                         SEQUENCE LISTING

<110>  RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL
 
<120>  RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INDUCING DUX4 EXON 
       SKIPPING

<130>  28335/50392PCT

<150>  US 62/300,500
<151>  2016-02-26

<160>  5     

<170>  PatentIn version 3.5

<210>  1
<211>  472
<212>  DNA
<213>  Homo sapiens

<400>  1
tttgctagct actgccgaat ccaggtctcc gggcttaaca acaacgaagg ggctgtgact       60

ggctgctttc tcaaccaatc agcaccgaac tcatttgcat gggctgagaa caaatgttcg      120

cgaactctag aaatgaatga cttaagtaag ttccttagaa tattattttt cctactgaaa      180

gttaccacat gcgtcgttgt ttatacagta ataggaacaa gaaaaaagtc acctaagctc      240

accctcatca attgtggagt tcctttatat cccatcttct ctccaaacac atacgcagag      300

ctcctccagc agagcccggt attcttcctc aatttttgga gtaggctttc tggcttttta      360

ccggaaagcc cctcttatga tgtttgttgc caatgataga ttgttttcac tgtgcaaaaa      420

ttatgggtag ttttggtggt cttgatgcag ttgtaagctt ggggactagt tt              472


<210>  2
<211>  475
<212>  DNA
<213>  Homo sapiens

<400>  2
tttgctagct actgccgaat ccaggtctcc gggcttaaca acaacgaagg ggctgtgact       60

ggctgctttc tcaaccaatc agcaccgaac tcatttgcat gggctgagaa caaatgttcg      120

cgaactctag aaatgaatga cttaagtaag ttccttagaa tattattttt cctactgaaa      180

gttaccacat gcgtcgttgt ttatacagta ataggaacaa gaaaaaagtc acctaagctc      240

accctcatca attgtggagt tcctttatat cccatcttct ctccaaacac atacgcagcg      300

aaccacccga ccccgtccca accccgcgtc ctaaattttt ggagtaggct ttctggcttt      360

ttaccggaaa gcccctctta tgatgtttgt tgccaatgat agattgtttt cactgtgcaa      420

aaattatggg tagttttggt ggtcttgatg cagttgtaag cttggggact agttt           475


<210>  3
<211>  483
<212>  DNA
<213>  Homo sapiens

<400>  3
tttgctagct actgccgaat ccaggtctcc gggcttaaca acaacgaagg ggctgtgact       60

ggctgctttc tcaaccaatc agcaccgaac tcatttgcat gggctgagaa caaatgttcg      120

cgaactctag aaatgaatga cttaagtaag ttccttagaa tattattttt cctactgaaa      180

gttaccacat gcgtcgttgt ttatacagta ataggaacaa gaaaaaagtc acctaagctc      240

accctcatca attgtggagt tcctttatat cccatcttct ctccaaacac atacgcaggc      300

acgtcagccg gggtgcgcac tgcgcgcagg tctagtcagg aaatttttgg agtaggcttt      360

ctggcttttt accggaaagc ccctcttatg atgtttgttg ccaatgatag attgttttca      420

ctgtgcaaaa attatgggta gttttggtgg tcttgatgca gttgtaagct tggggactag      480

ttt                                                                    483


<210>  4
<211>  470
<212>  DNA
<213>  Homo sapiens

<400>  4
tttgctagct actgccgaat ccaggtctcc gggcttaaca acaacgaagg ggctgtgact       60

ggctgctttc tcaaccaatc agcaccgaac tcatttgcat gggctgagaa caaatgttcg      120

cgaactctag aaatgaatga cttaagtaag ttccttagaa tattattttt cctactgaaa      180

gttaccacat gcgtcgttgt ttatacagta ataggaacaa gaaaaaagtc acctaagctc      240

accctcatca attgtggagt tcctttatat cccatcttct ctccaaacac atacgcaggg      300

agggggcatt ttaatatatc tctgaactaa tttttggagt aggctttctg gctttttacc      360

ggaaagcccc tcttatgatg tttgttgcca atgatagatt gttttcactg tgcaaaaatt      420

atgggtagtt ttggtggtct tgatgcagtt gtaagcttgg ggactagttt                 470


<210>  5
<211>  2347
<212>  DNA
<213>  Homo sapiens


<220>
<221>  5'UTR
<222>  (1)..(300)

<220>
<221>  misc_feature
<222>  (1)..(1582)
<223>  Exon 1

<220>
<221>  misc_feature
<222>  (301)..(1575)
<223>  DUX4 open reading frame (protein coding)

<220>
<221>  misc_binding
<222>  (1540)..(1571)
<223>  779 sequence binding site

<220>
<221>  misc_binding
<222>  (1573)..(1607)
<223>  778 sequence binding site

<220>
<221>  Intron
<222>  (1583)..(1718)
<223>  Intron 1

<220>
<221>  misc_feature
<222>  (1719)..(1811)
<223>  Exon 2

<220>
<221>  Intron
<222>  (1812)..(2174)
<223>  Intron 2

<220>
<221>  misc_feature
<222>  (2175)..(2347)
<223>  Exon 3

<400>  5
ccaccccccc cccccaccac caccaccacc accaccccgc cggccggccc caggcctcga       60

cgccctgggt cccttccggg gtggggcggg ctgtcccagg ggggctcacc gccattcatg      120

aaggggtgga gcctgcctgc ctgtgggcct ttacaagggc ggctggctgg ctggctggct      180

gtccgggcag gcctcctggc tgcacctgcc gcagtgcaca gtccggctga ggtgcacggg      240

agcccgccgg cctctctctg cccgcgtccg tccgtgaaat tccggccggg gctcaccgcg      300

atggccctcc cgacaccctc ggacagcacc ctccccgcgg aagcccgggg acgaggacgg      360

cgacggagac tcgtttggac cccgagccaa agcgaggccc tgcgagcctg ctttgagcgg      420

aacccgtacc cgggcatcgc caccagagaa cggctggccc aggccatcgg cattccggag      480

cccagggtcc agatttggtt tcagaatgag aggtcacgcc agctgaggca gcaccggcgg      540

gaatctcggc cctggcccgg gagacgcggc ccgccagaag gccggcgaaa gcggaccgcc      600

gtcaccggat cccagaccgc cctgctcctc cgagcctttg agaaggatcg ctttccaggc      660

atcgccgccc gggaggagct ggccagagag acgggcctcc cggagtccag gattcagatc      720

tggtttcaga atcgaagggc caggcacccg ggacagggtg gcagggcgcc cgcgcaggca      780

ggcggcctgt gcagcgcggc ccccggcggg ggtcaccctg ctccctcgtg ggtcgccttc      840

gcccacaccg gcgcgtgggg aacggggctt cccgcacccc acgtgccctg cgcgcctggg      900

gctctcccac agggggcttt cgtgagccag gcagcgaggg ccgcccccgc gctgcagccc      960

agccaggccg cgccggcaga ggggatctcc caacctgccc cggcgcgcgg ggatttcgcc     1020

tacgccgccc cggctcctcc ggacggggcg ctctcccacc ctcaggctcc tcgctggcct     1080

ccgcacccgg gcaaaagccg ggaggaccgg gacccgcagc gcgacggcct gccgggcccc     1140

tgcgcggtgg cacagcctgg gcccgctcaa gcggggccgc agggccaagg ggtgcttgcg     1200

ccacccacgt cccaggggag tccgtggtgg ggctggggcc ggggtcccca ggtcgccggg     1260

gcggcgtggg aaccccaagc cggggcagct ccacctcccc agcccgcgcc cccggacgcc     1320

tccgcctccg cgcggcaggg gcagatgcaa ggcatcccgg cgccctccca ggcgctccag     1380

gagccggcgc cctggtctgc actcccctgc ggcctgctgc tggatgagct cctggcgagc     1440

ccggagtttc tgcagcaggc gcaacctctc ctagaaacgg aggccccggg ggagctggag     1500

gcctcggaag aggccgcctc gctggaagca cccctcagcg aggaagaata ccgggctctg     1560

ctggaggagc tttaggacgc ggggttggga cggggtcggg tggttcgggg cagggccgtg     1620

gcctctcttt cgcggggaac acctggctgg ctacggaggg gcgtgtctcc gccccgcccc     1680

ctccaccggg ctgaccggcc tgggattcct gccttctagg tctaggcccg gtgagagact     1740

ccacaccgcg gagaactgcc attctttcct gggcatcccg gggatcccag agccggccca     1800

ggtaccagca ggtgggccgc ctactgcgca cgcgcgggtt tgcgggcagc cgcctgggct     1860

gtgggagcag cccgggcaga gctctcctgc ctctccacca gcccaccccg ccgcctgacc     1920

gccccctccc caccccccac cccccacccc cggaaaacgc gtcgtcccct gggctgggtg     1980

gagacccccg tcccgcgaaa caccgggccc cgcgcagcgt ccgggcctga ctccgctccg     2040

gcggctcgcc tcctgtgtgc ccccgcgcca ccgtcgcccg cccgcccggg cccctgcagc     2100

ctcccagctg ccagcgcgga gctcctggcg gtcaaaagca tacctctgtc tgtctttgcc     2160

cgcttcctgg ctagacctgc gcgcagtgcg caccccggct gacgtgcaag ggagctcgct     2220

ggcctctctg tgcccttgtt cttccgtgaa attctggctg aatgtctccc cccaccttcc     2280

gacgctgtct aggcaaacct ggattagagt tacatctcct ggatgattag ttcagagata     2340

tattaaa                                                               2347


