                               SEQUENCE LISTING

<110> UNIVERSITY OF MASSACHUSETTS
 
<120> COMPOSITIONS AND METHODS FOR THE TREATMENT OF EXPANDED 
      REPEAT-ASSOCIATED DISORDERS

<130> 606902: UM9-225PC

<140> PCT/US2018/059985
<141> 2018-11-09

<150> 62/584,176
<151> 2017-11-10

<160> 20    

<170> PatentIn version 3.5

<210> 1
<211> 185
<212> DNA
<213> Unknown

<220>
<223> Description of Unknown: 
      C9ORF72 sequence

<400> 1
gtgtgtgttt ttgtttttcc caccctctct ccccactact tgctctcaca gtactcgctg       60

agggtgaaca agaaaagacc tgataaagat taaccagaag aaaacaagga gggaaacaac      120

cgcagcctgt agcaagctct ggaactcagg agtcgcgcgc taggggccgg ggccggggcc      180

ggggc                                                                  185


<210> 2
<211> 22
<212> DNA
<213> Unknown

<220>
<223> Description of Unknown: 
      C9ORF72 sequence

<400> 2
acctgataaa gattaaccag aa                                                22


<210> 3
<211> 22
<212> DNA
<213> Unknown

<220>
<223> Description of Unknown: 
      C9ORF72 sequence

<400> 3
tgtagcaagc tctggaactc ag                                                22


<210> 4
<211> 20
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 4
gctctcacag tactcgctga                                                   20


<210> 5
<211> 20
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      oligonucleotide

<400> 5
tgtagcaagc tctggaactc                                                   20


<210> 6
<211> 86
<212> DNA
<213> Unknown

<220>
<223> Description of Unknown: 
      C9ORF72 sequence

<400> 6
tgagggtgaa caagaaaaga cctgataaag attaaccaga agaaaacaag gagggaaaca       60

accgcagcct gtagcaagct ctggaa                                            86


<210> 7
<211> 160
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polypeptide

<400> 7
Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
1               5                   10                  15      


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
            20                  25                  30          


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
        35                  40                  45              


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
    50                  55                  60                  


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
65                  70                  75                  80  


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
                85                  90                  95      


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
            100                 105                 110         


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
        115                 120                 125             


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
    130                 135                 140                 


Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg Gly Arg 
145                 150                 155                 160 


<210> 8
<211> 18
<212> RNA
<213> Unknown

<220>
<223> Description of Unknown: 
      C9ORF72 sequence

<400> 8
ggggccgggg ccggggcc                                                     18


<210> 9
<211> 18
<212> RNA
<213> Unknown

<220>
<223> Description of Unknown: 
      C9ORF72 sequence

<400> 9
ggccccggcc ccggcccc                                                     18


<210> 10
<211> 180
<212> DNA
<213> Unknown

<220>
<223> Description of Unknown: 
      C9ORF72 sequence

<400> 10
gtgtgtgttt ttgtttttcc caccctctct ccccactact tgctctcaca gtactcgctg       60

agggtgaaca agaaaagacc tgataaagat taaccagaag aaaacaagga gggaaacaac      120

cgcagcctgt agcaagctct ggaactcagg agtcgcgcgc taggggccgg ggccggggcc      180


<210> 11
<211> 450
<212> DNA
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polynucleotide

<400> 11
ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc       60

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      120

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      180

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      240

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      300

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      360

ggggccgggg ccggggccgg ggccggggcc ggggccgggg ccggggccgg ggccggggcc      420

ggggccgggg ccggggccgg ggccggggcc                                       450


<210> 12
<211> 4
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 12
Arg Leu Gly Ala 
1               


<210> 13
<211> 16
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 13
Pro Gly Gly Gly Pro Gly Gly Arg Gly Arg Gly Pro Gly Pro Gly Pro 
1               5                   10                  15      


<210> 14
<211> 31
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polypeptide

<400> 14
Arg Ala Val Gly Ser Asn Trp Leu Lys Ser Cys Ala Ala Thr Thr Glu 
1               5                   10                  15      


Arg Arg Thr Lys Lys Gln Asn Ile Lys Ile Leu Asp Lys Arg Thr 
            20                  25                  30      


<210> 15
<211> 19
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 15
Arg Thr Ser His Ser Cys Thr Thr Pro Leu Ser Pro Pro Phe Phe Leu 
1               5                   10                  15      


Phe Val Cys 
            


<210> 16
<211> 33
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polypeptide

<400> 16
Val Ala Ala Gly Gly Arg Ala Arg Gly Arg Ala Arg Gly Ser Trp Ala 
1               5                   10                  15      


Gly Ala Gly Ala Gly Ala Gly Leu Ala Arg Ser Arg Leu Glu Leu Ala 
            20                  25                  30          


Gln 
    


<210> 17
<211> 12
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 17
Leu Ser Arg Asn Asn Gly Glu Lys Asn Glu Glu Pro 
1               5                   10          


<210> 18
<211> 30
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polypeptide

<400> 18
Asp Lys Asp Pro Arg Lys Lys Asn Val Arg Leu Ser Tyr Gln Ser Leu 
1               5                   10                  15      


Leu Tyr His Pro Ser Leu Thr Pro Phe Val Phe Val Cys Val 
            20                  25                  30  


<210> 19
<211> 48
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      polypeptide

<400> 19
Gly Cys Gly Arg Gly Pro Gly Ala Gly Pro Gly Ala Gly Val Val Gly 
1               5                   10                  15      


Arg Gly Arg Gly Arg Gly Arg Ala Arg Ser Glu Gln Thr Gly Ser Ser 
            20                  25                  30          


Ala Val Pro Gln Pro Gln Lys Gly Gly Gln Lys Arg Arg Thr Leu Arg 
        35                  40                  45              


<210> 20
<211> 26
<212> PRT
<213> Artificial Sequence

<220>
<223> Description of Artificial Sequence: Synthetic
      peptide

<400> 20
Thr Lys Glu Gln Glu Gly Glu Ala Leu Val Thr Leu Ala Leu Leu Pro 
1               5                   10                  15      


Ser Leu Pro His Ser Phe Cys Phe Cys Val 
            20                  25      


