                         SEQUENCE LISTING

<110>  RaNA Therapeutics, Inc.
 
<120>  METHODS FOR IDENTIFYING AND TARGETING NON-CODING RNA SCAFFOLDS

<130>  R0693.70035WO00

<140>  Not Yet Assigned
<141>  Concurrently Herewith

<150>  US 62/369,729
<151>  2016-08-01

<150>  US 62/343,335
<151>  2016-05-31

<150>  US 62/242,863
<151>  2015-10-16

<160>  53    

<170>  PatentIn version 3.5

<210>  1
<211>  441
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  SMN AS 4263 region EMSA probe

<400>  1
tcccctaaac aaagacgagg tcttgctatg ttgcccagac tggtctcaaa ctcctgagct       60

caagtgatcc tcctgcctca gccttctaaa atgccgggat tacaggcatg agccactgta      120

cctggcctta aatttcttaa catagctagc atttggagaa aaccaaccaa taacaacaaa      180

agaccaacaa aattaaattt aacgaggacg aaaagacagc aagtgacata aaaagtttaa      240

acattttgat ttagactatg tatctgttcc actatgaagc tatgagtaaa aaaaaaaaat      300

caagcataaa tactttcatg cttttcctta atacacacac acacacacac acacacacag      360

ctcacatagc atttcgaggg cgattttaag taaatgtctt gggtagaaca cctgttctaa      420

ccccatccca atacacagta t                                                441


<210>  2
<211>  441
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  SMN AS neg. control

<400>  2
aaaatcagcc ccctgagacc aatgaagcat gatgtatata ttctaagagg gtacatcatt       60

ttagattcaa gaaactgtaa tataatgtaa gcctcaataa gaacattatc acagaaaatc      120

ttaaaacttt tggtgagtca tgcttgtttt ttgaaaatga ctgcctaggc taggcgcctg      180

taatcctagc actttggaag gccaaggtgg ggagatcact tgaggtcagg agttcaagac      240

cagcctggcc aacatggtga aaccccatct ctactaaaaa tacaaaataa gccgggtgtg      300

gtggcgggtg cctgtaatct cagctacttg ggaggctgaa gcaggagaat cacttgaacc      360

caggaggtgg aagttgcagt gagctgaaat ggtgccactg cactccagcc tgagcgacag      420

agcaagactc catctcgaaa a                                                441


<210>  3
<211>  441
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  MBP 1-441 nt

<400>  3
gaagaaggta aactggtaat ctggattaac ggcgataaag gctataacgg tctcgctgaa       60

gtcggtaaga aattcgagaa agataccgga attaaagtca ccgttgagca tccggataaa      120

ctggaagaga aattcccaca ggttgcggca actggcgatg gccctgacat tatcttctgg      180

gcacacgacc gctttggtgg ctacgctcaa tctggcctgt tggctgaaat caccccggac      240

aaagcgttcc aggacaagct gtatccgttt acctgggatg ccgtacgtta caacggcaag      300

ctgattgctt acccgatcgc tgttgaagcg ttatcgctga tttataacaa agatctgctg      360

ccgaacccgc caaaaacctg ggaagagatc ccggcgctgg ataaagaact gaaagcgaaa      420

ggtaagagcg cgctgatgtt c                                                441


<210>  4
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  4
cataguggaa cagat                                                        15


<210>  5
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  5
agatgcagtg ctctt                                                        15


<210>  6
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  6
agaugcagtg cucut                                                        15


<210>  7
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  7
cataguggaa cagat                                                        15


<210>  8
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  8
tcactttcat aatgctgg                                                     18


<210>  9
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  9
catagtggaa cagat                                                        15


<210>  10
<211>  40
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  10
taatacgact cactatagtc ccctaaacaa agacgaggtc                             40


<210>  11
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  11
atactgtgta ttgggatggg gt                                                22


<210>  12
<211>  40
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  12
taatacgact cactatagaa aatcagcccc ctgagaccaa                             40


<210>  13
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  13
ttttcgagat ggagtcttgc tctg                                              24


<210>  14
<211>  46
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  14
taatacgact cactatagat tgtttatata ttcttgccca tcgggg                      46


<210>  15
<211>  68
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  15
cacaaaacca tatttccatc caccaagcta atacgactca ctatagatga aaataaaaac       60

aggtgcac                                                                68


<210>  16
<211>  29
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  16
cagatctttg ttataaatca gcgataacg                                         29


<210>  17
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  17
gcagtgctct tgtagtccca                                                   20


<210>  18
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  18
cctccttatg gcatagacac c                                                 21


<210>  19
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  19
cctccttatg gcatagacac c                                                 21


<210>  20
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  20
cttctgccag gaaagaaggc aacc                                              24


<210>  21
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  21
gctgatgctt tgggaagtat gtta                                              24


<210>  22
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  22
caccttcctt ctttttgatt ttgtc                                             25


<210>  23
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  23
tacatgagtg gctatcatac t                                                 21


<210>  24
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  24
tggaccacca ataattcccc                                                   20


<210>  25
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  25
atgccagcat ttccatataa tagcc                                             25


<210>  26
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  26
tccagattct cttgatgatg                                                   20


<210>  27
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  27
catttgtgaa acttcgggta aacca                                             25


<210>  28
<211>  28
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  28
gtaaggaagc tgcagtattc ttcttttg                                          28


<210>  29
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  29
cacacctaaa agaaaacc                                                     18


<210>  30
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  30
tttacccagc taccattgct tcaa                                              24


<210>  31
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  31
cggacagatt ttgctcctct ctatt                                             25


<210>  32
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  32
acctgtgttg tggtttac                                                     18


<210>  33
<211>  26
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  33
ccttctggac caccagtaag taaaaa                                            26


<210>  34
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  34
gggatgttct acaatgacat tttacaatcc                                        30


<210>  35
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  35
ttgctttcac atacaatttg                                                   20


<210>  36
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  36
atcactcagc atcttttcct gacaa                                             25


<210>  37
<211>  45
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  37
gcctcagaca gttgtatttt tttattttta ttttttagta atata                       45


<210>  38
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  38
atgtgacttt gttttgtaaa ttta                                              24


<210>  39
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  39
aaaatgtctt gtgaaacaaa atgcttttta                                        30


<210>  40
<211>  30
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  40
ccttcttttt gattttgtct gaaacctgta                                        30


<210>  41
<211>  26
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  41
aaaataaagg aagttaaaaa aaatag                                            26


<210>  42
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  42
cggtggtgag gcagttga                                                     18


<210>  43
<211>  32
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  43
cccttctcac agctcataaa attaccaata at                                     32


<210>  44
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  44
aatccacatt caaattttc                                                    19


<210>  45
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  45
tcccattttg taggttgcct gtt                                               23


<210>  46
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  46
actaaagagc ttctgcacag caaa                                              24


<210>  47
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  47
cactctgatg gtagtttct                                                    19


<210>  48
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  48
cagcctcctg agtagctagg atta                                              24


<210>  49
<211>  26
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  49
ggtgaaaccc cgtctctact aaaaaa                                            26


<210>  50
<211>  17
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  50
caggcacacg ccaccat                                                      17


<210>  51
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  51
gagacttcag cagtcacagt gat                                               23


<210>  52
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  52
ggaggagagc gctgtaact                                                    19


<210>  53
<211>  16
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic polynucleotide

<400>  53
tccggtgcac atccta                                                       16


