                         SEQUENCE LISTING

<110>  ICAHN SCHOOL OF MEDICINE AT MOUNT SINAI
 
<120>  VIRAL DELIVERY OF RNA UTILIZING SELF-CLEAVING RIBOZYMES AND 
       CRISPR-BASED APPLICATIONS THEREOF

<130>  084284.00151

<140>  PCT/US17/38780
<141>  2017-06-22

<150>  62/353,452
<151>  2016-06-22

<160>  43    

<170>  PatentIn version 3.5

<210>  1
<211>  442
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  1
atcccgggtg aggcatccca ccatcctcag tcacagagag acccaatcta ccatcagcat       60

cagccagtaa agattaagaa aaacttaggg tgaaagaaat ttcacctaac acggcgcagc      120

gatcgcgtgg ccctgatgag tccgtgagga cgaaacggta ggaattccta ccgtcggcca      180

cgagttcgag atcgagtttt agagctagaa atagcaagtt aaaataaggc tagtccgtta      240

tcaacttgaa aaagtggcac cgagtcggtg cacgtatcac cggagtcgac tccggtctga      300

tgagtccgtg aggacgaaat acgtatcccg ggtgaggcat cccaccatcc tcagtcacag      360

agagacccaa tctaccatca gcatcagcca gtaaagatta agaaaaactt agggtgaaag      420

aaatttcacc taacacggcg ca                                               442


<210>  2
<211>  39
<212>  RNA
<213>  Artificial

<220>
<223>  synthetic

<400>  2
guggcccuga ugagcgaaac gguaggaauu ccuaccguc                              39


<210>  3
<211>  47
<212>  RNA
<213>  Artificial

<220>
<223>  synthetic

<400>  3
caccggaguc gacuccgguc ugaugagucc gugaggacga aauacgu                     47


<210>  4
<211>  19
<212>  PRT
<213>  Artificial

<220>
<223>  synthetic

<400>  4

Ala Thr Asn Phe Ser Leu Leu Lys Gln Ala Gly Asp Val Glu Glu Asn 
1               5                   10                  15      


Pro Gly Pro 
            


<210>  5
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  5
ggccacgagt tcgagatcga ggg                                               23


<210>  6
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  6
caggttggac caagctatgc agg                                               23


<210>  7
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  7
cagactggat caagctatgc cag                                               23


<210>  8
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  8
caagttacaa caagctatgc aag                                               23


<210>  9
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  9
aaggtttttc caagctatgc tag                                               23


<210>  10
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  10
caggattcac caagctctgc cag                                               23


<210>  11
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  11
cagtttggtt caagctatgt tag                                               23


<210>  12
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  12
agaattcagc cctaacctct ggg                                               23


<210>  13
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  13
agaattcagg cttaacctct tag                                               23


<210>  14
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  14
aaaattcttc cctaacctct aag                                               23


<210>  15
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  15
acatttcagc tctaacctct ggg                                               23


<210>  16
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  16
ataaatcagc cctaacatct gag                                               23


<210>  17
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  17
aaaagtttgc cctaacctct cag                                               23


<210>  18
<211>  19
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  18
ggcgaggagg ataacatgg                                                    19


<210>  19
<211>  21
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  19
cttcagcctc tgcttgatct c                                                 21


<210>  20
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  20
ttgtcatggt catctgctac tc                                                22


<210>  21
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  21
gtgtcacaag cccacagata tt                                                22


<210>  22
<211>  24
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  22
ctccactttc cataacagtc tagg                                              24


<210>  23
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  23
ggtccttgga acagtagaga tag                                               23


<210>  24
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  24
tgtttgctgt gaggctactt tg                                                22


<210>  25
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  25
tcactgtcca atctgcttta cc                                                22


<210>  26
<211>  25
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  26
gcagaggcat tataaaccca atatg                                             25


<210>  27
<211>  19
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  27
ccaggaggaa ctggcaaat                                                    19


<210>  28
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  28
aagctccatc ttcttcgttc tt                                                22


<210>  29
<211>  25
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  29
agtaggagat ggatttacag gtatt                                             25


<210>  30
<211>  20
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  30
cagtgacatg agcacctgaa                                                   20


<210>  31
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  31
gcaaggacat cctcatccat aa                                                22


<210>  32
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  32
cctggacaag gactggtact at                                                22


<210>  33
<211>  20
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  33
tagcacaggg tcccaaattc                                                   20


<210>  34
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  34
gcaggctggt aattgatctt tc                                                22


<210>  35
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  35
tgatccacag ttggttgaat cc                                                22


<210>  36
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  36
ccagaatgtg tcctgggttt ag                                                22


<210>  37
<211>  20
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  37
gtgtcagagc gagactttgt                                                   20


<210>  38
<211>  23
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  38
ggagtatctt cagctgtgag aag                                               23


<210>  39
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  39
ctgttacacg ttccttgcta ct                                                22


<210>  40
<211>  22
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  40
ctgattgagt gggtcatcag aa                                                22


<210>  41
<211>  19
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  41
gctacgtgct ggtgctaaa                                                    19


<210>  42
<211>  24
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  42
gtccaggaaa gaaagttgca taag                                              24


<210>  43
<211>  21
<212>  DNA
<213>  Artificial

<220>
<223>  synthetic

<400>  43
gctgtctgct ggaaagatag t                                                 21


