                               SEQUENCE LISTING

<110> SOLID BIOSCIENCES INC.
 
<120> COMBINATION THERAPY FOR TREATING MUSCULAR DYSTROPHY

<130> 129159-11120

<140> PCT/US2021/012942
<141> 2021-01-11

<150> 62/959,256
<151> 2020-01-10

<160> 40    

<170> PatentIn version 3.5

<210> 1
<211> 129
<212> DNA
<213> Unknown

<220>
<223> Description of Unknown: 
      Heterologous intron sequence

<400> 1
gtatcaaggt tacaagacag gtttaaggag accaatagaa actgggcttg tcgagacaga       60

gaagactctt gcgtttctga taggcaccta ttggtcttac tgacatccac tttgcctttc      120

tctccacag                                                              129


<210> 2
<211> 217
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 2
gtatcaaggt tacaagacag gtttaaggag accaatagaa actgggcttg tcgagacaga       60

tctcttacac aggctgaccg atttctcctg gtgttcagag tctgtttttg tctagcacca      120

tttgaaatcg gttatgatgt agggggaaga agactcttgc gtttctgata ggcacctatt      180

ggtcttactg acatccactt tgcctttctc tccacag                               217


<210> 3
<211> 88
<212> DNA
<213> Unknown

<220>
<223> Description of Unknown: 
      miR-29c sequence

<400> 3
atctcttaca caggctgacc gatttctcct ggtgttcaga gtctgttttt gtctagcacc       60

atttgaaatc ggttatgatg taggggga                                          88


<210> 4
<211> 722
<212> DNA
<213> Homo sapiens

<400> 4
agacagcctg ggaggggaga aggagttgga gctcaagttg gagacagcga ggagaaacct       60

gccatagcca gggtgtgtct ttgatcctct tcaggaggtg aggagaagcc agaggtcctt      120

ggtgtgccct cagaaatctg cctgcagttc tcaccaagcc gctgtgaaaa tggggataaa      180

cacccgggag ctgtttctca acttcactat tgtcttgatt acggttattc ttatgtggct      240

ccttgtgagg tcctatcagt actgagaggc catgccatgg tcctgggatt gactgagatg      300

ctccggagct gcctgctcta tgccctgaga ccccactgct gtcattgtca caggatgcca      360

ttctccatcc gagggcacct gtgacctgca ctcacaatat ctgctatgct gtagtgctag      420

gattgattat gtgttctcca aagatgctgc tcccaagggc tgccaagtgt ttgccaggga      480

acggtagatt tattccccaa ctcttaactg aaaatgtgtt agacaagcca caaagttaaa      540

attaaactgg attcatgatg atgtaggatt gttacaagcc cctgatctgt ctcaccacac      600

atcccttcaa cccacacggt ctgcaaccaa actctaattc aacctgccag aaggaatgtt      660

agaggaagtc tttgtcagcc cttatagcta tcatgtgaat aaagttaagt caacttcaaa      720

aa                                                                     722


<210> 5
<211> 31
<212> PRT
<213> Homo sapiens

<400> 5
Met Gly Ile Asn Thr Arg Glu Leu Phe Leu Asn Phe Thr Ile Val Leu 
1               5                   10                  15      


Ile Thr Val Ile Leu Met Trp Leu Leu Val Arg Ser Tyr Gly Tyr 
            20                  25                  30      


<210> 6
<211> 22
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 6
accgatttca aatggtgcta ga                                                22


<210> 7
<211> 24
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 7
tctagcacca tttgaaatcg gtta                                              24


<210> 8
<211> 15
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 8
gtgaagccac agatg                                                        15


<210> 9
<211> 206
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 9
cagccactat gggtctaggc tgcccatgta aggaggcaag gcctggggac acccgagatg       60

cctggttata attaacccag acatgtggct gctccccccc cccaacacct gctgcctgag      120

cctcaccccc accccggtgc ctgggtctta ggctctgtac accatggagg agaagctcgc      180

tctaaaaata accctgtccc tggtgg                                           206


<210> 10
<211> 358
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 10
gctgtggggg actgagggca ggctgtaaca ggcttggggg ccagggctta tacgtgcctg       60

ggactcccaa agtattactg ttccatgttc ccggcgaagg gccagctgtc ccccgccagc      120

tagactcagc acttagttta ggaaccagtg agcaagtcag cccttggggc agcccataca      180

aggccatggg gctgggcaag ctgcacgcct gggtccgggg tgggcacggt gcccgggcaa      240

cgagctgaaa gctcatctgc tctcaggggc ccctccctgg ggacagcccc tcctggctag      300

tcacaccctg taggctcctc tatataaccc aggggcacag gggctgcccc cgggtcac        358


<210> 11
<211> 157
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 11
tcgacttctt aacccaacag aaggctcgag aaggtatatt gctgttgaca gtgagcgtaa       60

ccgatttcaa atggtgctat agtgaagcca cagatgtata gcaccatttg aaatcggtta      120

tgcctactgc ctcggacttc aaggggctag aattcga                               157


<210> 12
<211> 159
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 12
tcgacttctt aacccaacag aaggctcgag aaggtatatt gctgttgaca gtgagcgaac       60

ttcactattg tcttgattac tagtgaagcc acagatgtag taatcaagac aatagtgaag      120

tttgcctact gcctcggact tcaaggggct agaattcga                             159


<210> 13
<211> 159
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 13
tcgacttctt aacccaacag aaggctcgag aaggtatatt gctgttgaca gtgagcgaac       60

acccgggagc tgtttctcaa tagtgaagcc acagatgtat tgagaaacag ctcccgggtg      120

tttgcctact gcctcggact tcaaggggct agaattcga                             159


<210> 14
<211> 153
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 14
ggttaaccca acagaaggct aaagaaggta tattgctgtt gacagtgagc gactagcacc       60

atttgaaatc ggttactgtg aagccacaga tgggtaaccg attaaatggt gctagctgcc      120

tactgcctcg gacttcaagg ggctacttta gga                                   153


<210> 15
<211> 204
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 15
ccaccagaaa ggatgccgtt gaccgacaca gtgactgaca ggctgccctg gcgaaccgat       60

ttcaaatggt gcataccgtc tattctaaag gtagcaccat ttgaaatcgg ttaggatggc      120

agccatctta ccttccatca gaggagcctc accgtaccca ggaagaaaga aggtgaaaga      180

ggaatgtgaa acaggtggct ggga                                             204


<210> 16
<211> 133
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 16
cctggaggct tgctgaaggc tgtatgctgt agcaccattt gaaatcggtt attttggcct       60

ctgactgatg accgctggaa tggtgctaca ggacacaagg cctgttacta gcactcacat      120

ggaacaaatg gcc                                                         133


<210> 17
<211> 135
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 17
cctggaggct tgctgaaggc tgtatgctgt agcaccattt gaaatcggtt agttttggcc       60

actgactgac taaccgatca aatggtgcta caggacacaa ggcctgttac tagcactcac      120

atggaacaaa tggcc                                                       135


<210> 18
<211> 133
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 18
cctggaggct tgctgaaggc tgtatgctgg tgatgaggac aactgtgaag gttttggcca       60

ctgactgacc ttcacaggtc ctcatcacca ggacacaagg cctgttacta gcactcacat      120

ggaacaaatg gcc                                                         133


<210> 19
<211> 137
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 19
cctggaggct tgctgaaggc tgtatgctgg tgatgaggac aactgtgaag ttgttttggc       60

cactgactga caacttcact tgtcctcatc accaggacac aaggcctgtt actagcactc      120

acatggaaca aatggcc                                                     137


<210> 20
<211> 137
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 20
cctggaggct tgctgaaggc tgtatgctgg taatcaagac aatagtgaag ttgttttggc       60

cactgactga caacttcact tgtcttgatt accaggacac aaggcctgtt actagcactc      120

acatggaaca aatggcc                                                     137


<210> 21
<211> 139
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 21
cctggaggct tgctgaaggc tgtatgctgt tgagaaacag ctcccgggtg ttgttttggc       60

cactgactga caacacccgg gagctgtttc tcaacaggac acaaggcctg ttactagcac      120

tcacatggaa caaatggcc                                                   139


<210> 22
<211> 215
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 22
ggacaggaga gatgctgcaa gcccaagaag ctctctgctc agcctgtcac aacctactga       60

ctgccagggc acttgggaat ggcaaggtag caccatttga aatcggttac gatttcaaat      120

ggtgctgtct tgctataccc agaaaacgtg ccaggaagag aactcaggac cctgaagcag      180

actactggaa gggagactcc agctcaaaca aggca                                 215


<210> 23
<211> 74
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 23
gatcgtaacc gatttcaaat ggtgctagcc ctgacccagc tagcaccatt tgaaatcggt       60

tattttttga agct                                                         74


<210> 24
<211> 65
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 24
gatcgacttc acagttgtcc tcatcactcg agtgatgagg acaactgtga agcttttttg       60

aagct                                                                   65


<210> 25
<211> 67
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 25
gatcgacttc acagttgtcc tcatcactca agaggtgatg aggacaactg tgaagttttt       60

tgaagct                                                                 67


<210> 26
<211> 63
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 26
taaccgattt caaatggtgc tagccctgac ccagctagca ccatttgaaa tcggttattt       60

ttt                                                                     63


<210> 27
<211> 57
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 27
taaccgattt caaatggtgc tatcaagagt agcaccattt gaaatcggtt atttttt          57


<210> 28
<211> 62
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 28
taaccgattt caaatggtgc tacttcctgt cagatagcac catttgaaat cggttatttt       60

tt                                                                      62


<210> 29
<211> 59
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 29
taaccgattt caaatggtgc tattcaagag atagcaccat ttgaaatcgg ttatttttt        59


<210> 30
<211> 141
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 30
cctggaggct tgctgaaggc tgtatgctgt agcaccattt gaaatcggtt agttttggcc       60

actgactgac taaccgatca aatggtgcta caggacacaa ggcctgttac tagcactcac      120

atggaacaaa tggccttttt t                                                141


<210> 31
<211> 54
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 31
acttcacagt tgtcctcatc actcgagtga tgaggacaac tgtgaagctt tttt             54


<210> 32
<211> 53
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 32
acttcacagt tgtcctcatc actcgagtga tgaggacaac tgtgaagttt ttt              53


<210> 33
<211> 62
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 33
acttcacagt tgtcctcatc acgccctgac ccagcgtgat gaggacaact gtgaagtttt       60

tt                                                                      62


<210> 34
<211> 56
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 34
acttcacagt tgtcctcatc actcaagagg tgatgaggac aactgtgaag tttttt           56


<210> 35
<211> 52
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 35
cttcactatt gtcttgatta ctcgagtaat caagacaata gtgaagtttt tt               52


<210> 36
<211> 61
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 36
cttcactatt gtcttgatta cgccctgacc cagcgtaatc aagacaatag tgaagttttt       60

t                                                                       61


<210> 37
<211> 52
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 37
cacccgggag ctgtttctca atcgattgag aaacagctcc cgggtgtttt tt               52


<210> 38
<211> 61
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 38
cacccgggag ctgtttctca agccctgacc cagcttgaga aacagctccc gggtgttttt       60

t                                                                       61


<210> 39
<211> 52
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 39
tgtggctcct tgtgaggtcc ttcgaaggac ctcacaagga gccacatttt tt               52


<210> 40
<211> 61
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 40
tgtggctcct tgtgaggtcc tgccctgacc cagcaggacc tcacaaggag ccacattttt       60

t                                                                       61


