                         SEQUENCE LISTING

<110>  CONSEJO NACIONAL DE INVESTIGACIONES CIENTIFICAS Y TECNICAS 
       (CONICET)
       MARASCO, LUCIANO E.
       KORNBLIHTT, ALBERTO R.
       KRAINER, ADRIAN
       STIGLIANO, JOSE
 
<120>  COMPOSITIONS FOR TREATMENT OF SPINAL MUSCULAR ATROPHY

<130>  3181.007PC01

<150>  US 63/051,279
<151>  2020-07-13

<160>  86    

<170>  PatentIn version 3.5

<210>  1
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  ASO1

<400>  1
attcactttc ataatgctgg                                                   20


<210>  2
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  2
aaagtatgtt tcttccacac                                                   20


<210>  3
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  3
auucacuuuc auaaugcugg                                                   20


<210>  4
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  4
aagtgagaac tccaggtctc ctg                                               23


<210>  5
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  5
tctgatcgtt tctttagtgg tgtc                                              24


<210>  6
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  6
cgggtttgct atggcgatga g                                                 21


<210>  7
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  7
ggctgcggaa ggagagttgg                                                   20


<210>  8
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  8
ccttccatat tccagttctc ttg                                               23


<210>  9
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  9
tacctgtaac gcttcacatt cc                                                22


<210>  10
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  10
caaatgtggg agggcgataa cc                                                22


<210>  11
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  11
ttctgggagc ggaacagtac g                                                 21


<210>  12
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  12
ggctcactac aacctcctc                                                    19


<210>  13
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  13
ttcagattat tctcctccat tcc                                               23


<210>  14
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  14
tccttacagg gttttagaca aaatc                                             25


<210>  15
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  15
cataatgctg gcagacttac tcc                                               23


<210>  16
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  16
acatataagc catttagcaa ccc                                               23


<210>  17
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  17
gaactcctga cctcgtaatc c                                                 21


<210>  18
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  18
gagaccagcc tacacaatat gc                                                22


<210>  19
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  19
ccgcctcaac ctcccaag                                                     18


<210>  20
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  20
ccgaaacccc gtctctacta aatac                                             25


<210>  21
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  21
aagcgatcct cccacctcag                                                   20


<210>  22
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  22
aatgtagtat ggttctgtgt ctc                                               23


<210>  23
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  23
gtttgctcaa ggtagtctgg                                                   20


<210>  24
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  24
tttatctccc tcccgctatt c                                                 21


<210>  25
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  25
aatctctttg agtcttagtt tccc                                              24


<210>  26
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  26
tctcttgatg atgctgatgc                                                   20


<210>  27
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  27
agatgctgag tgattactta cc                                                22


<210>  28
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  28
gcaaggcaag gcattacag                                                    19


<210>  29
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  29
cctgagcaat agagtgagac c                                                 21


<210>  30
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  30
cactgtgcct agcctgag                                                     18


<210>  31
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  31
ggatcacttg agacctggag                                                   20


<210>  32
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  32
actggttggt tgtgtggaag                                                   20


<210>  33
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  33
agtctgctgg tctgcctac                                                    19


<210>  34
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  34
acagtgggtg ggcattcag                                                    19


<210>  35
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  35
gagcggtggc gacagtag                                                     18


<210>  36
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  36
tctctgccgc ttgggttg                                                     18


<210>  37
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  37
catagaagtc gtccgttgtg g                                                 21


<210>  38
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  38
ctctctccca tcccttctcc                                                   20


<210>  39
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  39
ttgccaagtt gcctgtcc                                                     18


<210>  40
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  40
atgaatgggc agccgttag                                                    19


<210>  41
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  41
tcgctccacc tgacttcc                                                     18


<210>  42
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  42
gcatcgttaa agtctctctt cacc                                              24


<210>  43
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  43
ctcctcaggc tctcatcagt tg                                                22


<210>  44
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  44
tggcattaaa gaagacactg aag                                               23


<210>  45
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  45
tcaaaggtta caaaggcaaa gc                                                22


<210>  46
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  46
aagtgagaac tccaggtctc ctg                                               23


<210>  47
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  47
cttctgagtc ttgggcatgt cagtg                                             25


<210>  48
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  48
gaatgggaag cttgtcatca acgg                                              24


<210>  49
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  49
ccgttcagct ctgggatgac cttg                                              24


<210>  50
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  50
ctgaagcttt tggctttgag                                                   20


<210>  51
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  51
ccgctgccaa attctttgg                                                    19


<210>  52
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  52
ttgtctagag agcatggagg gccatgtcaa                                        30


<210>  53
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  53
ccactcctct gtgacacttt agccctccga                                        30


<210>  54
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  54
ataacaccac cactcttact c                                                 21


<210>  55
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  55
gtagccgtga tgccattgtc a                                                 21


<210>  56
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  56
agcctgaaga acgagatcag c                                                 21


<210>  57
<211>  8
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  57
ccagcauu                                                                 8


<210>  58
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  58
tgctggcaga cttac                                                        15


<210>  59
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  59
cataatgctg gcaga                                                        15


<210>  60
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  60
tcataatgct ggcag                                                        15


<210>  61
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  61
ttcataatgc tggca                                                        15


<210>  62
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  62
tttcataatg ctggc                                                        15


<210>  63
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Nusinersen

<400>  63
tcactttcat aatgctgg                                                     18


<210>  64
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  64
agtaagattc acttt                                                        15


<210>  65
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  65
ctttcataat gctgg                                                        15


<210>  66
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  66
tcataatgct gg                                                           12


<210>  67
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  67
actttcataa tgctg                                                        15


<210>  68
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  68
ttcataatgc tg                                                           12


<210>  69
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  69
cactttcata atgct                                                        15


<210>  70
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  70
tttcataatg ct                                                           12


<210>  71
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  71
tcactttcat aatgc                                                        15


<210>  72
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  72
ctttcataat gc                                                           12


<210>  73
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  73
ttcactttca taatg                                                        15


<210>  74
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  74
actttcataa tg                                                           12


<210>  75
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  75
attcactttc ataat                                                        15


<210>  76
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  76
cactttcata at                                                           12


<210>  77
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  77
gattcacttt cataa                                                        15


<210>  78
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  78
tcactttcat aa                                                           12


<210>  79
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  79
ttcactttca ta                                                           12


<210>  80
<211>  12
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  80
attcactttc at                                                           12


<210>  81
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  81
ccagcauuau gaaag                                                        15


<210>  82
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  82
ccagcauuau gaaaguga                                                     18


<210>  83
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  83
ccagcauuau gaaagugaau                                                   20


<210>  84
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence


<220>
<221>  misc_feature
<222>  (6)..(10)
<223>  Wherein n can be any nucleotide

<400>  84
ccagcnnnnn gaaag                                                        15


<210>  85
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  85
gctcaggtga tccaactgtc tc                                                22


<210>  86
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic sequence

<400>  86
cgtggtggct caggctagg                                                    19


