                               SEQUENCE LISTING

<110> APPLIED GENETIC TECHNOLOGIES CORPORATION
 
<120> ADENO-ASSOCIATED VIRUS (AAV) SYSTEMS FOR TREATMENT OF GENETIC 
      HEARING LOSS

<130> 119561-01920

<140>
<141>

<150> 62/907,834
<151> 2019-09-30

<160> 43    

<170> PatentIn version 3.5

<210> 1
<211> 1680
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 1
ctcagatctg aattcggtac ctagttatta atagtaatca attacggggt cattagttca       60

tagcccatat atggagttcc gcgttacata acttacggta aatggcccgc ctggctgacc      120

gcccaacgac ccccgcccat tgacgtcaat aatgacgtat gttcccatag taacgccaat      180

agggactttc cattgacgtc aatgggtgga gtatttacgg taaactgccc acttggcagt      240

acatcaagtg tatcatatgc caagtacgcc ccctattgac gtcaatgacg gtaaatggcc      300

cgcctggcat tatgcccagt acatgacctt atgggacttt cctacttggc agtacatcta      360

cgtattagtc atcgctatta ccatggtcga ggtgagcccc acgttctgct tcactctccc      420

catctccccc ccctccccac ccccaatttt gtatttattt attttttaat tattttgtgc      480

agcgatgggg gcgggggggg ggggggggcg cgcgccaggc ggggcggggc ggggcgaggg      540

gcggggcggg gcgaggcgga gaggtgcggc ggcagccaat cagagcggcg cgctccgaaa      600

gtttcctttt atggcgaggc ggcggcggcg gcggccctat aaaaagcgaa gcgcgcggcg      660

ggcgggagtc gctgcgcgct gccttcgccc cgtgccccgc tccgccgccg cctcgcgccg      720

cccgccccgg ctctgactga ccgcgttact cccacaggtg agcgggcggg acggcccttc      780

tcctccgggc tgtaattagc gcttggttta atgacggctt gtttcttttc tgtggctgcg      840

tgaaagcctt gaggggctcc gggagggccc tttgtgcggg gggagcggct cggggggtgc      900

gtgcgtgtgt gtgtgcgtgg ggagcgccgc gtgcggctcc gcgctgcccg gcggctgtga      960

gcgctgcggg cgcggcgcgg ggctttgtgc gctccgcagt gtgcgcgagg ggagcgcggc     1020

cgggggcggt gccccgcggt gcgggggggg ctgcgagggg aacaaaggct gcgtgcgggg     1080

tgtgtgcgtg ggggggtgag cagggggtgt gggcgcgtcg gtcgggctgc aaccccccct     1140

gcacccccct ccccgagttg ctgagcacgg cccggcttcg ggtgcggggc tccgtacggg     1200

gcgtggcgcg gggctcgccg tgccgggcgg ggggtggcgg caggtggggg tgccgggcgg     1260

ggcggggccg cctcgggccg gggagggctc gggggagggg cgcggcggcc cccggagcgc     1320

cggcggctgt cgaggcgcgg cgagccgcag ccattgcctt ttatggtaat cgtgcgagag     1380

ggcgcaggga cttcctttgt cccaaatctg tgcggagccg aaatctggga ggcgccgccg     1440

caccccctct agcgggcgcg gggcgaagcg gtgcggcgcc ggcaggaagg aaatgggcgg     1500

ggagggcctt cgtgcgtcgc cgcgccgccg tccccttctc cctctccagc ctcggggctg     1560

tccgcggggg gacggctgcc ttcggggggg acggggcagg gcggggttcg gcttctggcg     1620

tgtgaccggc ggctctagag cctctgctaa ccatgttcat gccttcttct ttttcctaca     1680


<210> 2
<211> 806
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 2
gagtcaatgg gaaaaaccca ttggagccaa gtacactgac tcaataggga ctttccattg       60

ggttttgccc agtacataag gtcaataggg ggtgagtcaa caggaaagtc ccattggagc      120

caagtacatt gagtcaatag ggactttcca atgggttttg cccagtacat aaggtcaatg      180

ggaggtaagc caatgggttt ttcccattac tgacatgtat actgagtcat tagggacttt      240

ccaatgggtt ttgcccagta cataaggtca ataggggtga atcaacagga aagtcccatt      300

ggagccaagt acactgagtc aatagggact ttccattggg ttttgcccag tacaaaaggt      360

caataggggg tgagtcaatg ggtttttccc attattggca catacataag gtcaataggg      420

gtgactagtg gagaagagca tgcttgaggg ctgagtgccc ctcagtgggc agagagcaca      480

tggcccacag tccctgagaa gttgggggga ggggtgggca attgaactgg tgcctagaga      540

aggtggggct tgggtaaact gggaaagtga tgtggtgtac tggctccacc tttttcccca      600

gggtggggga gaaccatata taagtgcagt agtctctgtg aacattcaag cttctgcctt      660

ctccctcctg tgagtttggt aagtcactga ctgtctatgc ctgggaaagg gtgggcagga      720

ggtggggcag tgcaggaaaa gtggcactgt gaaccctgca gccctagaca attgtactaa      780

ccttcttctc tttcctctcc tgacag                                           806


<210> 3
<211> 1055
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 3
ggagttccgc gttacataac ttacggtaaa tggcccgcct ggctgaccgc ccaacgaccc       60

ccgcccattg acgtcaataa tgacgtatgt tcccatagta acgccaatag ggactttcca      120

ttgacgtcaa tgggtggagt atttacggta aactgcccac ttggcagtac atcaagtgta      180

tcatatgcca agtacgcccc ctattgacgt caatgacggt aaatggcccg cctggcatta      240

tgcccagtac atgaccttat gggactttcc tacttggcag tacatctacg tattagtcat      300

cgctattacc atggtcgagg tgagccccac gttctgcttc actctcccca tctccccccc      360

ctccccaccc ccaattttgt atttatttat tttttaatta ttttgtgcag cgatgggggc      420

gggggggggg gggggcgcgc gccaggcggg gcggggcggg gcgaggggcg gggcggggcg      480

aggcggagag gtgcggcggc agccaatcag agcggcgcgc tccgaaagtt tccttttatg      540

gcgaggcggc ggcggcggcg gccctataaa aagcgaagcg cgcggcgggc gggagtcgct      600

gcgcgctgcc ttcgccccgt gccccgctcc gccgccgcct cgcgccgccc gccccggctc      660

tgactgaccg cgttactaaa acaggtaagt ccggcctccg cgccgggttt tggcgcctcc      720

cgcgggcgcc cccctcctca cggcgagcgc tgccacgtca gacgaagggc gcagcgagcg      780

tcctgatcct tccgcccgga cgctcaggac agcggcccgc tgctcataag actcggcctt      840

agaaccccag tatcagcaga aggacatttt aggacgggac ttgggtgact ctagggcact      900

ggttttcttt ccagagagcg gaacaggcga ggaaaagtag tcccttctcg gcgattctgc      960

ggagggatct ccgtggggcg gtgaacgccg atgatgcctc tactaaccat gttcatgttt     1020

tctttttttt tctacaggtc ctgggtgacg aacag                                1055


<210> 4
<211> 961
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 4
cctcagatct gaattcggta ccctagttat taatagtaat caattacggg gtcattagtt       60

catagcccat atatggagtt ccgcgttaca taacttacgg taaatggccc gcctggctga      120

ccgcccaacg acccccgccc attgacgtca ataatgacgt atgttcccat agtaacgcca      180

atagggactt tccattgacg tcaatgggtg gactatttac ggtaaactgc ccacttggca      240

gtacatcaag tgtatcatat gccaagtacg ccccctattg acgtcaatga cggtaaatgg      300

cccgcctggc attatgccca gtacatgacc ttatgggact ttcctacttg gcagtacatc      360

tacgtattag tcatcgctat taccatggtc gaggtgagcc ccacgttctg cttcactctc      420

cccatctccc ccccctcccc acccccaatt ttgtatttat ttatttttta attattttgt      480

gcagcgatgg gggcgggggg gggggggggg cgcgcgccag gcggggcggg gcggggcgag      540

gggcggggcg gggcgaggcg gagaggtgcg gcggcagcca atcagagcgg cgcgctccga      600

aagtttcctt ttatggcgag gcggcggcgg cggcggccct ataaaaagcg aagcgcgcgg      660

cgggcgggag tcgctgcgac gctgccttcg ccccgtgccc cgctccgccg ccgcctcgcg      720

ccgcccgccc cggctctgac tgaccgcgtt actcccacag gtgagcgggc gggacggccc      780

ttctcctccg ggctgtaatt agcgcttggt ttaatgacgg cttgtttctt ttctgtggct      840

gcgtgaaagc cttgaggggc tccgggagct agagcctctg ctaaccatgt tcatgccttc      900

ttctttttcc tacagctcct gggcaacgtg ctggttattg tgctgtctca tcattttggc      960

a                                                                      961


<210> 5
<211> 1675
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 5
gtctgcaagc agacctggca gcattgggct ggccgccccc cagggcctcc tcttcatgcc       60

cagtgaatga ctcaccttgg cacagacaca atgttcgggg tgggcacagt gcctgcttcc      120

cgccgcaccc cagcccccct caaatgcctt ccgagaagcc cattgagtag ggggcttgca      180

ttgcacccca gcctgacagc ctggcatctt gggataaaag cagcacagcc ccctaggggc      240

tgcccttgct gtgtggcgcc accggcggtg gagaacaagg ctctattcag cctgtgccca      300

ggaaagggga tcaggggatg cccaggcatg gacagtgggt ggcagggggg gagaggaggg      360

ctgtctgctt cccagaagtc caaggacaca aatgggtgag gggactgggc agggttctga      420

ccctgtggga ccagagtgga gggcgtagat ggacctgaag tctccaggga caacagggcc      480

caggtctcag gctcctagtt gggcccagtg gctccagcgt ttccaaaccc atccatcccc      540

agaggttctt cccatctctc caggctgatg tgtgggaact cgaggaaata aatctccagt      600

gggagacgga ggggtggcca gggaaacggg gcgctgcagg aataaagacg agccagcaca      660

gccagctcat gcgtaacggc tttgtggagc tgtcaaggcc tggtctctgg gagagaggca      720

cagggaggcc agacaaggaa ggggtgacct ggagggacag atccaggggc taaagtcctg      780

ataaggcaag agagtgccgg ccccctcttg ccctatcagg acctccactg ccacatagag      840

gccatgattg acccttagac aaagggctgg tgtccaatcc cagcccccag ccccagaact      900

ccagggaatg aatgggcaga gagcaggaat gtgggacatc tgtgttcaag ggaaggactc      960

caggagtctg ctgggaatga ggcctagtag gaaatgaggt ggcccttgag ggtacagaac     1020

aggttcattc ttcgccaaat tcccagcacc ttgcaggcac ttacagctga gtgagataat     1080

gcctgggtta tgaaatcaaa aagttggaaa gcaggtcaga ggtcatctgg tacagccctt     1140

ccttcccttt tttttttttt tttttttttg tgagacaagg tctctctctg ttgcccaggc     1200

tggagtggcg caaacacagc tcactgcagc ctcaacctac tgggctcaag caatcctcca     1260

gcctcagcct cccaaagtgc tgggattaca agcatgagcc accccactca gccctttcct     1320

tcctttttaa ttgatgcata ataattgtaa gtattcatca tggtccaacc aaccctttct     1380

tgacccacct tcctagagag agggtcctct tgattcagcg gtcagggccc cagacccatg     1440

gtctggctcc aggtaccacc tgcctcatgc aggagttggc gtgcccagga agctctgcct     1500

ctgggcacag tgacctcagt ggggtgaggg gagctctccc catagctggg ctgcggccca     1560

accccacccc ctcaggctat gccagggggt gttgccaggg gcacccgggc atcgccagtc     1620

tagcccactc cttcataaag ccctcgcatc ccaggagcga gcagagccag agcat          1675


<210> 6
<211> 1000
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 6
ctcataaatg ccaagtcctc tcgcactatg cggagtacag aggacaacga ccacagccat       60

ccctgaaccc cgcccacggc acagcgccgg agccggggtc tggggcgccg cttcctgggg      120

ggtcccgact ctcagccgcc cccgcttcac ccgggccgcc aaggggctgg gggaggcggc      180

gctcggggta accgggggag actcagggcg ctgggggcac ttggggaact catgggggct      240

caaaggaact aggagatcgg gacctcgaag gggacttggg gggttcgggg ctttcggggg      300

cggtcggggg ttcgcggacc cgggaagctc tgaggaccca gaggccgggc gcgctccgcc      360

cgcggcgccg ccccctccgt aactttccca gtctccgagg gaagaggcgg ggtgtggggt      420

gcggttaaaa ggcgccacgg cgggagacag gtgttgcggc cccgcagcgc ccgcgcgctc      480

ctctccccga ctcggagccc ctcggcggcg cccggcccag gacccgccta ggagcgcagg      540

agccccagcg cagagacccc aacgccgaga cccccgcccc ggccccgccg cgcttcctcc      600

cgacgcaggt gagcccgccg gccccggact gcccggccag gaacctggcg cggggaggga      660

ccgcgagacc cagagcggtt gcccggccgc gtgggtctcg gggaaccggg gggctggacc      720

aacacacgtc cttgggccgg ggggcggggg ccgccttctg gagcgggcgt ttctgcggcc      780

gagctccgga gctggaatgg ggcggccggg gaagtggacg cgatggcacc gcccggggtg      840

cgagtggggc cgggcgcgcg cgggagggga aaaaggcgcg ggcgagccgc cagcgcgagg      900

tttgtggtgt cgccgatgtc ccttcggggt actctagcgc agccgcctgg ctacttgacc      960

cactgccacc aaacgtttta aattcaccga aagcttagct                           1000


<210> 7
<211> 143
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 7
ttggccactc cctctctgcg cgctcgctcg ctcactgagg ccgggcgacc aaaggtcgcc       60

cgacgcccgg gctttgcccg ggcggcctca gtgagcgagc gagcgcgcag agagggagtg      120

gccaactcca tcactagggg ttc                                              143


<210> 8
<211> 143
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 8
aaccggtgag ggagagacgc gcgagcgagc gagtgactcc ggcccgctgg tttccagcgg       60

gctgcgggcc cgaaacgggc ccgccggagt cactcgctcg ctcgcgcgtc tctccctcac      120

cggttgaggt agtgatcccc aag                                              143


<210> 9
<211> 106
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 9
gacgcgcgag cgagcgagtg actccggcgg gcccgtttcg ggcccgcagc ccgctggaaa       60

ccagcgggcc ggagtcactc gctcgctcgc gcgtctctcc ctcacc                     106


<210> 10
<211> 678
<212> DNA
<213> Homo sapiens

<400> 10
atggattggg gcacgctgca gacgatcctg gggggtgtga acaaacactc caccagcatt       60

ggaaagatct ggctcaccgt cctcttcatt tttcgcatta tgatcctcgt tgtggctgca      120

aaggaggtgt ggggagatga gcaggccgac tttgtctgca acaccctgca gccaggctgc      180

aagaacgtgt gctacgatca ctacttcccc atctcccaca tccggctatg ggccctgcag      240

ctgatcttcg tgtccacgcc agcgctccta gtggccatgc acgtggccta ccggagacat      300

gagaagaaga ggaagttcat caagggggag ataaagagtg aatttaagga catcgaggag      360

atcaaaaccc agaaggtccg catcgaaggc tccctgtggt ggacctacac aagcagcatc      420

ttcttccggg tcatcttcga agccgccttc atgtacgtct tctatgtcat gtacgacggc      480

ttctccatgc agcggctggt gaagtgcaac gcctggcctt gtcccaacac tgtggactgc      540

tttgtgtccc ggcccacgga gaagactgtc ttcacagtgt tcatgattgc agtgtctgga      600

atttgcatcc tgctgaatgt cactgaattg tgttatttgc taattagata ttgttctggg      660

aagtcaaaaa agccagtt                                                    678


<210> 11
<211> 678
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 11
atggactggg gcaccctgca gactatcctg gggggcgtca ataagcattc aactagcatc       60

ggaaagattt ggctgactgt cctgtttatc tttcggatca tgatcctggt ggtggcagca      120

aaggaagtgt ggggcgacga gcaggccgat ttcgtgtgca acacactgca gccaggctgc      180

aagaacgtgt gctacgacca ctattttccc atctctcaca tcaggctgtg ggccctgcag      240

ctgatcttcg tgagcacccc tgccctgctg gtggcaatgc acgtggccta tcggagacac      300

gagaagaagc gcaagtttat caagggcgag atcaagagcg agttcaagga tatcgaggag      360

atcaagacac agaaggtgag gatcgagggc tccctgtggt ggacctacac aagctccatc      420

ttctttcgcg tgatcttcga ggccgccttt atgtacgtgt tctatgtgat gtacgacggc      480

ttttctatgc agcggctggt gaagtgcaac gcctggccct gtcctaatac agtggattgt      540

ttcgtgtcca gacccaccga gaagacagtg ttcaccgtgt ttatgatcgc cgtgtctggc      600

atctgcatcc tgctgaacgt gaccgagctg tgctatctgc tgatccggta ctgtagtgga      660

aagagcaaaa aacccgtg                                                    678


<210> 12
<211> 678
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 12
atggactggg gaacattgca aactattttg ggaggagtca acaagcattc aactagcatc       60

gggaagatct ggctgaccgt gctgttcatc tttcgcatca tgattctcgt ggtggccgct      120

aaggaagtct ggggcgatga acaggccgac ttcgtgtgta acacgctgca gcccggttgc      180

aaaaacgtct gctacgatca ctacttcccc atctcacaca ttagactgtg ggcgctgcag      240

ctgattttcg tgtccacccc ggcacttctt gtggcgatgc acgtggccta ccggcggcac      300

gagaagaaaa ggaagttcat taagggcgaa atcaagtccg agttcaagga catcgaagaa      360

atcaagaccc agaaggtccg cattgagggc tccctctggt ggacctacac ctcgtccatc      420

ttcttccggg tcatattcga ggccgccttt atgtacgtgt tttacgtgat gtacgacggt      480

ttcagcatgc aaagactcgt caagtgcaac gcttggcctt gccccaatac cgtggattgc      540

ttcgtgtccc gcccgaccga gaaaactgtg ttcactgtgt tcatgatcgc cgtgtccggc      600

atctgcatcc tgctgaacgt gaccgagctg tgctatctcc tgatccggta ctgtagcgga      660

aagtcgaaga agcctgtg                                                    678


<210> 13
<211> 678
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 13
atggattggg ggacgctcca gactatactt ggcggggtaa acaaacattc cacctcaatt       60

ggcaaaatct ggctcacagt cctcttcatc ttcagaataa tgatactcgt ggttgccgct      120

aaagaagttt ggggtgacga gcaagccgat ttcgtctgta acaccctcca accaggttgc      180

aaaaatgtct gttacgatca ctactttcct attagccata ttagactctg ggccctgcaa      240

cttatcttcg tttccactcc tgctctgctc gtcgctatgc acgttgccta tcgccgccat      300

gaaaaaaaac ggaaattcat taagggagag attaagagtg aattcaagga tattgaagag      360

attaaaacgc aaaaagttag aattgaggga tcactgtggt ggacttatac cagtagcatc      420

ttttttaggg tcattttcga agctgctttc atgtatgttt tctatgtaat gtacgacggt      480

ttctccatgc aacgcttggt taaatgtaac gcctggccat gccctaatac ggttgattgc      540

tttgtctccc gccctactga aaagacagtg tttaccgttt tcatgatcgc cgtaagtgga      600

atttgtatcc ttcttaacgt gaccgagttg tgctatctcc ttattcgcta ctgttcagga      660

aaaagtaaaa aaccagta                                                    678


<210> 14
<211> 27
<212> DNA
<213> Human influenza virus

<400> 14
tacccatacg atgttccaga ttacgct                                           27


<210> 15
<211> 589
<212> DNA
<213> Woodchuck hepatitis virus

<400> 15
aatcaacctc tggattacaa aatttgtgaa agattgactg gtattcttaa ctatgttgct       60

ccttttacgc tatgtggata cgctgcttta atgcctttgt atcatgctat tgcttcccgt      120

atggctttca ttttctcctc cttgtataaa tcctggttgc tgtctcttta tgaggagttg      180

tggcccgttg tcaggcaacg tggcgtggtg tgcactgtgt ttgctgacgc aacccccact      240

ggttggggca ttgccaccac ctgtcagctc ctttccggga ctttcgcttt ccccctccct      300

attgccacgg cggaactcat cgccgcctgc cttgcccgct gctggacagg ggctcggctg      360

ttgggcactg acaattccgt ggtgttgtcg gggaaatcat cgtcctttcc ttggctgctc      420

gcctgtgttg ccacctggat tctgcgcggg acgtccttct gctacgtccc ttcggccctc      480

aatccagcgg accttccttc ccgcggcctg ctgccggctc tgcggcctct tccgcgtctt      540

cgccttcgcc ctcagacgag tcggatctcc ctttgggccg cctccccgc                  589


<210> 16
<211> 122
<212> DNA
<213> Simian virus 40

<400> 16
taagatacat tgatgagttt ggacaaacca caactagaat gcagtgaaaa aaatgcttta       60

tttgtgaaat ttgtgatgct attgctttat ttgtaaccat tataagctgc aataaacaag      120

tt                                                                     122


<210> 17
<211> 208
<212> DNA
<213> Simian virus 40

<400> 17
ctgtgccttc tagttgccag ccatctgttg tttgcccctc ccccgtgcct tccttgaccc       60

tggaaggtgc cactcccact gtcctttcct aataaaatga ggaaattgca tcgcattgtc      120

tgagtaggtg tcattctatt ctggggggtg gggtggggca ggacagcaag ggggaggatt      180

gggaagacaa tagcaggcat gctgggga                                         208


<210> 18
<211> 681
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 18
atggactggg gcacgctgca gactatcctg gggggtgtca acaagcattc aactagcatc       60

ggaaagatct ggctgaccgt cctgttcatc tttcgcatca tgatcctcgt ggtggccgct      120

aaggaagtgt ggggcgacga gcaggccgat ttcgtgtgta acaccctgca gccaggttgc      180

aaaaacgtct gctacgatca ctactttccc atctcccaca ttagactgtg ggccctgcag      240

ctgatcttcg tgtccacccc tgcgctgcta gtggccatgc acgtggccta tcggcgacac      300

gagaagaaac ggaagttcat taagggcgag atcaagagcg agttcaagga tatcgaagag      360

atcaagaccc agaaggtccg cattgagggc tccctgtggt ggacctacac cagctccatc      420

ttctttcggg tcatcttcga ggccgccttt atgtacgtgt tctatgtgat gtacgacggt      480

ttctccatgc aacggctggt gaagtgcaac gcctggcctt gccctaatac tgtggattgc      540

ttcgtgtccc gccccaccga gaagacagtg ttcaccgtgt tcatgatcgc cgtgtctggc      600

atctgcatcc tgctgaacgt gaccgagctg tgctatctcc tgatccggta ctgtagtgga      660

aagtcaaaaa aaccagtgta a                                                681


<210> 19
<211> 226
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polypeptide

<400> 19
Met Asp Trp Gly Thr Leu Gln Thr Ile Leu Gly Gly Val Asn Lys His 
1               5                   10                  15      


Ser Thr Ser Ile Gly Lys Ile Trp Leu Thr Val Leu Phe Ile Phe Arg 
            20                  25                  30          


Ile Met Ile Leu Val Val Ala Ala Lys Glu Val Trp Gly Asp Glu Gln 
        35                  40                  45              


Ala Asp Phe Val Cys Asn Thr Leu Gln Pro Gly Cys Lys Asn Val Cys 
    50                  55                  60                  


Tyr Asp His Tyr Phe Pro Ile Ser His Ile Arg Leu Trp Ala Leu Gln 
65                  70                  75                  80  


Leu Ile Phe Val Ser Thr Pro Ala Leu Leu Val Ala Met His Val Ala 
                85                  90                  95      


Tyr Arg Arg His Glu Lys Lys Arg Lys Phe Ile Lys Gly Glu Ile Lys 
            100                 105                 110         


Ser Glu Phe Lys Asp Ile Glu Glu Ile Lys Thr Gln Lys Val Arg Ile 
        115                 120                 125             


Glu Gly Ser Leu Trp Trp Thr Tyr Thr Ser Ser Ile Phe Phe Arg Val 
    130                 135                 140                 


Ile Phe Glu Ala Ala Phe Met Tyr Val Phe Tyr Val Met Tyr Asp Gly 
145                 150                 155                 160 


Phe Ser Met Gln Arg Leu Val Lys Cys Asn Ala Trp Pro Cys Pro Asn 
                165                 170                 175     


Thr Val Asp Cys Phe Val Ser Arg Pro Thr Glu Lys Thr Val Phe Thr 
            180                 185                 190         


Val Phe Met Ile Ala Val Ser Gly Ile Cys Ile Leu Leu Asn Val Thr 
        195                 200                 205             


Glu Leu Cys Tyr Leu Leu Ile Arg Tyr Cys Ser Gly Lys Ser Lys Lys 
    210                 215                 220                 


Pro Val 
225     


<210> 20
<211> 7
<212> PRT
<213> Adeno-associated virus

<400> 20
Leu Gly Glu Thr Thr Arg Pro 
1               5           


<210> 21
<211> 11
<212> PRT
<213> Adeno-associated virus

<400> 21
Pro Ser Gly Thr Thr Thr Gln Ser Arg Leu Gln 
1               5                   10      


<210> 22
<211> 11
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 22
Ala Ser Gly Asn Val Thr Gln Ser Thr Leu Gln 
1               5                   10      


<210> 23
<211> 5
<212> PRT
<213> Adeno-associated virus

<400> 23
Lys Asp Asp Glu Glu 
1               5   


<210> 24
<211> 5
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 24
Arg Asp Asp Asp Asp 
1               5   


<210> 25
<211> 5
<212> PRT
<213> Adeno-associated virus

<400> 25
Lys Thr Ser Ala Asp 
1               5   


<210> 26
<211> 5
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 26
Thr Thr Pro Ala Asp 
1               5   


<210> 27
<211> 5
<212> PRT
<213> Adeno-associated virus

<400> 27
Lys Gln Asp Ala Glu 
1               5   


<210> 28
<211> 5
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 28
Lys Gln Asp Gly Glu 
1               5   


<210> 29
<211> 12
<212> PRT
<213> Adeno-associated virus

<400> 29
Gln Gly Ser Glu Lys Thr Asn Val Asp Ile Glu Lys 
1               5                   10          


<210> 30
<211> 12
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 30
Glu Asp Ala Thr Glu Asn Asn Ile Asp Ile Asp Arg 
1               5                   10          


<210> 31
<211> 12
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 31
Gln Ser Ala Ala Gly Ala Asp Val Ala Ile Asp Ser 
1               5                   10          


<210> 32
<211> 5
<212> PRT
<213> Adeno-associated virus

<400> 32
Asp Gly Glu Asp Phe 
1               5   


<210> 33
<211> 681
<212> DNA
<213> Homo sapiens

<400> 33
atggattggg gcacgctgca gacgatcctg gggggtgtga acaaacactc caccagcatt       60

ggaaagatct ggctcaccgt cctcttcatt tttcgcatta tgatcctcgt tgtggctgca      120

aaggaggtgt ggggagatga gcaggccgac tttgtctgca acaccctgca gccaggctgc      180

aagaacgtgt gctacgatca ctacttcccc atctcccaca tccggctatg ggccctgcag      240

ctgatcttcg tgtccacgcc agcgctccta gtggccatgc acgtggccta ccggagacat      300

gagaagaaga ggaagttcat caagggggag ataaagagtg aatttaagga catcgaggag      360

atcaaaaccc agaaggtccg catcgaaggc tccctgtggt ggacctacac aagcagcatc      420

ttcttccggg tcatcttcga agccgccttc atgtacgtct tctatgtcat gtacgacggc      480

ttctccatgc agcggctggt gaagtgcaac gcctggcctt gtcccaacac tgtggactgc      540

tttgtgtccc ggcccacgga gaagactgtc ttcacagtgt tcatgattgc agtgtctgga      600

atttgcatcc tgctgaatgt cactgaattg tgttatttgc taattagata ttgttctggg      660

aagtcaaaaa agccagttta a                                                681


<210> 34
<211> 681
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 34
atggattggg ggacgctcca gactatactt ggcggggtaa acaaacattc cacctcaatt       60

ggcaaaatct ggctcacagt cctcttcatc ttcagaataa tgatactcgt ggttgccgct      120

aaagaagttt ggggtgacga gcaagccgat ttcgtctgta acaccctcca accaggttgc      180

aaaaatgtct gttacgatca ctactttcct attagccata ttagactctg ggccctgcaa      240

cttatcttcg tttccactcc tgctctgctc gtcgctatgc acgttgccta tcgccgccat      300

gaaaaaaaac ggaaattcat taagggagag attaagagtg aattcaagga tattgaagag      360

attaaaacgc aaaaagttag aattgaggga tcactgtggt ggacttatac cagtagcatc      420

ttttttaggg tcattttcga agctgctttc atgtatgttt tctatgtaat gtacgacggt      480

ttctccatgc aacgcttggt taaatgtaac gcctggccat gccctaatac ggttgattgc      540

tttgtctccc gccctactga aaagacagtg tttaccgttt tcatgatcgc cgtaagtgga      600

atttgtatcc ttcttaacgt gaccgagttg tgctatctcc ttattcgcta ctgttcagga      660

aaaagtaaaa aaccagtata a                                                681


<210> 35
<211> 440
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide


<220>
<221> modified_base
<222> (36)..(36)
<223> a, c, t, or g

<220>
<221> modified_base
<222> (264)..(264)
<223> a, c, t, or g 

<220>
<221> modified_base
<222> (270)..(270)
<223> a, c, t, or g 

<220>
<221> modified_base
<222> (276)..(276)
<223> a, c, t, or g 

<400> 35
atggaytggg gvacvctgca gactathctg ggvggngtva acaarcattc macyagcaty       60

ggvaagatct ggctsachgt cctsttcatc tttcgvatha tgathctcgt ggtggchgcw      120

aaggaagtbt gggghgayga gcaggccgay ttcgtstgya acacvctgca gccaggytgc      180

aaraacgtst gctacgatca ctacttyccc atctchcaca tyagrctvtg ggccctgcag      240

ctgatcttcg tgtccacbcc dgcnctbctn gtggcnatgc acgtggccta ycggmgvcay      300

gagaagaarm ggaagttcat yaagggvgag athaagagyg arttcaagga yatcgargag      360

atcaaracvc agaaggtbmg vatygagggc tccctgtggt ggacctacac magbwscatc      420

ttcttycggg tcathttcga                                                  440


<210> 36
<211> 440
<212> DNA
<213> Homo sapiens

<400> 36
atggattggg gcacgctgca gacgatcctg gggggtgtga acaaacactc caccagcatt       60

ggaaagatct ggctcaccgt cctcttcatt tttcgcatta tgatcctcgt tgtggctgca      120

aaggaggtgt ggggagatga gcaggccgac tttgtctgca acaccctgca gccaggctgc      180

aagaacgtgt gctacgatca ctacttcccc atctcccaca tccggctatg ggccctgcag      240

ctgatcttcg tgtccacgcc agcgctccta gtggccatgc acgtggccta ccggagacat      300

gagaagaaga ggaagttcat caagggggag ataaagagtg aatttaagga catcgaggag      360

atcaaaaccc agaaggtccg catcgaaggc tccctgtggt ggacctacac aagcagcatc      420

ttcttccggg tcatcttcga                                                  440


<210> 37
<211> 440
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 37
atggactggg gcaccctgca gactatcctg gggggcgtca ataagcattc aactagcatc       60

ggaaagattt ggctgactgt cctgtttatc tttcggatca tgatcctggt ggtggcagca      120

aaggaagtgt ggggcgacga gcaggccgat ttcgtgtgca acacactgca gccaggctgc      180

aagaacgtgt gctacgacca ctattttccc atctctcaca tcaggctgtg ggccctgcag      240

ctgatcttcg tgagcacccc tgccctgctg gtggcaatgc acgtggccta tcggagacac      300

gagaagaagc gcaagtttat caagggcgag atcaagagcg agttcaagga tatcgaggag      360

atcaagacac agaaggtgag gatcgagggc tccctgtggt ggacctacac aagctccatc      420

ttctttcgcg tgatcttcga                                                  440


<210> 38
<211> 440
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 38
atggactggg gaacattgca aactattttg ggaggagtca acaagcattc aactagcatc       60

gggaagatct ggctgaccgt gctgttcatc tttcgcatca tgattctcgt ggtggccgct      120

aaggaagtct ggggcgatga acaggccgac ttcgtgtgta acacgctgca gcccggttgc      180

aaaaacgtct gctacgatca ctacttcccc atctcacaca ttagactgtg ggcgctgcag      240

ctgattttcg tgtccacccc ggcacttctt gtggcgatgc acgtggccta ccggcggcac      300

gagaagaaaa ggaagttcat taagggcgaa atcaagtccg agttcaagga catcgaagaa      360

atcaagaccc agaaggtccg cattgagggc tccctctggt ggacctacac ctcgtccatc      420

ttcttccggg tcatattcga                                                  440


<210> 39
<211> 440
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 39
atggattggg ggacgctcca gactatactt ggcggggtaa acaaacattc cacctcaatt       60

ggcaaaatct ggctcacagt cctcttcatc ttcagaataa tgatactcgt ggttgccgct      120

aaagaagttt ggggtgacga gcaagccgat ttcgtctgta acaccctcca accaggttgc      180

aaaaatgtct gttacgatca ctactttcct attagccata ttagactctg ggccctgcaa      240

cttatcttcg tttccactcc tgctctgctc gtcgctatgc acgttgccta tcgccgccat      300

gaaaaaaaac ggaaattcat taagggagag attaagagtg aattcaagga tattgaagag      360

attaaaacgc aaaaagttag aattgaggga tcactgtggt ggacttatac cagtagcatc      420

ttttttaggg tcattttcga                                                  440


<210> 40
<211> 320
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 40
acggtttctc catgcaacgg ctggtgaagt gcaacgcctg gccttgccct aatactgtgg       60

attgcttcgt gtcccgcccc accgagaaga cagtgttcac cgtgttcatg atcgccgtgt      120

ctggcatctg catcctgctg aacgtgaccg agctgtgcta tctcctgatc cggtactgta      180

gtggaaagtc aaaaaaacca gtggactaca aagaccatga cggtgattat aaagatcatg      240

atatcgatta caaggatgac gatgacaagt aaggatccta atcaacctct ggattacaaa      300

atttgtgaaa gattgactgg                                                  320


<210> 41
<211> 22
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 41
Asp Tyr Lys Asp His Asp Gly Asp Tyr Lys Asp His Asp Ile Asp Tyr 
1               5                   10                  15      


Lys Asp Asp Asp Asp Lys 
            20          


<210> 42
<211> 83
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 42
tgctatggat ccatcatgat ctttataatc accgtcatgg tctttgtagt ccactggttt       60

ttttgacttt ccactacagt acc                                               83


<210> 43
<211> 74
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 43
tgctatggat ccttacttgt catcgtcatc cttgtaatcg atatcatgat ctttataatc       60

accgtcatgg tctt                                                         74


