                         SEQUENCE LISTING

<110>  The Trustees of the University of Pennsylvania
       KHURANA, Tejvir S.
       MISHRA, MANOJ KUMAR
       AISHWARYA, Veenu
 
<120>  2'F-ANA-LET7 MEDIATED UTROPHIN UPREGULATION FOR DMD THERAPY

<130>  P-572129-PC

<140>  PCT/US2019/022826
<141>  2019-03-18

<150>  62/645,170
<151>  2018-03-19

<160>  76    

<170>  PatentIn version 3.5

<210>  1
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  1
ugagguagua gguuguaugg uu                                                22


<210>  2
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  2
aaccauacaa ccuacuaccu ca                                                22


<210>  3
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  3
uuuggucccc uucaaccagc ua                                                22


<210>  4
<211>  21
<212>  RNA
<213>  Homo sapiens

<400>  4
uagcugguug aaggggacca a                                                 21


<210>  5
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  5
ucucccaacc cuuguaccag ug                                                22


<210>  6
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  6
cacugguaca aggguuggga ga                                                22


<210>  7
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  7
uagguaguuu ccuguuguug gg                                                22


<210>  8
<211>  21
<212>  RNA
<213>  Homo sapiens

<400>  8
ccaacaacag gaaacuaccu a                                                 21


<210>  9
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  9
uggaauguaa ggaagugugu gg                                                22


<210>  10
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  10
ccacacacuu ccuuacauuc ca                                                22


<210>  11
<211>  21
<212>  RNA
<213>  Homo sapiens

<400>  11
agggcccccc cucaauccug u                                                 21


<210>  12
<211>  21
<212>  RNA
<213>  Homo sapiens

<400>  12
acaggauuga gggggggccc u                                                 21


<210>  13
<211>  2391
<212>  DNA
<213>  Mus musculus

<400>  13
tgagcatcta tccagccagc caacatttcc cgaccttcag tattgccctc ttctgcaaat       60

gccaatccca agacccattc aaccccaaag ctccgtggct ccacgacaca agctgttgag      120

tgcttactgg gtgttctact gagggaacca aacactgact atccaaagag aaaaggatat      180

tttggttttc taataacgta tattattgtt ttcttctccc ctttctatgc aactgtaaat      240

taatgaacag agaagtattt ggaggtggta aagcatttgt cactgatttg tataatatat      300

acagccatgg gaaagtgggt gggggctttc taatatgaaa ctgtcttttt aataaccaag      360

agaaaaaatt gcataagaat tagaccactt tacattatta cattccttct gctgttcaca      420

ttaaccttgt acaataactt cacttattat ttgactgttt taccattatg ttttggttat      480

ttataaattt atcagccata caaacaaata gattctatgt atttgtttct ataatctggc      540

caaattccta agttcatata tttgaatcaa atattttaca tatgtggagt aggcaggcat      600

tctgaagata ctatttaact ttagttgacg tcacacacac catcctttag taaccactgg      660

atgactacac taaaaatcct gtggacttta acggcaagct gctggggtat ttttcctcct      720

gtttttattc cttttttgta agtagatctt gacgtcttta tttatttcat cttgcaatct      780

ctataataaa gaagactgta ttgtaatagt ctcaaaaaat tattttacca agggttacca      840

tttaagcata ttttcatttt gattcagaaa ccaaagttgg tacaacctct cctagtacat      900

gcaaccttgg ttttcatgag aaaacacacg gcaggccttt gcccattgtg aggagagcac      960

acatcatgct cttcagtttc ctttgaatag acttttattg ttgtttttgt atttttcgag     1020

tcctgtgtaa gttttgaaag ctctggttgt ttcctttgtg aaagcaggca gatacttagt     1080

tggctgtctc atttgaagct ttggagcaga tagtcagatg tctcatgacc cctcacttgg     1140

ccagcagcac atccgagaag gatgtcactc acaagcctac accacggctt ctctagaatg     1200

aaatcagtgc tcggatgatt gtatccctgc ctctacttct gagtgtgttc aactaggtat     1260

tggcttcttt ttctttttct tttctttttt ttttaattta acacttaatt gccgatttta     1320

gagaaaccaa aaataaaggt gaaggtaata tgttttgatt caaacatata tgcttttaaa     1380

catcagacat gctaactttg gttctcttta ctggaatctg gcccagagga ggtgaaattt     1440

agaaatgtta ttctttagat gggtgggtgg gttggggggc caagggtgtc tattttccag     1500

cattagatat ttttgagacg aagaaaattg ttttatataa ggggagagcc atgatcacct     1560

ttctacctca gaaccacctt cctccattgt gttggacata gctttatatg ccgcagtgtg     1620

caaaacctag ggctgtagtc aggcctttcc atacccagga agcacctgtg taaagaagat     1680

caacagaaac tcccggaact cagaacccca agttgtagat ttggtgtcgt ccttgttctt     1740

gctttgagga gtcatgtatt cttttatttc ctgcctgtat ttgtatgcaa aatgatctct     1800

atctgctatt acagaaaaag ctacacaaaa cactacattg taaccttctg agtaataaat     1860

aagaggaaat atattacagt aaccatgatg agaaataagt gtattgttct tttgaaatat     1920

gtggttaatc gcagactgtc atctaatctg ttacataccg tatttttcat cctgaataaa     1980

agtaatttta acacaaaatg actttgatgt ttggctgtgt tcagctgatg aaatcagatc     2040

tctgaatgta tgtgatgaaa gctaactata agatgatcta tattctgata aatctaaata     2100

ttttctgaaa ctctctctta tacattaatc tagtctccat tcactcatta tctctctctc     2160

ctttcttgca tataaatatg attatatatt tttcaatttc ctgtacaaat cagagtctta     2220

ttactaggga aaatggatgt tataagtaca ttcctaaagc ccattgggcc ttcattttta     2280

taacttggag ctactgagat ttatcaggtt actctctcaa atccactttc atcactagac     2340

tcatagtttt ctatgtatct atattattat aactaaataa aaatatacat g              2391


<210>  14
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  14
atgggaaagt gggtgggggc ttt                                               23


<210>  15
<211>  22
<212>  DNA
<213>  Homo sapiens

<400>  15
ccactttaca ttattacatt cc                                                22


<210>  16
<211>  20
<212>  DNA
<213>  Homo sapiens

<400>  16
atgggtgggt gggttggggg                                                   20


<210>  17
<211>  17
<212>  DNA
<213>  Homo sapiens

<400>  17
gtgggttggg gggccaa                                                      17


<210>  18
<211>  24
<212>  DNA
<213>  Mus musculus

<400>  18
agccatgatc acctttctac ctca                                              24


<210>  19
<211>  19
<212>  DNA
<213>  Homo sapiens

<400>  19
ccatacccag gaagcacct                                                    19


<210>  20
<211>  21
<212>  RNA
<213>  Homo sapiens

<400>  20
aaguggauau uguugccauc a                                                 21


<210>  21
<211>  21
<212>  DNA
<213>  Homo sapiens

<400>  21
aguacugcuu acgauacggt t                                                 21


<210>  22
<211>  21
<212>  DNA
<213>  Homo sapiens

<400>  22
ccguaucgua agcaguacut t                                                 21


<210>  23
<211>  21
<212>  DNA
<213>  Homo sapiens

<400>  23
gggtgggtgg gttggggggc c                                                 21


<210>  24
<211>  26
<212>  RNA
<213>  Mus musculus

<400>  24
cugagguaga aaggugauca uggcuc                                            26


<210>  25
<211>  26
<212>  RNA
<213>  Homo sapiens

<400>  25
cugagguaga aaggugguca uggcuu                                            26


<210>  26
<211>  27
<212>  RNA
<213>  Mus musculus

<400>  26
cugagguaga aaggugauca uggcucu                                           27


<210>  27
<211>  28
<212>  RNA
<213>  Mus musculus

<400>  27
cugagguaga aaggugauca uggcucuc                                          28


<210>  28
<211>  29
<212>  RNA
<213>  Mus musculus

<400>  28
cugagguaga aaggugauca uggcucucc                                         29


<210>  29
<211>  27
<212>  RNA
<213>  Mus musculus

<400>  29
ucugagguag aaaggugauc auggcuc                                           27


<210>  30
<211>  28
<212>  RNA
<213>  Mus musculus

<400>  30
uucugaggua gaaaggugau cauggcuc                                          28


<210>  31
<211>  29
<212>  RNA
<213>  Mus musculus

<400>  31
guucugaggu agaaagguga ucauggcuc                                         29


<210>  32
<211>  28
<212>  RNA
<213>  Mus musculus

<400>  32
ucugagguag aaaggugauc auggcucu                                          28


<210>  33
<211>  29
<212>  RNA
<213>  Mus musculus

<400>  33
uucugaggua gaaaggugau cauggcucu                                         29


<210>  34
<211>  30
<212>  RNA
<213>  Mus musculus

<400>  34
guucugaggu agaaagguga ucauggcucu                                        30


<210>  35
<211>  29
<212>  RNA
<213>  Mus musculus

<400>  35
ucugagguag aaaggugauc auggcucuc                                         29


<210>  36
<211>  30
<212>  RNA
<213>  Mus musculus

<400>  36
uucugaggua gaaaggugau cauggcucuc                                        30


<210>  37
<211>  31
<212>  RNA
<213>  Mus musculus

<400>  37
guucugaggu agaaagguga ucauggcucu c                                      31


<210>  38
<211>  30
<212>  RNA
<213>  Mus musculus

<400>  38
ucugagguag aaaggugauc auggcucucc                                        30


<210>  39
<211>  31
<212>  RNA
<213>  Mus musculus

<400>  39
uucugaggua gaaaggugau cauggcucuc c                                      31


<210>  40
<211>  32
<212>  RNA
<213>  Mus musculus

<400>  40
guucugaggu agaaagguga ucauggcucu cc                                     32


<210>  41
<211>  27
<212>  RNA
<213>  Homo sapiens

<400>  41
cugagguaga aaggugguca uggcuuu                                           27


<210>  42
<211>  28
<212>  RNA
<213>  Homo sapiens

<400>  42
cugagguaga aaggugguca uggcuuuc                                          28


<210>  43
<211>  29
<212>  RNA
<213>  Homo sapiens

<400>  43
cugagguaga aaggugguca uggcuuucc                                         29


<210>  44
<211>  27
<212>  RNA
<213>  Homo sapiens

<400>  44
ucugagguag aaaggugguc auggcuu                                           27


<210>  45
<211>  28
<212>  RNA
<213>  Homo sapiens

<400>  45
aucugaggua gaaagguggu cauggcuu                                          28


<210>  46
<211>  29
<212>  RNA
<213>  Homo sapiens

<400>  46
gaucugaggu agaaaggugg ucauggcuu                                         29


<210>  47
<211>  28
<212>  RNA
<213>  Homo sapiens

<400>  47
ucugagguag aaaggugguc auggcuuu                                          28


<210>  48
<211>  29
<212>  RNA
<213>  Homo sapiens

<400>  48
aucugaggua gaaagguggu cauggcuuu                                         29


<210>  49
<211>  30
<212>  RNA
<213>  Homo sapiens

<400>  49
gaucugaggu agaaaggugg ucauggcuuu                                        30


<210>  50
<211>  29
<212>  RNA
<213>  Homo sapiens

<400>  50
ucugagguag aaaggugguc auggcuuuc                                         29


<210>  51
<211>  30
<212>  RNA
<213>  Homo sapiens

<400>  51
aucugaggua gaaagguggu cauggcuuuc                                        30


<210>  52
<211>  31
<212>  RNA
<213>  Homo sapiens

<400>  52
gaucugaggu agaaaggugg ucauggcuuu c                                      31


<210>  53
<211>  30
<212>  RNA
<213>  Homo sapiens

<400>  53
ucugagguag aaaggugguc auggcuuucc                                        30


<210>  54
<211>  31
<212>  RNA
<213>  Homo sapiens

<400>  54
aucugaggua gaaagguggu cauggcuuuc c                                      31


<210>  55
<211>  32
<212>  RNA
<213>  Homo sapiens

<400>  55
gaucugaggu agaaaggugg ucauggcuuu cc                                     32


<210>  56
<211>  2045
<212>  DNA
<213>  Homo sapiens

<400>  56
tgaagtattc atccggccaa ccaatgtttc ctgacgtaca gtgttgccct tttcagcaaa       60

tgccaattcc aagttccatt aaatcagaag ctccatggct ccttggccca cgatgttgag      120

tgctgactgt gtgttctact gaaagagtaa aacactgact atccaaagag aaatggatat      180

tttgttttta taataaccat atattattgt tttcttcttc cctttctatg caagtgtaaa      240

ttaatgaaca gagaggtatt tggaaatggt aatacatttg tcacggattt gtataatgta      300

tacagcattg ggaaagtggg tgggggcttt ctaatatgat accgtctttt taataactat      360

gacaaagctt acataagaat tagaagacca ctttacattt ttacattcct tctgctgttc      420

atattaacct tgcacaatta cttcattttt tctttgactc ttttaccaca atgttttggt      480

tatttataat ttatcagcca tatgtttatc agccatataa ccaactagat cccaaataga      540

tccatgtatt tgtttccgtg atttggccac attaataaat tcataaattt caatcaaata      600

tcttatatat acacacatat ggtttaagct acagccctgt gtatgccgtt taactttatt      660

tgacgttgcc cacttacttc tttgctgacc acttggataa ccgtaataaa aatcctataa      720

gcctaaatgg catttctttt gggatatttt tcctgcattt tattcccttt ttatataagt      780

aggaattaat tatttatttt atgtcttaat ctatttgata aagaagacta cattataata      840

atctcaaaga tcatattacc aaaggttgcc cacttgagca tattttcatt ttgacacaga      900

aacaaaattt agtacaacct ttcctagttc ccatgtcttg attttcatca ttacatgcac      960

agcagacctt tacctattgt gataccagaa cacatcattg tctttggttc ccttcaaaga     1020

gaattttatt gttgttttgt attttcaagt ccttaatagt tcttgaaact cctagttgtt     1080

ttcttgttga aagcagacac acatttagtg cacggcttat tttacctttc gggtgaaaga     1140

tcagatgttt ttataccctt cacttgatca atatatttgg aaagaatgtt tatcaaaagt     1200

ctatgtcact gcttctacag aagaatgaaa ttaatgctta ggtgatggta cctccaccta     1260

catctttttg agtgcattca attatgtatt ttggtttagc ttctgattta acatttaatt     1320

gattcagttt aaacatgtta cttaattagc aaatgtagag gaaccaaaaa aaggtgaaaa     1380

taatatgttt tgattcaaac ctaaagacat aaaaacataa agacatttta actttgggtt     1440

ctctttagct gggatctggc cagaaggagg cttaaagtta gaaattgcta ttattttaga     1500

ataggttggg tgggttgggg ggcaagggtg tctatttgca gcagagatat tttgaaaaga     1560

agaaaattgt tttatataaa aaggaaagcc atgaccacct ttctacctca gatccatctt     1620

catccattgc attggaaact gctttatgct gctgcagtct gcaaagtcta gagcttttat     1680

caggccatgt catacccaag aaagcaccta tttaaagaaa aaacaattcc ctgagctctc     1740

aactccaagt tgtagatttg gtgtcttcct tgttcttact ttaaaaagtc atgtgttaat     1800

tttttttctg cctgtatttg tatgcaaaat gtcctctatc tgctattaaa gaaaagctac     1860

gtaaaacact acattgtaac cttctaagta ataataaata aaaagaaata tattgcagta     1920

acaatgggaa gtaagtatgt agttcttttg aaatatgtgg taaagaacta atcacagact     1980

atcatctaat ctggttacat attgtatttt tcatcctgaa taaaagtaat tttaacacaa     2040

aaaaa                                                                 2045


<210>  57
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  57
ttgggaaagt gggtgggggc ttt                                               23


<210>  58
<211>  26
<212>  DNA
<213>  Homo sapiens

<400>  58
ataggttggg tgggttgggg ggcaag                                            26


<210>  59
<211>  25
<212>  DNA
<213>  Homo sapiens

<400>  59
gaccacttta catttttaca ttcct                                             25


<210>  60
<211>  22
<212>  DNA
<213>  Homo sapiens

<400>  60
ataggttggg tgggttgggg gg                                                22


<210>  61
<211>  24
<212>  DNA
<213>  Homo sapiens

<400>  61
aggttgggtg ggttgggggg caag                                              24


<210>  62
<211>  24
<212>  DNA
<213>  Homo sapiens

<400>  62
agccatgacc acctttctac ctca                                              24


<210>  63
<211>  24
<212>  DNA
<213>  Homo sapiens

<400>  63
atccattgca ttggaaactg cttt                                              24


<210>  64
<211>  26
<212>  DNA
<213>  Human

<400>  64
cugagguaga aaggugatca uggcuc                                            26


<210>  65
<211>  21
<212>  DNA
<213>  Human

<400>  65
cugagguaga aaggugatca u                                                 21


<210>  66
<211>  21
<212>  DNA
<213>  Human

<400>  66
guagaaaggt gaucatggcu c                                                 21


<210>  67
<211>  26
<212>  DNA
<213>  Homo Sapien

<400>  67
cugaggtaga aaggtgauca uggcuc                                            26


<210>  68
<211>  22
<212>  DNA
<213>  Human

<400>  68
cugaggtaga aaggtgauca ug                                                22


<210>  69
<211>  22
<212>  DNA
<213>  Homo Sapiens

<400>  69
ggtagaaagg tgaucauggc uc                                                22


<210>  70
<211>  26
<212>  DNA
<213>  Homo Sapiens

<400>  70
cugagguaga aaggtgatca uggcuc                                            26


<210>  71
<211>  21
<212>  DNA
<213>  Human

<400>  71
cugaggtaga aaggtgauca u                                                 21


<210>  72
<211>  21
<212>  DNA
<213>  Human

<400>  72
guagaaaggt gatcatggcu c                                                 21


<210>  73
<211>  26
<212>  DNA
<213>  Human

<400>  73
ctgagguaga aaggugatca uggcuc                                            26


<210>  74
<211>  21
<212>  DNA
<213>  Human

<400>  74
ctgagguaga aaggugatca u                                                 21


<210>  75
<211>  21
<212>  DNA
<213>  Human

<400>  75
gtagaaaggt gaucatggct c                                                 21


<210>  76
<211>  25
<212>  DNA
<213>  Human

<400>  76
gugagcacut ctuuccttcu uttuu                                             25


