking sequence

<400>  20
tcaacgccct aggtttatgt ttggatgaac tgacatacgc gttctccaat tggcaactat       60

tttatcaatt ttttgcgtcg ac                                                82


