
                                SEQUENCE LISTING

<110> Sarepta Therapeutics, Inc.
      Hanson, Gunnar J.
      Schnell, Frederick Joseph
      Dworzak, Johannes Christian
      Mourich, Dan V.

<120> METHODS AND COMPOUNDS FOR TREATMENT OF
  LYMPHOCYTE-RELATED DISEASES AND CONDITIONS
  

<130> 120178.50001WO

<140> PCT                 
<141> 2016-06-03  

<150> US 62/171,102       
<151> 2015-06-04  

<160> 12

<170> FastSEQ for Windows Version 4.0

<210> 1
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> A PMO designed to restore correct splicing in the
      enhanced green fluorescent protein (EGFP) gene

<400> 1
gctattacct taacccag                                                    18

<210> 2
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence
      
<220> 
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<400> 2
gctattacct taacccag                                                    18

<210> 3
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence
      
<220> 
<221> modified_base  
<222> (1)...(1)
<223> Guanidine

<220> 
<221> modified_base  
<222> (2)...(2)
<223> modified intersubunit linkage G-pip

<220> 
<221> modified_base  
<222> (5)...(5)
<223> modified intersubunit linkage G-pip

<220> 
<221> modified_base  
<222> (10)...(10)
<223> modified intersubunit linkage G-pip

<220> 
<221> modified_base  
<222> (18)...(18)
<223> Trityl

<400> 3
gctattacct taacccag                                                    18

<210> 4
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence
 
<220>      
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<220> 
<221> modified_base  
<222> (2)...(2)
<223> modified intersubunit linkage map

<220> 
<221> modified_base  
<222> (4)...(4)
<223> modified intersubunit linkage map

<220> 
<221> modified_base  
<222> (5)...(5)
<223> modified intersubunit linkage map

<220> 
<221> misc_structure 
<222> (10)...(10)
<223> modified intersubunit linkage map


<400> 4
gctattacct taacccag                                                    18

<210> 5
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence
 
<220>      
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<220> 
<221> modified_base  
<222> (2)...(2)
<223> modified intersubunit linkage map

<220> 
<221> modified_base  
<222> (4)...(4)
<223> modified intersubunit linkage map

<220> 
<221> modified_base  
<222> (5)...(5)
<223> modified intersubunit linkage map

<220> 
<221> modified_base  
<222> (9)...(9)
<223> modified intersubunit linkage map

<220> 
<221> modified_base  
<222> (10)...(10)
<223> modified intersubunit linkage map


<400> 5
gctattacct taacccag                                                    18

<210> 6
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence

<220> 
<221> modified_base  
<222> (1)...(1)
<223> modified intersubunit linkage morph and 
      ethylene glycol trimer

<220> 
<221> modified_base  
<222> (2)...(2)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (3)...(3)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (4)...(4)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (5)...(5)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (6)...(6)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (7)...(7)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (8)...(8)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (9)...(9)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (10)...(10)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (11)...(11)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (12)...(12)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (13)...(13)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (14)...(14)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (15)...(15)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (16)...(16)
<223> modified intersubunit linkage morph

<220> 
<221> modified_base  
<222> (17)...(17)
<223> modified intersubunit linkage morph

<400> 6
gctattacct taacccag                                                    18

<210> 7
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence

<220>      
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<220> 
<221> modified_base  
<222> (2)...(2)
<223> modified intersubunit linkage MG-pip

<220> 
<221> modified_base  
<222> (4)...(4)
<223> modified intersubunit linkage MG-pip

<220> 
<221> modified_base  
<222> (5)...(5)
<223> modified intersubunit linkage MG-pip

<220> 
<221> modified_base  
<222> (10)...(10)
<223> modified intersubunit linkage MG-pip

<220>
<221> modified_base  
<222> (18)...(18)
<223> (NH)NH2


<400> 7
gctattacct taacccag                                                    18

<210> 8
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence
    
<220> 
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<220> 
<221> modified_base  
<222> (2)...(2)
<223> modified intersubunit linkage MG-pip

<220> 
<221> modified_base  
<222> (4)...(4)
<223> modified intersubunit linkage MG-pip

<220> 
<221> modified_base  
<222> (5)...(5)
<223> modified intersubunit linkage MG-pip

<220> 
<221> modified_base  
<222> (9)...(9)
<223> modified intersubunit linkage MG-pip

<220> 
<221> modified_base  
<222> (10)...(10)
<223> modified intersubunit linkage MG-pip

<220> 
<221> modified_base  
<222> (18)...(18)
<223> (NH)NH2

<400> 8
gctattacct taacccag                                                    18


<210> 9
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence
 
<220>      
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<220> 
<221> modified_base  
<222> (18)...(18)
<223> (Arg aminohexanoic acid Arg Arg beta-alanine Arg
      Arg aminohexanoic acid Arg Arg beta-alanine Arg
      aminohexanoic acid beta alanine

<400> 9
gctattacct taacccag                                                    18

<210> 10
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence

<220> 
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<220> 
<221> modified_base  
<222> (18)...(18)
<223> Arg Arg Arg Arg Arg Arg Gly

<400> 10
gctattacct taacccag                                                    18

<210> 11
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence

<220> 
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<220> 
<221> modified_base  
<222> (2)...(2)
<223> modified intersubunit linkage guanidinyl

<220> 
<221> modified_base  
<222> (5)...(5)
<223> modified intersubunit linkage guanidinyl

<220> 
<221> modified_base  
<222> (10)...(10)
<223> modified intersubunit linkage guanidinyl

<220> 
<221> modified_base  
<222> (18)...(18)
<223> Guanidinyl

<400> 11
gctattacct taacccag                                                    18

<210> 12
<211> 18
<212> DNA
<213> Artificial Sequence

<220> 
<223> Synthetic oligomer sequence

<220> 
<221> modified_base  
<222> (1)...(1)
<223> ethylene glycol trimer

<220> 
<221> modified_base  
<222> (2)...(2)
<223> modified intersubunit linkage apn

<220> 
<221> modified_base  
<222> (5)...(5)
<223> modified intersubunit linkage apn

<220> 
<221> modified_base  
<222> (10)...(10)
<223> modified intersubunit linkage apn

<400> 12
gctattacct taacccag                                                    18
