               SEQUENCE LISTING

<110> GENETHON
      UNIVERSITE D'EVRY VAL D'ESSONNE
      Institut National de la Sante et de la Recherche Medicale
      (INSERM)

<120> CORRECTION OF ΒETA-THALASSEMIA PHENOTYPE BY GENETICALLY ENGINEERED HEMATOPOIETIC STEM CELL

<130> PR86587_EP_MGG

<150> EP19305484.8
<151> 2019-04-12

<160> 42

<170> BiSSAP 1.3.6

<210> 1
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA 10

<400> 1
gggtttatgc ttggggcgcg                                                20


<210> 2
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA 10

<400> 2
gggtttatgc ttggggcgcg ggg                                            23


<210> 3
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA 12

<400> 3
gactcagaga gaacccacca                                                20


<210> 4
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA 12

<400> 4
gactcagaga gaacccacca tgg                                            23


<210> 5
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA 14

<400> 5
tgggttctct ctgagtctgt                                                20


<210> 6
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA 14

<400> 6
tgggttctct ctgagtctgt ggg                                            23


<210> 7
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA 15.1

<400> 7
gggttctctc tgagtctgtg                                                20


<210> 8
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA 15.1

<400> 8
gggttctctc tgagtctgtg ggg                                            23


<210> 9
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA 16.1

<400> 9
gtcggcagga gacagcacca                                                20


<210> 10
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA 16.1

<400> 10
gtcggcagga gacagcacca tgg                                            23


<210> 11
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA 17-G

<400> 11
gcaggagaca gcaccatggt                                                20


<210> 12
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA 17-G

<400> 12
gcaggagaca gcaccatggt ggg                                            23


<210> 13
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA 20.1

<400> 13
cataaaccct ggcgcgctcg                                                20


<210> 14
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA 20.1

<400> 14
cataaaccct ggcgcgctcg cgg                                            23


<210> 15
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA 5.1

<400> 15
ttgaatgctc cagccggttc                                                20


<210> 16
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA 5.1

<400> 16
ttgaatgctc cagccggttc cag                                            23


<210> 17
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by gRNA2

<400> 17
cgggaggctt cgcccaatcc                                                20


<210> 18
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence target by gRNA2

<400> 18
cgggaggctt cgcccaatcc tgg                                            23


<210> 19
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by gRNA19

<400> 19
cgggcgagcg agtgcgagcc                                                20


<210> 20
<211> 22
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by gRNA19

<400> 20
cgggcgagcg agtgcgagcc gg                                             22


<210> 21
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by gRNA11

<400> 21
gggaggcttc gcccaatcct                                                20


<210> 22
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by gRNA11

<400> 22
gggaggcttc gcccaatcct ggg                                            23


<210> 23
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA INT1 72.1

<400> 23
caggccaccc tcaaccgtcc                                                20


<210> 24
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA INT1 72.1

<400> 24
caggccaccc tcaaccgtcc tgg                                            23


<210> 25
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA INT1 73.2

<400> 25
tccggggcca ggacggttga                                                20


<210> 26
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA INT1 73.2

<400> 26
tccggggcca ggacggttga ggg                                            23


<210> 27
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA INT1 73b.1

<400> 27
gtccggggcc aggacggttg                                                20


<210> 28
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA INT1 73b.1

<400> 28
gtccggggcc aggacggttg agg                                            23


<210> 29
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA INT2 13.2

<400> 29
ccctcgaccc agatcgctcc                                                20


<210> 30
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA INT2 13.2

<400> 30
ccctcgaccc agatcgctcc cgg                                            23


<210> 31
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> Partial nucleic acid sequence targeted by HBA INT2 74.1

<400> 31
gcgtgatcct ctgccctgag                                                20


<210> 32
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> Full nucleic acid sequence targeted by HBA INT2 74.1

<400> 32
gcgtgatcct ctgccctgag agg                                            23


<210> 33
<211> 26
<212> DNA
<213> Artificial Sequence


<220> 
<223> GAPDH transcript

<400> 33
cttcattgac ctcaactaca tggttt                                         26


<210> 34
<211> 22
<212> DNA
<213> Artificial Sequence


<220> 
<223> GAPDH transcript

<400> 34
tgggatttcc attgatgaca ag                                             22


<210> 35
<211> 19
<212> DNA
<213> Artificial Sequence


<220> 
<223> HBG1 transcript

<400> 35
cctgtcctct gcctctgcc                                                 19


<210> 36
<211> 19
<212> DNA
<213> Artificial Sequence


<220> 
<223> HBG2 transcript

<400> 36
ggattgccaa aacggtcac                                                 19


<210> 37
<211> 22
<212> DNA
<213> Artificial Sequence


<220> 
<223> HBB transcript

<400> 37
gcaaggtgaa cgtggatgaa gt                                             22


<210> 38
<211> 23
<212> DNA
<213> Artificial Sequence


<220> 
<223> HBB transcript

<400> 38
taacagcatc aggagtggac aga                                            23


<210> 39
<211> 21
<212> DNA
<213> Artificial Sequence


<220> 
<223> HBA transcript

<400> 39
cggtcaactt caagctccta a                                              21


<210> 40
<211> 20
<212> DNA
<213> Artificial Sequence


<220> 
<223> HBA transcript

<400> 40
acagaagcca ggaacttgtc                                                20


<210> 41
<211> 19
<212> DNA
<213> Artificial Sequence


<220> 
<223> HBD transcript

<400> 41
caagggcact ttttctcag                                                 19


<210> 42
<211> 19
<212> DNA
<213> Artificial Sequence


<220> 
<223> HBD transcript

<400> 42
aattccttgc caaagttgc                                                 19


