                               SEQUENCE LISTING

<110> SKYHAWK THERAPEUTICS, INC.
 
<120> METHODS FOR MODULATING SPLICING

<130> 51503-708.601

<140> PCT/US2020/037910
<141> 2020-06-16

<150> 16/813,069
<151> 2020-03-09

<150> 62/862,468
<151> 2019-06-17

<160> 21    

<170> PatentIn version 3.5

<210> 1
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 1
aaaagaguaa gauuauau                                                     18


<210> 2
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 2
aucaugguga ggccccau                                                     18


<210> 3
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 3
uuacaggugu gagccacc                                                     18


<210> 4
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 4
aacagaguaa gcaggagu                                                     18


<210> 5
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 5
ugaugaguaa gagaguua                                                     18


<210> 6
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 6
aauagaguaa gauuauau                                                     18


<210> 7
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 7
aggagaguaa gaggaggg                                                     18


<210> 8
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 8
gacuaaguau uugaagag                                                     18


<210> 9
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 9
gacagaguaa gaugaaaa                                                     18


<210> 10
<211> 18
<212> DNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<220>
<221> source
<223> /note="Description of Combined DNA/RNA Molecule: Unknown 
      splice site sequence"

<400> 10
tcaagaguaa gaauugau                                                     18


<210> 11
<211> 11
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      U1 snRNA sequence"


<220>
<221> modified_base
<222> (5)..(6)
<223> Pseudouridine

<400> 11
auacnnaccu g                                                            11


<210> 12
<211> 11
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 12
cagguaagua u                                                            11


<210> 13
<211> 12
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 13
cagaguaagg gg                                                           12


<210> 14
<211> 10
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 14
caguaaguaa                                                              10


<210> 15
<211> 13
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 15
cagguuuaag uau                                                          13


<210> 16
<211> 12
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 16
cagguuuagu au                                                           12


<210> 17
<211> 11
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 17
aaggucugug u                                                            11


<210> 18
<211> 11
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 18
gagguuagaa u                                                            11


<210> 19
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 19
gacagaguga gacuccau                                                     18


<210> 20
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 20
gagagaguga guguagac                                                     18


<210> 21
<211> 18
<212> RNA
<213> Unknown

<220>
<221> source
<223> /note="Description of Unknown: 
      splice site sequence"

<400> 21
ucaagaguaa gauugauu                                                     18


