                         SEQUENCE LISTING

<110>  The University of North Carolina at Chapel Hill
       Hirsch, Matthew L.
       Samulski, Richard J.
 
<120>  AAV-IDUA Vector for Treatment of MPS I-Associated Blindness

<130>  5470-772WO

<150>  US 62/298,126
<151>  2016-02-22

<160>  3     

<170>  PatentIn version 3.5

<210>  1
<211>  1993
<212>  DNA
<213>  Homo sapiens

<400>  1
caccggtcgc caccatgcga ccactgagac cacgggccgc tctgctggct ctgctggctt       60

cactgctggc cgctccccct gtcgctcctg ctgaggctcc ccacctggtg catgtggacg      120

cagctcgcgc cctgtggcca ctgaggagat tctggaggag cacaggcttt tgcccacctc      180

tgcctcacag ccaggctgac cagtacgtgc tgtcctggga tcagcagctg aacctggcat      240

atgtgggagc cgtcccccac agggggatca aacaggtgag aactcattgg ctgctggagc      300

tggtcaccac acgaggatct actggaaggg ggctgagtta caacttcacc cacctggacg      360

gctatctgga tctgctgaga gagaatcagc tgctgcctgg atttgaactg atgggctcag      420

ccagcggaca tttcaccgac tttgaggata agcagcaggt gttcgaatgg aaagacctgg      480

tcagctccct ggctcggcgc tacattgggc ggtatggcct ggcacacgtg agtaagtgga      540

actttgagac ttggaatgaa ccagaccacc atgacttcga taacgtgtca atgaccatgc      600

aggggtttct gaattactat gatgcctgct ccgagggcct gcgggcagcc tctccagctc      660

tgcgactggg aggaccaggc gattccttcc acacaccacc cagaagtccc ctgtcatggg      720

gcctgctgcg gcactgtcat gacggaacca acttctttac aggagaagca ggggtgagac      780

tggattacat ctccctgcat cgaaaggggg ccaggtctag tatctctatt ctggagcagg      840

aaaaggtggt cgctcagcag atccggcagc tgttccccaa atttgccgac acacctatct      900

acaatgacga ggctgatcct ctggtgggat ggtctctgcc tcagccatgg cgagccgatg      960

tgacttatgc tgcaatggtg gtcaaagtca ttgctcagca ccagaacctg ctgctggcaa     1020

atactaccag tgctttccca tacgcactgc tgagtaacga caatgccttc ctgtcatatc     1080

acccccatcc ttttgcccag agaacactga ctgctcggtt tcaggtgaac aatacccgac     1140

ctccacatgt gcagctgctg aggaagcctg tcctgacagc catgggcctg ctggctctgc     1200

tggacgagga acagctgtgg gcagaggtgt ctcaggccgg gactgtcctg gatagtaacc     1260

acaccgtggg cgtcctggct tctgcacatc gacctcaggg accagcagac gcttggcgag     1320

cagctgtgct gatctacgca tcagacgata cacgagcaca ccctaaccga agcgtggcag     1380

tcactctgcg actgcgagga gtgccacctg gaccaggact ggtgtacgtc acccgctatc     1440

tggacaatgg cctgtgctct cccgatggag agtggcgaag gctggggagg cccgtgttcc     1500

ctacagcaga gcagtttaga cggatgagag cagccgaaga tccagtggct gcagcaccac     1560

gaccactgcc tgcaggaggc agactgaccc tgcggccagc cctgcgcctg ccaagcctgc     1620

tgctggtgca cgtctgcgca aggcctgaaa agccacccgg acaggtgaca aggctgagag     1680

ctctgccact gactcaggga cagctggtgc tggtctggtc agacgagcat gtggggagca     1740

aatgtctgtg gacttacgaa attcagttca gccaggatgg gaaggcctat acccctgtga     1800

gccggaaacc cagcaccttc aacctgttcg tcttttcccc agacaccggg gccgtgtccg     1860

gctcttaccg ggtccgcgct ctggactatt gggcaaggcc aggccccttc agcgatcctg     1920

tgccatacct ggaagtgcct gtgcctcgcg gcccaccatc tcctggaaac ccttgagggg     1980

atccgtcgac tag                                                        1993


<210>  2
<211>  20
<212>  DNA
<213>  Artificial

<220>
<223>  qPCR primer

<400>  2
caagtacgcc ccctattgac                                                   20


<210>  3
<211>  20
<212>  DNA
<213>  Artificial

<220>
<223>  qPCR primer

<400>  3
aagtcccgtt gattttggtg                                                   20


