                         SEQUENCE LISTING

<110>  Research Institute at Nationwide Children's Hospital
 
<120>  COMPOSITIONS AND METHODS FOR TREATING FACIOSCAPULOHUMERAL 
       MUSCULAR DYSTROPHY (FSHD)

<130>  28335/56061/PC

<140>  PCT/US2021/061109
<141>  2021-11-30

<150>  US 63/119,268
<151>  2020-11-30

<160>  43    

<170>  PatentIn version 3.5

<210>  1
<211>  34
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  1
gctgaggggt gcttccagcg aggcggcctc ttcc                                   34


<210>  2
<211>  33
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  2
aggcctccag ctcccccggg gcctccgttt cta                                    33


<210>  3
<211>  32
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  3
tgcagaaact ccgggctcgc caggagctca tc                                     32


<210>  4
<211>  44
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  4
aaccccgcgt cctaaagctc ctccagcaga gcccggtatt cttc                        44


<210>  5
<211>  48
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  5
gctcctccag cagagcccgg tattcttcct cgctgagggg tgcttcca                    48


<210>  6
<211>  35
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  6
cgaaccaccc gaccccgtcc caaccccgcg tccta                                  35


<210>  7
<211>  32
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  7
agctcctcca gcagagcccg gtattcttcc tc                                     32


<210>  8
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  8
ggagggggca ttttaatata tctctgaact                                        30


<210>  9
<211>  29
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  9
gtgctgtccg agggtgtcgg gagggccat                                         29


<210>  10
<211>  45
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  10
ggcttccgcg gggagggtgc tgtccgaggg tgtcgggagg gccat                       45


<210>  11
<211>  47
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  11
gaaccacccg accccgtccc aaccccgcgt cctaaagctc ctccagc                     47


<210>  12
<211>  64
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  12
gaaccacccg accccgtccc aaccccgcgt cctaaagctc ctccagcaga gcccggtatt       60

cttc                                                                    64


<210>  13
<211>  32
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  13
gtgcgcagta ggcggcccac ctgctggtac ct                                     32


<210>  14
<211>  35
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  14
cgcgcaggtc tagtcaggaa gcgggcaaag acaga                                  35


<210>  15
<211>  65
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  15
cggggtgcgc actgcgcgca ggtctagtca ggaagcgggc aaagacagac agaggtatgc       60

ttttg                                                                   65


<210>  16
<211>  42
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  16
gcacgtcagc cggggtgcgc actgcgcgca ggtctagtca gg                          42


<210>  17
<211>  40
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  17
gggggcattt taatatatct ctgaactaat catccaggag                             40


<210>  18
<211>  61
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  18
ggagggggca ttttaatata tctctgaact aatcatccag gagatgtaac tctaatccag       60

g                                                                       61


<210>  19
<211>  34
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  19
ggaagaggcc gcctcgctgg aagcacccct cagc                                   34


<210>  20
<211>  33
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  20
tagaaacgga ggccccgggg gagctggagg cct                                    33


<210>  21
<211>  32
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  21
gatgagctcc tggcgagccc ggagtttctg ca                                     32


<210>  22
<211>  44
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  22
gaagaatacc gggctctgct ggaggagctt taggacgcgg ggtt                        44


<210>  23
<211>  48
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  23
tggaagcacc cctcagcgag gaagaatacc gggctctgct ggaggagc                    48


<210>  24
<211>  35
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  24
taggacgcgg ggttgggacg gggtcgggtg gttcg                                  35


<210>  25
<211>  32
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  25
gaggaagaat accgggctct gctggaggag ct                                     32


<210>  26
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  26
agttcagaga tatattaaaa tgccccctcc                                        30


<210>  27
<211>  29
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  27
atggccctcc cgacaccctc ggacagcac                                         29


<210>  28
<211>  45
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  28
atggccctcc cgacaccctc ggacagcacc ctccccgcgg aagcc                       45


<210>  29
<211>  47
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  29
gctggaggag ctttaggacg cggggttggg acggggtcgg gtggttc                     47


<210>  30
<211>  64
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  30
gaagaatacc gggctctgct ggaggagctt taggacgcgg ggttgggacg gggtcgggtg       60

gttc                                                                    64


<210>  31
<211>  32
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  31
aggtaccagc aggtgggccg cctactgcgc ac                                     32


<210>  32
<211>  35
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  32
tctgtctttg cccgcttcct gactagacct gcgcg                                  35


<210>  33
<211>  65
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  33
caaaagcata cctctgtctg tctttgcccg cttcctgact agacctgcgc gcagtgcgca       60

ccccg                                                                   65


<210>  34
<211>  42
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  34
cctgactaga cctgcgcgca gtgcgcaccc cggctgacgt gc                          42


<210>  35
<211>  40
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  35
ctcctggatg attagttcag agatatatta aaatgccccc                             40


<210>  36
<211>  61
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  36
cctggattag agttacatct cctggatgat tagttcagag atatattaaa atgccccctc       60

c                                                                       61


<210>  37
<211>  1275
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  37
atggccctcc cgacaccctc ggacagcacc ctccccgcgg aagcccgggg acgaggacgg       60

cgacggagac tcgtttggac cccgagccaa agcgaggccc tgcgagcctg ctttgagcgg      120

aacccgtacc cgggcatcgc caccagagaa cggctggccc aggccatcgg cattccggag      180

cccagggtcc agatttggtt tcagaatgag aggtcacgcc agctgaggca gcaccggcgg      240

gaatctcggc cctggcccgg gagacgcggc ccgccagaag gccggcgaaa gcggaccgcc      300

gtcaccggat cccagaccgc cctgctcctc cgagcctttg agaaggatcg ctttccaggc      360

atcgccgccc gggaggagct ggccagagag acgggcctcc cggagtccag gattcagatc      420

tggtttcaga atcgaagggc caggcacccg ggacagggtg gcagggcgcc cgcgcaggca      480

ggcggcctgt gcagcgcggc ccccggcggg ggtcaccctg ctccctcgtg ggtcgccttc      540

gcccacaccg gcgcgtgggg aacggggctt cccgcacccc acgtgccctg cgcgcctggg      600

gctctcccac agggggcttt cgtgagccag gcagcgaggg ccgcccccgc gctgcagccc      660

agccaggccg cgccggcaga ggggatctcc caacctgccc cggcgcgcgg ggatttcgcc      720

tacgccgccc cggctcctcc ggacggggcg ctctcccacc ctcaggctcc tcggtggcct      780

ccgcacccgg gcaaaagccg ggaggaccgg gacccgcagc gcgacggcct gccgggcccc      840

tgcgcggtgg cacagcctgg gcccgctcaa gcggggccgc agggccaagg ggtgcttgcg      900

ccacccacgt cccaggggag tccgtggtgg ggctggggcc ggggtcccca ggtcgccggg      960

gcggcgtggg aaccccaagc cggggcagct ccacctcccc agcccgcgcc cccggacgcc     1020

tccgcctccg cgcggcaggg gcagatgcaa ggcatcccgg cgccctccca ggcgctccag     1080

gagccggcgc cctggtctgc actcccctgc ggcctgctgc tggatgagct cctggcgagc     1140

ccggagtttc tgcagcaggc gcaacctctc ctagaaacgg aggccccggg ggagctggag     1200

gcctcggaag aggccgcctc gctggaagca cccctcagcg aggaagaata ccgggctctg     1260

ctggaggagc tttag                                                      1275


<210>  38
<211>  424
<212>  PRT
<213>  Artificial Seuqence

<220>
<223>  Synthetic

<400>  38

Met Ala Leu Pro Thr Pro Ser Asp Ser Thr Leu Pro Ala Glu Ala Arg 
1               5                   10                  15      


Gly Arg Gly Arg Arg Arg Arg Leu Val Trp Thr Pro Ser Gln Ser Glu 
            20                  25                  30          


Ala Leu Arg Ala Cys Phe Glu Arg Asn Pro Tyr Pro Gly Ile Ala Thr 
        35                  40                  45              


Arg Glu Arg Leu Ala Gln Ala Ile Gly Ile Pro Glu Pro Arg Val Gln 
    50                  55                  60                  


Ile Trp Phe Gln Asn Glu Arg Ser Arg Gln Leu Arg Gln His Arg Arg 
65                  70                  75                  80  


Glu Ser Arg Pro Trp Pro Gly Arg Arg Gly Pro Pro Glu Gly Arg Arg 
                85                  90                  95      


Lys Arg Thr Ala Val Thr Gly Ser Gln Thr Ala Leu Leu Leu Arg Ala 
            100                 105                 110         


Phe Glu Lys Asp Arg Phe Pro Gly Ile Ala Ala Arg Glu Glu Leu Ala 
        115                 120                 125             


Arg Glu Thr Gly Leu Pro Glu Ser Arg Ile Gln Ile Trp Phe Gln Asn 
    130                 135                 140                 


Arg Arg Ala Arg His Pro Gly Gln Gly Gly Arg Ala Pro Ala Gln Ala 
145                 150                 155                 160 


Gly Gly Leu Cys Ser Ala Ala Pro Gly Gly Gly His Pro Ala Pro Ser 
                165                 170                 175     


Trp Val Ala Phe Ala His Thr Gly Ala Trp Gly Thr Gly Leu Pro Ala 
            180                 185                 190         


Pro His Val Pro Cys Ala Pro Gly Ala Leu Pro Gln Gly Ala Phe Val 
        195                 200                 205             


Ser Gln Ala Ala Arg Ala Ala Pro Ala Leu Gln Pro Ser Gln Ala Ala 
    210                 215                 220                 


Pro Ala Glu Gly Ile Ser Gln Pro Ala Pro Ala Arg Gly Asp Phe Ala 
225                 230                 235                 240 


Tyr Ala Ala Pro Ala Pro Pro Asp Gly Ala Leu Ser His Pro Gln Ala 
                245                 250                 255     


Pro Arg Trp Pro Pro His Pro Gly Lys Ser Arg Glu Asp Arg Asp Pro 
            260                 265                 270         


Gln Arg Asp Gly Leu Pro Gly Pro Cys Ala Val Ala Gln Pro Gly Pro 
        275                 280                 285             


Ala Gln Ala Gly Pro Gln Gly Gln Gly Val Leu Ala Pro Pro Thr Ser 
    290                 295                 300                 


Gln Gly Ser Pro Trp Trp Gly Trp Gly Arg Gly Pro Gln Val Ala Gly 
305                 310                 315                 320 


Ala Ala Trp Glu Pro Gln Ala Gly Ala Ala Pro Pro Pro Gln Pro Ala 
                325                 330                 335     


Pro Pro Asp Ala Ser Ala Ser Ala Arg Gln Gly Gln Met Gln Gly Ile 
            340                 345                 350         


Pro Ala Pro Ser Gln Ala Leu Gln Glu Pro Ala Pro Trp Ser Ala Leu 
        355                 360                 365             


Pro Cys Gly Leu Leu Leu Asp Glu Leu Leu Ala Ser Pro Glu Phe Leu 
    370                 375                 380                 


Gln Gln Ala Gln Pro Leu Leu Glu Thr Glu Ala Pro Gly Glu Leu Glu 
385                 390                 395                 400 


Ala Ser Glu Glu Ala Ala Ser Leu Glu Ala Pro Leu Ser Glu Glu Glu 
                405                 410                 415     


Tyr Arg Ala Leu Leu Glu Glu Leu 
            420                 


<210>  39
<211>  61
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  39
gaatcgagca ccagttacgc atgccgaggt cgacttccta gatttttttt tttttttttt       60

t                                                                       61


<210>  40
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  40
cagaatgaga ggtcacgcca g                                                 21


<210>  41
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  41
gaatcgagca ccagttacgc atg                                               23


<210>  42
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  42
gagcaccagt tacgcatgcc                                                   20


<210>  43
<211>  34
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  synthetic

<400>  43
gtcatgtcgc gtgccccggt ggtcgacacg tcgg                                   34


