SEQUENCE LISTING

<110>   PROQR THERAPEUTICS II B.V.

<120>   OLIGONUCLEOTIDE THERAPY FOR LEBER CONGENITAL AMAUROSIS

<130>   P065863WO

<140>   PCT/EP2016/______
<141>   2016-02-26

<150>   GB-1503408.5 
<151>   2015-02-27

<160>   36

<170>   SeqWin2010, version 1.0

<210>   1
<211>   128
<212>   DNA
<213>   Homo sapiens

<400>   1
tagagatggg gtttcacctt gttagccagg atggtgtcga tctcctgaac tcgtgatcca  60
cccgcctcgg cctcctaaag tgctgggatt acagatgtga gccaccgcac ctggccccag  120
ttgtaatt                                                           128

<210>   2
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   2
gcgguggcuc acaucug                                                 17

<210>   3
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   3
gguggcucac aucugua                                                 17

<210>   4
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   4
ggcucacauc uguaauc                                                 17

<210>   5
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   5
ucaggagauc gacacca                                                 17

<210>   6
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   6
cacgaguuca ggagauc                                                 17

<210>   7
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   7
gguggaucac gaguuca                                                 17

<210>   8
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   8
uggcucacau cuguaau                                                 17

<210>   9
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   9
ugcgguggcu cacaucu                                                 17

<210>   10
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   10
cucacaauua caacugg                                                 17

<210>   11
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   11
gguaugagau acucaca                                                 17

<210>   12
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   12
ggauagguau gagauac                                                 17

<210>   13
<211>   31
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   13
cuggggccag gugcgguggc ucacaucugu a                                 31

<210>   14
<211>   25
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   14
gggauaggua ugagauacuc acaau                                        25

<210>   15
<211>   21
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   15
ccgaggcggg uggaucacga g                                            21

<210>   16
<211>   22
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   16
gguaugagau acucacaauu ac                                           22

<210>   17
<211>   31
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   17
gguaugagau acucacaauu acaacugggg c                                 31

<210>   18
<211>   20
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   18
taatcccagc actttaggag                                              20

<210>   19
<211>   16
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   19
gggccaggtg cggtgg                                                  16

<210>   20
<211>   17
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   20
aactggggcc aggtgcg                                                 17

<210>   21
<211>   18
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   21
tacaactggg gccaggtg                                                18

<210>   22
<211>   20
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   Antisense oligonucleotide

<400>   22
actcacaatt acaactgggg                                              20

<210>   23
<211>   23
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   primer

<400>   23
tgctaagtac agggacatct tgc                                          23

<210>   24
<211>   25
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   primer

<400>   24
agactccact tgttctttta aggag                                        25

<210>   25
<211>   26
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   primer

<400>   25
tgactgctaa gtacagggac atcttg                                       26

<210>   26
<211>   24
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   primer

<400>   26
aggagatgtt ttcacactcc aggt                                         24

<210>   27
<211>   23
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   primer

<400>   27
ctggccccag ttgtaatttg tga                                          23

<210>   28
<211>   24
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   primer

<400>   28
ctgttcccag gcttgttcaa tagt                                         24

<210>   29
<211>   17
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Sense oligonucleotide

<400>   29
cgcaccuggc cccaguu                                                 17

<210>   30
<211>   158
<212>   DNA
<213>   Homo sapiens

<400>   30
tagagatggg gtttcacctt gttagccagg atggtgtcga tctcctgaac tcgtgatcca  60
cccgcctcgg cctcctaaag tgctgggatt acagatgtga gccaccgcac ctggccccag  120
ttgtaattgt gaatatctca tacctatccc tattggca                          158

<210>   31
<211>   26
<212>   DNA
<213>   Homo sapiens

<400>   31
atggtgtcga tctcctgaac tcgtga                                       26

<210>   32
<211>   8
<212>   DNA
<213>   Artificial Sequence

<220>
<223>   Homo sapiens

<400>   32
atctcctg                                                           8

<210>   33
<211>   22
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Micro RNA

<400>   33
gcgguggcuc acaucuguaa uc                                           22

<210>   34
<211>   23
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   Micro RNA

<400>   34
gggcgcggug gcucacaucu gua                                          23

<210>   35
<211>   19
<212>   RNA
<213>   Artificial Sequence

<220>
<223>   siRNA

<400>   35
cgcgguggcu cacaucugu                                               19

<210>   36
<211>   8
<212>   DNA
<213>   Homo sapiens

<400>   36
caggagat                                                           8

