                         SEQUENCE LISTING

<110>  SAREPTA THERAPEUTICS, INC.
       CATABASIS PHARMACEUTICALS, INC.
 
<120>  COMBINATION THERAPIES FOR TREATING MUSCULAR DYSTROPHY

<130>  4140.013PC02

<140>  PCT/US18/053543
<141>  2018-09-28

<150>  US 62/737,750
<151>  2018-09-27

<150>  US 62/565,016
<151>  2017-09-28

<160>  20    

<170>  PatentIn version 3.5

<210>  1
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  SRP-4053 (+36+60)

<400>  1
gttgcctccg gttctgaagg tgttc                                             25


<210>  2
<211>  25
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  PRO053 (+36+60)


<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  n is 5-methylcytosine

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  n is 5-methylcytosine

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  n is 5-methylcytosine

<220>
<221>  misc_feature
<222>  (9)..(9)
<223>  n is 5-methylcytosine

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  n is 5-methylcytosine

<220>
<221>  misc_feature
<222>  (25)..(25)
<223>  n is 5-methylcytosine

<400>  2
guugnnunng guunugaagg uguun                                             25


<210>  3
<211>  18
<212>  RNA
<213>  Artificial Sequence

<220>
<223>  WO 2004/083432 (SIN: 29)

<400>  3
cuguugccuc cgguucug                                                     18


<210>  4
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  WO 2012/029986 (SIN: 11)

<400>  4
cctccggttc tgaaggtgtt cttgt                                             25


<210>  5
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  WO 2012/029986 (SIN:35)

<400>  5
cctccggttc tgaaggtgtt c                                                 21


<210>  6
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  US 8,084,601 (SIN: 10)


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (4)..(4)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (9)..(9)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (15)..(15)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (17)..(17)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (23)..(23)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (25)..(25)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (26)..(26)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (28)..(28)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (29)..(29)
<223>  n is u or t

<400>  6
cngnngccnc cggnncngaa ggngnncnng                                        30


<210>  7
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  US 8,084,601 (SIN: 11)


<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (7)..(7)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (17)..(17)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (18)..(18)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (20)..(20)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (26)..(26)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (28)..(28)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (29)..(29)
<223>  n is u or t

<400>  7
caacngnngc cnccggnncn gaaggngnnc                                        30


<210>  8
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  US 8,084,601 (SIN: 12)


<220>
<221>  misc_feature
<222>  (1)..(1)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (20)..(20)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (22)..(22)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (23)..(23)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (25)..(25)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (26)..(26)
<223>  n is u or t

<220>
<221>  misc_feature
<222>  (28)..(28)
<223>  n is u or t

<400>  8
nngccnccgg nncngaaggn gnncnngnac                                        30


<210>  9
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  WO 2012/109296 (SIN: 116)

<400>  9
caactgttgc ctccggttct gaag                                              24


<210>  10
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  M23D (AVI-4225)

<400>  10
ggccaaacct cggcttacct gaaat                                             25


<210>  11
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  (RXR)4


<220>
<221>  MISC_FEATURE
<222>  (2)..(2)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (5)..(5)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (8)..(8)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (11)..(11)
<223>  Xaa is 6-aminohexanoic acid

<400>  11

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg 
1               5                   10          


<210>  12
<211>  10
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  (RFF)3R

<400>  12

Arg Phe Phe Arg Phe Phe Arg Phe Phe Arg 
1               5                   10  


<210>  13
<211>  14
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  (RXR)4XB


<220>
<221>  MISC_FEATURE
<222>  (2)..(2)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (5)..(5)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (8)..(8)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (11)..(11)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (13)..(13)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (14)..(14)
<223>  Asx is bAla or beta-Alanine

<400>  13

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Xaa Asx 
1               5                   10                  


<210>  14
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  (RFF)3RXB


<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  Xaa is 6-aminohexanoic acid

<220>
<221>  MISC_FEATURE
<222>  (12)..(12)
<223>  Asx is bAla or beta-Alanine

<400>  14

Arg Phe Phe Arg Phe Phe Arg Phe Phe Arg Xaa Asx 
1               5                   10          


<210>  15
<211>  11
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  (RFF)3RG

<400>  15

Arg Phe Phe Arg Phe Phe Arg Phe Phe Arg Gly
1               5                   10  


<210>  16
<211>  6
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  R5G

<400>  16

Arg Arg Arg Arg Arg Gly 
1               5       


<210>  17
<211>  5
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  R5

<400>  17

Arg Arg Arg Arg Arg 
1               5   


<210>  18
<211>  7
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  R6G

<400>  18

Arg Arg Arg Arg Arg Arg Gly 
1               5           


<210>  19
<211>  6
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  R6

<400>  19

Arg Arg Arg Arg Arg Arg 
1               5       


<210>  20
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Viltolarsen

<400>  20
cctccggttc tgaaggtgtt c                                                 21


