                         SEQUENCE LISTING

<110>  ASC Therapeutics Inc.
 
<120>  Methods and compositions for treating thalassemia or sickle cell 
       disease

<130>  044903-8026WO01

<160>  65    

<170>  PatentIn version 3.5

<210>  1
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  1
gtaacggcag acttctcctc agg                                               23


<210>  2
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  2
guaacggcag acuucuccuc                                                   20


<210>  3
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  3
uaacggcaga cuucuccuc                                                    19


<210>  4
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  4
aacggcagac uucuccuc                                                     18


<210>  5
<211>  17
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  5
acggcagacu ucuccuc                                                      17


<210>  6
<211>  16
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  6
cggcagacuu cuccuc                                                       16


<210>  7
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  7
ggcagacuuc uccuc                                                        15


<210>  8
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  8
gtaacggcag acttctccac agg                                               23


<210>  9
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  9
guaacggcag acuucuccac                                                   20


<210>  10
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  10
uaacggcaga cuucuccac                                                    19


<210>  11
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  11
aacggcagac uucuccac                                                     18


<210>  12
<211>  17
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  12
acggcagacu ucuccac                                                      17


<210>  13
<211>  16
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  13
cggcagacuu cuccac                                                       16


<210>  14
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  14
ggcagacuuc uccac                                                        15


<210>  15
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  15
cacaggagtc agatgcacca tgg                                               23


<210>  16
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  16
cacaggaguc agaugcacca                                                   20


<210>  17
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  17
acaggaguca gaugcacca                                                    19


<210>  18
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  18
caggagucag augcacca                                                     18


<210>  19
<211>  17
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  19
aggagucaga ugcacca                                                      17


<210>  20
<211>  16
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  20
ggagucagau gcacca                                                       16


<210>  21
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  21
gagucagaug cacca                                                        15


<210>  22
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  22
gcaacctcaa acagacacca tgg                                               23


<210>  23
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  23
gcaaccucaa acagacacca                                                   20


<210>  24
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  24
caaccucaaa cagacacca                                                    19


<210>  25
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  25
aaccucaaac agacacca                                                     18


<210>  26
<211>  17
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  26
accucaaaca gacacca                                                      17


<210>  27
<211>  16
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  27
ccucaaacag acacca                                                       16


<210>  28
<211>  15
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  28
cucaaacaga cacca                                                        15


<210>  29
<211>  27
<212>  DNA
<213>  Homo sapiens

<400>  29
tttgcttctg acacaactgt gttcact                                           27


<210>  30
<211>  23
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  30
cuucugacac aacuguguuc acu                                               23


<210>  31
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  31
cuucugacac aacuguguuc ac                                                22


<210>  32
<211>  21
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  32
cuucugacac aacuguguuc a                                                 21


<210>  33
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  33
cuucugacac aacuguguuc                                                   20


<210>  34
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  34
cuucugacac aacuguguu                                                    19


<210>  35
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  35
cuucugacac aacugugu                                                     18


<210>  36
<211>  27
<212>  DNA
<213>  Homo sapiens

<400>  36
tttgaggttg ctagtgaaca cagttgt                                           27


<210>  37
<211>  23
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  37
agguugcuag ugaacacagu ugu                                               23


<210>  38
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  38
agguugcuag ugaacacagu ug                                                22


<210>  39
<211>  21
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  39
agguugcuag ugaacacagu u                                                 21


<210>  40
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  40
agguugcuag ugaacacagu                                                   20


<210>  41
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  41
agguugcuag ugaacacag                                                    19


<210>  42
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  42
agguugcuag ugaacaca                                                     18


<210>  43
<211>  27
<212>  DNA
<213>  Homo sapiens

<400>  43
tttaaggaga ccaatagaaa ctgggca                                           27


<210>  44
<211>  23
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  44
aggagaccaa uagaaacugg gca                                               23


<210>  45
<211>  27
<212>  DNA
<213>  Homo sapiens

<400>  45
tttctattgg tctccttaaa cctgtct                                           27


<210>  46
<211>  23
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  46
uauuggucuc cuuaaaccug ucu                                               23


<210>  47
<211>  27
<212>  DNA
<213>  Homo sapiens

<400>  47
tttctgatag gcactgactc tctctgc                                           27


<210>  48
<211>  23
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  48
ugauaggcac ugacucucuc ugc                                               23


<210>  49
<211>  22
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  49
ugauaggcac ugacucucuc ug                                                22


<210>  50
<211>  21
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  50
ugauaggcac ugacucucuc u                                                 21


<210>  51
<211>  20
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  51
ugauaggcac ugacucucuc                                                   20


<210>  52
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  52
ugauaggcac ugacucucu                                                    19


<210>  53
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  53
ugauaggcac ugacucuc                                                     18


<210>  54
<211>  36
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic


<220>
<221>  misc_feature
<222>  (1)..(20)
<223>  n can be a, u, g or c.

<400>  54
nnnnnnnnnn nnnnnnnnnn guuuuagagc uaugcu                                 36


<210>  55
<211>  67
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  55
agcauagcaa guuaaaauaa ggcuaguccg uuaucaacuu gaaaaagugg caccgagucg       60

gugcuuu                                                                 67


<210>  56
<211>  99
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic


<220>
<221>  misc_feature
<222>  (1)..(20)
<223>  n can be a, u, g or c.

<400>  56
nnnnnnnnnn nnnnnnnnnn guuuuagagc uagaaauagc aaguuaaaau aaggcuaguc       60

cguuaucaac uugaaaaagu ggcaccgagu cggugcuuu                              99


<210>  57
<211>  43
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic


<220>
<221>  misc_feature
<222>  (21)..(43)
<223>  n can be a, u, g or c.

<400>  57
uaauuucuac ucuuguagau nnnnnnnnnn nnnnnnnnnn nnn                         43


<210>  58
<211>  185
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  58
cagggcagag ccatctattg cttacatttg cttctgacac aactgtgttc actagcaacc       60

tcaaacagac accatggtgc atctgactcc tgtggaaaag tctgccgtta ctgccctgtg      120

gggcaaggtg aacgtggatg aagttggtgg tgaggccctg ggcaggttgg tatcaaggtt      180

acaag                                                                  185


<210>  59
<211>  23
<212>  RNA
<213>  Homo sapiens

<400>  59
aggaguggac agauccccaa agg                                               23


<210>  60
<211>  21
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  60
aggaguggac agauccccaa a                                                 21


<210>  61
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  61
cttgccccac agggcagtaa cgg                                               23


<210>  62
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  62
cuugccccac agggcaguaa                                                   20


<210>  63
<211>  185
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  63
cagggcagag ccatctattg cttacatttg cttctgacac aactgtgttc actagcaacc       60

tcaaacagac accatggtgc atctgactcc tgaggagaag tctgccgtta ctgccctgtg      120

gggcaaggtg aacgtggatg aagttggtgg tgaggccctg ggcaggttgg tatcaaggtt      180

acaag                                                                  185


<210>  64
<211>  185
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  64
attgcttaca tttgcttctg acacaactgt gttcactagc aacctcaaac agacaccatg       60

gtgcatctga ctcctgagga gaagtctgcc gtcactgccc tgtggggcaa ggtgaacgtg      120

gatgaagttg gtggtgaggc cctgggcagg ttggtatcaa ggttacaaga caggtttaag      180

gagac                                                                  185


<210>  65
<211>  1581
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic

<400>  65
gcagagagag tcagtgccta tcagaaatct ctctgcctat tggtctattt tcccaccctt       60

agctggaagc ggagctacta acttcagcct gctgaagcag gctggagacg tggaggagaa      120

ccctggagtg catctgactc ctgaggagaa gtctgccgtt actgccctgt ggggcaaggt      180

gaacgtggat gaagttggtg gtgaggccct gggcaggctg ctggtggtct acccttggac      240

ccagaggttc tttgagtcct ttggggatct gtccactcct gatgctgtta tgggcaaccc      300

taaggtgaag gctcatggca agaaagtgct cggtgccttt agtgatggcc tggctcacct      360

ggacaacctc aagggcacct ttgccacact gagtgagctg cactgtgaca agctgcacgt      420

ggatcctgag aacttcaggg tgagtctatg ggacgcttga tgttttcttt ccccttcttt      480

tctatggtta agttcatgtc ataggaaggg gataagtaac agggtacagt ttagaatggg      540

aaacagacga atgattgcat cagtgtggaa gtctcaggat cgttttagtt tcttttattt      600

gctgttcata acaattgttt tcttttgttt aattcttgct ttcttttttt ttcttctccg      660

caatttttac tattatactt aatgccttaa cattgtgtat aacaaaagga aatatctctg      720

agatacatta agtaacttaa aaaaaaactt tacacagtct gcctagtaca ttactatttg      780

gaatatatgt gtgcttattt gcatattcat aatctcccta ctttattttc ttttattttt      840

aattgataca taatcattat acatatttat gggttaaagt gtaatgtttt aatatgtgta      900

cacatattga ccaaatcagg gtaattttgc atttgtaatt ttaaaaaatg ctttcttctt      960

ttaatatact tttttgttta tcttatttct aatactttcc ctaatctctt tctttcaggg     1020

caataatgat acaatgtatc atgcctcttt gcaccattct aaagaataac agtgataatt     1080

tctgggttaa ggcaatagca atatctctgc atataaatat ttctgcatat aaattgtaac     1140

tgatgtaaga ggtttcatat tgctaatagc agctacaatc cagctaccat tctgctttta     1200

ttttatggtt gggataaggc tggattattc tgagtccaag ctaggccctt ttgctaatca     1260

tgttcatacc tcttatcttc ctcccacagc tcctgggcaa cgtgctggtc tgtgtgctgg     1320

cccatcactt tggcaaagaa ttcaccccac cagtgcaggc tgcctatcag aaagtggtgg     1380

ctggtgtggc taatgccctg gcccacaagt atcactaagc tcgctttctt gctgtccaat     1440

ttctattaaa ggttcctttg ttccctaagt ccaactacta aactggggga tattatgaag     1500

ggccttgagc atctggattc tgcctaataa aaaacattta ttttcattgc aatggcagag     1560

agagtcagtg cctatcagaa a                                               1581


