                         SEQUENCE LISTING

<110>  Fulcrum Therapeutics, Inc.
       CACAE, Angela M
       ROJAS SOTO, Luis G. A.
       THOMPSON, Lorin A.
       WALLACE, Owen B.
 
<120>  P38 KINASE INHIBITORS REDUCE DUX4 AND DOWNSTREAM GENE EXPRESSION 
       FOR THE TREATMENT OF FSHD

<130>  FULC-026/02WO

<150>  62/568,673
<151>  2017-10-05

<150>  62/568,754
<151>  2017-10-05

<150>  62/682,563
<151>  2018-06-08

<150>  62/682,565
<151>  2018-06-08

<160>  12    

<170>  PatentIn version 3.5

<210>  1
<211>  16
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  DUX4 antisense oligonucleotide

<400>  1
cagcgtcgga aggtgg                                                       16


<210>  2
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Non-targeting antisense oligonucleotide

<400>  2
aacacgtcta tacgc                                                        15


<210>  3
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  NT-CRL

<400>  3
gtattactga tattggtggg                                                   20


<210>  4
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  MAPK14 sgRNA targeting sequence

<400>  4
gctgaacaag acaatctggg                                                   20


<210>  5
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  MAPK14 sgRNA targeting sequence

<400>  5
ctgcttttga cacaaaaacg                                                   20


<210>  6
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  MAPK14 sgRNA targeting sequence

<400>  6
cttatctacc aaattctccg                                                   20


<210>  7
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  pLAM sgRNA targeting sequence

<400>  7
agaatttcac ggaagaacaa                                                   20


<210>  8
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  pLAM sgRNA targeting sequence

<400>  8
attaaaatgc cccctccctg                                                   20


<210>  9
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  pLAM sgRNA targeting sequence

<400>  9
aatcttctat aggatccaca                                                   20


<210>  10
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  MAPK14 siRNA

<400>  10
uagauuacua gguuuuaggt c                                                 21


<210>  11
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  MAPK14 siRNA

<400>  11
ccuaaaaccu aguaaucuat t                                                 21


<210>  12
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  pLAM sgRNA targeting sequence

<400>  12
caggtttgcc tagacagcgt                                                   20


