               SEQUENCE LISTING

<110> INSTITUT NATIONAL DE LA SANTE ET DE LA RECHERCHE MEDICALE
      UNIVERSITE D'EVRY-VAL-D'ESSONNE
      GENETHON
      CENTRE D'ETUDE DES CELLULES SOUCHES (CECS)

<120> USE OF THIOSTREPTON OR ITS DERIVATIVES FOR THE TREATMENT OF GENETIC DISEASES LINKED TO A PROTEIN-CONFORMATIONAL DISORDER

<130> C517-B-55401 PCT

<150> EP19305097.8
<151> 2019-01-24

<160> 12

<170> BiSSAP 1.3.2

<210> 1
<211> 33
<212> DNA
<213> Artificial Sequence

<220> 
<223> R34H primer (forward)

<400> 1
cacccacttg tgggccacgt ctttgtgcac acc                                  33


<210> 2
<211> 33
<212> DNA
<213> Artificial Sequence

<220> 
<223> R34H primer (reverse)

<400> 2
ggtgtgcaca aagacgtggc ccacaagtgg gtg                                  33


<210> 3
<211> 28
<212> DNA
<213> Artificial Sequence

<220> 
<223> R77C primer (forward)

<400> 3
gccccggtgg ctctgctaca cccagcgc                                       28


<210> 4
<211> 28
<212> DNA
<213> Artificial Sequence

<220> 
<223> R77C primer (reverse)

<400> 4
gcgctgggtg tagcagagcc accggggc                                       28


<210> 5
<211> 27
<212> DNA
<213> Artificial Sequence

<220> 
<223> I124T primer (forward)

<400> 5
ctggtgctgg agactgggga cccagaa                                        27


<210> 6
<211> 27
<212> DNA
<213> Artificial Sequence

<220> 
<223> I124T primer (reverse)

<400> 6
ttctgggtcc ccagtctcca gcaccag                                        27


<210> 7
<211> 31
<212> DNA
<213> Artificial Sequence

<220> 
<223> V247M primer (forward)

<400> 7
gttgactggt gcaatatgac cctggtggat a                                   31


<210> 8
<211> 31
<212> DNA
<213> Artificial Sequence

<220> 
<223> V247M primer (reverse)

<400> 8
tatccaccag ggtcatattg caccagtcaa c                                   31


<210> 9
<211> 20
<212> DNA
<213> Artificial Sequence

<220> 
<223> SGCA primer (forward)

<400> 9
tgctggccta tgtcatgtgc                                                20


<210> 10
<211> 20
<212> DNA
<213> Artificial Sequence

<220> 
<223> SGCA primer (reverse)

<400> 10
tctggatgtc ggaggtagcc                                                20


<210> 11
<211> 25
<212> DNA
<213> Artificial Sequence

<220> 
<223> SGCA probe

<400> 11
cgggagggaa ggctgaagag agacc                                          25


<210> 12
<211> 17
<212> PRT
<213> Artificial Sequence

<220> 
<223> THSP prepeptide

<400> 12
Ile Ala Ser Ala Ser Cys Thr Thr Cys Ile Cys Thr Cys Ser Cys Ser 
1               5                   10                  15      
Ser 
    

