                         SEQUENCE LISTING

<110>  Expansion Therapeutics, Inc.
 
<120>  SMALL MOLECULES THAT TARGET THE RNA THAT CAUSES ALS

<130>  32894/1941 PC

<150>  US 63/075,390
<151>  2020-09-08

<160>  22    

<170>  PatentIn version 3.5

<210>  1
<211>  24
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  1
ggggccgggg ccggggccgg ggcc                                              24


<210>  2
<211>  48
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  2
ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggcc                    48


<210>  3
<211>  24
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  3
ggccccggcc ccggccccgg cccc                                              24


<210>  4
<211>  48
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  4
ggccccggcc ccggccccgg ccccggcccc ggccccggcc ccggcccc                    48


<210>  5
<211>  48
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  5
ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggcc                    48


<210>  6
<211>  24
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  6
cggcggcggc ggcggcggcg gcgg                                              24


<210>  7
<211>  36
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  7
cggcggcggc ggcggcggcg gcggcggcgg cggcgg                                 36


<210>  8
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  8
ggccggccga aaggccggcc                                                   20


<210>  9
<211>  36
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  9
ggccggccgg ccggccgaaa ggccggccgg ccggcc                                 36


<210>  10
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  10
gcgcgcgcga aagcgcgcgc                                                   20


<210>  11
<211>  396
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  11
ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc       60

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      120

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      180

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      240

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      300

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      360

ggggccgggg ccggggccgg ggccggggcc ggggcc                                396


<210>  12
<211>  396
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  12
ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc       60

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      120

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      180

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      240

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      300

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      360

ggggccgggg ccggggccgg ggccggggcc ggggcc                                396


<210>  13
<211>  372
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  13
tgggcctggg cctgggcctg ggcctgggcc tgggcctggg cctgggcctg ggcctgggcc       60

tgggcctggg cctgggcctg ggcctgggcc tgggcctggg cctgggcctg ggcctgggcc      120

tgggcctggg cctgggcctg ggcctgggcc tgggcctggg cctgggcctg ggcctgggcc      180

tgggcctggg cctgggcctg ggcctgggcc tgggcctggg cctgggcctg ggcctgggcc      240

tgggcctggg cctgggcctg ggcctgggcc tgggcctggg cctgggcctg ggcctgggcc      300

tgggcctggg cctgggcctg ggcctgggcc tgggcctggg cctgggcctg ggcctgggcc      360

tgggcctggg cc                                                          372


<210>  14
<211>  434
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  14
tggggcctgg ggcctggggc ctggggcctg gggcctgggg cctggggcct ggggcctggg       60

gcctggggcc tggggcctgg ggcctggggc ctggggcctg gggcctgggg cctggggcct      120

ggggcctggg gcctggggcc tggggcctgg ggcctggggc ctggggcctg gggcctgggg      180

cctggggcct ggggcctggg gcctggggcc tggggcctgg ggcctggggc ctggggcctg      240

gggcctgggg cctggggcct ggggcctggg gcctggggcc tggggcctgg ggcctggggc      300

ctggggcctg gggcctgggg cctggggcct ggggcctggg gcctggggcc tggggcctgg      360

ggcctggggc ctggggcctg gggcctgggg cctggggcct ggggcctggg gcctggggcc      420

tggggcctgg ggcc                                                        434


<210>  15
<211>  36
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  15
ggccggccgg ccggccaaaa ggccggccgg ccggcc                                 36


<210>  16
<211>  48
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  16
ugggccuggg ccugggccug ggccugggcc ugggccuggg ccugggcc                    48


<210>  17
<211>  33
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  17
uaggguuagg guaggguuag gguaggguua ggg                                    33


<210>  18
<211>  48
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  18
ugggccuggg ccugggccug ggccugggcc ugggccuggg ccugggcc                    48


<210>  19
<211>  33
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  19
uaggguuagg guaggguuag gguaggguua ggg                                    33


<210>  20
<211>  23
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  20
uaggguuagg guuaggguua ggg                                               23


<210>  21
<211>  372
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  21
ugggccuggg ccugggccug ggccugggcc ugggccuggg ccugggccug ggccugggcc       60

ugggccuggg ccugggccug ggccugggcc ugggccuggg ccugggccug ggccugggcc      120

ugggccuggg ccugggccug ggccugggcc ugggccuggg ccugggccug ggccugggcc      180

ugggccuggg ccugggccug ggccugggcc ugggccuggg ccugggccug ggccugggcc      240

ugggccuggg ccugggccug ggccugggcc ugggccuggg ccugggccug ggccugggcc      300

ugggccuggg ccugggccug ggccugggcc ugggccuggg ccugggccug ggccugggcc      360

ugggccuggg cc                                                          372


<210>  22
<211>  12
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotide

<400>  22
ggggccgggg cc                                                           12


