                         SEQUENCE LISTING

<110>  University of Florida Research Foundation, Incorporated
       
 
<120>  ADENO-ASSOCIATED VIRAL VECTORS FOR THE TREATMENT OF BEST DISEASE

<130>  U1197.70139WO00

<140>  Not Yet Assigned
<141>  Concurrently Herewith

<150>  US 62/754,530
<151>  2018-11-01

<150>  US 62/749,622
<151>  2018-10-23

<150>  US 62/726,184
<151>  2018-08-31

<160>  20    

<170>  PatentIn version 3.5

<210>  1
<211>  48
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  1
ccgucaaagc uucacagugu uucaagagaa cacugugaag cuuugacg                    48


<210>  2
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  2
cgucaaagc uucacagugu                                                    19


<210>  3
<211>  19
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  3
acacugugaa gcuuugacg                                                    19


<210>  4
<211>  48
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  4
aagaacucgc cauauagcag ccucgaggcu gcuauauggc gaguucuu                    48


<210>  5
<211>  21
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  5
aagaacucgc cauauagcag c                                                 21


<210>  6
<211>  21
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  6
gcugcuauau ggcgaguucu u                                                 21


<210>  7
<211>  9
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  7
uucaagaga                                                                9


<210>  8
<211>  6
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  8
cucgag                                                                   6


<210>  9
<211>  1758
<212>  DNA
<213>  Homo sapiens


<220>
<221>  misc_feature
<222>  (213)..(213)
<223>  n is a, c, g, or t

<220>
<221>  misc_feature
<222>  (1410)..(1410)
<223>  n is a, c, g, or t

<400>  9
atgaccatca cttacacaag ccaagtggct aatgcccgct taggctcctt ctcccgcctg       60

ctgctgtgct ggcggggcag catctacaag ctgctatatg gcgagttctt aatcttcctg      120

ctctgctact acatcatccg ctttatttat aggctggccc tcacggaaga acaacagctg      180

atgtttgaga aactgactct gtattgcgac agntacatcc agctcatccc catttccttc      240

gtgctgggct tctacgtgac gctggtcgtg acccgctggt ggaaccagta cgagaacctg      300

ccgtggcccg accgcctcat gagcctggtg tcgggcttcg tcgaaggcaa ggacgagcaa      360

ggccggctgc tgcggcgcac gctcatccgc tacgccaacc tgggcaacgt gctcatcctg      420

cgcagcgtca gcaccgcagt ctacaagcgc ttccccagcg cccagcacct ggtgcaagca      480

ggctttatga ctccggcaga acacaagcag ttggagaaac tgagcctacc acacaacatg      540

ttctgggtgc cctgggtgtg gtttgccaac ctgtcaatga aggcgtggct tggaggtcga      600

atccgggacc ctatcctgct ccagagcctg ctgaacgaga tgaacacctt gcgtactcag      660

tgtggacacc tgtatgccta cgactggatt agtatcccac tggtgtatac acaggtggtg      720

actgtggcgg tgtacagctt cttcctgact tgtctagttg ggcggcagtt tctgaaccca      780

gccaaggcct accctggcca tgagctggac ctcgttgtgc ccgtcttcac gttcctgcag      840

ttcttcttct atgttggctg gctgaaggtg gcagagcagc tcatcaaccc ctttggagag      900

gatgatgatg attttgagac caactggatt gtcgacagga atttgcaggt gtccctgttg      960

gctgtggatg agatgcacca ggacctgcct cggatggagc cggacatgta ctggaataag     1020

cccgagccac agccccccta cacagctgct tccgcccagt tccgtcgagc ctcctttatg     1080

ggctccacct tcaacatcag cctgaacaaa gaggagatgg agttccagcc caatcaggag     1140

gacgaggagg atgctcacgc tggcatcatt ggccgcttcc taggcctgca gtcccatgat     1200

caccatcctc ccagggcaaa ctcaaggacc aaactactgt ggcccaagag ggaatccctt     1260

ctccacgagg gcctgcccaa aaaccacaag gcagccaaac agaacgttag gggccaggaa     1320

gacaacaagg cctggaagct taaggctgtg gacgccttca agtctgcccc actgtatcag     1380

aggccaggct actacagtgc cccacagacn cccctcagcc ccactcccat gttcttcccc     1440

ctagaaccat cagcgccgtc aaagcttcac agtgtcacag gcatagacac caaagacaaa     1500

agcttaaaga ctgtgagttc tggggccaag aaaagttttg aattgctctc agagagcgat     1560

ggggccttga tggagcaccc agaagtatct caagtgagga ggaaaactgt ggagtttaac     1620

ctgacggata tgccagagat ccccgaaaat cacctcaaag aacctttgga acaatcacca     1680

accaacatac acactacact caaagatcac atggatcctt attgggcctt ggaaaacagg     1740

gatgaagcac attcctaa                                                   1758


<210>  10
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  10
ctactgtacg gagaatttct                                                   20


<210>  11
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  11
ccagcaagct gcacagcgt                                                    19


<210>  12
<211>  623
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  12
aattctgtca ttttactagg gtgatgaaat tcccaagcaa caccatcctt ttcagataag       60

ggcactgagg ctgagagagg agctgaaacc tacccggcgt caccacacac aggtggcaag      120

gctgggacca gaaaccagga ctgttgactg cagcccggta ttcattcttt ccatagccca      180

cagggctgtc aaagacccca gggcctagtc agaggctcct ccttcctgga gagttcctgg      240

cacagaagtt gaagctcagc acagccccct aacccccaac tctctctgca aggcctcagg      300

ggtcagaaca ctggtggagc agatccttta gcctctggat tttagggcca tggtagaggg      360

ggtgttgccc taaattccag ccctggtctc agcccaacac cctccaagaa gaaattagag      420

gggccatggc caggctgtgc tagccgttgc ttctgagcag attacaagaa gggaccaaga      480

caaggactcc tttgtggagg tcctggctta gggagtcaag tgacggcggc tcagcactca      540

cgtgggcagt gccagcctct aagagtgggc aggggcactg gccacagagt cccagggagt      600

cccaccagcc tagtcgccag acc                                              623


<210>  13
<211>  114
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  13
taaaacgacg gccagtgaat tcatatttgc atgtcgctat gtgttctggg aaatcaccat       60

aaacgtgaaa tgtctttgga tttgggaatc ttataagttc tgtatgagac cact	       114


<210>  14
<211>  241
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  14
gagggcctat ttcccatgat tccttcatat ttgcatatac gatacaaggc tgttagagag       60

ataattggaa ttaatttgac tgtaaacaca aagatattag tacaaaatac gtgacgtaga      120

aagtaataat ttcttgggta gtttgcagtt ttaaaattat gttttaaaat ggactatcat      180

atgcttaccg taacttgaaa gtatttcgat ttcttggctt tatatatctt gtggaaagga      240

c                                                                      241


<210>  15
<211>  24
<212>  DNA
<213>  Homo sapiens

<400>  15
aagctgctat atggcgagtt ctta                                              24


<210>  16
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  16
cgacgatata ccgctcaaga a                                                 21


<210>  17
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  17
aagctgctgt acggcgagtt cctg                                              24


<210>  18
<211>  48
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  18
ccgtcaaagc ttcacagtgt ttcaagagaa cactgtgaag ctttgacg                    48


<210>  19
<211>  48
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  19
gctgctatat ggcgagttct tctcgagaag aactcgccat atagcagc                    48


<210>  20
<211>  174
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Polynucleotide

<400>  20
taaaacgacg gccagtgaat tcatatttgc atgtcgctat gtgttctggg aaatcaccat       60

aaacgtgaaa tgtctttgga tttgggaatc ttataagttc tgtatgagac cactcggatc      120

ccgtcaaagc ttcacagtgt ttcaagagaa cactgtgaag ctttgacgtt tttt            174


