                         SEQUENCE LISTING

<110>  CASE WESTERN RESERVE UNIVERISTY
 
<120>  COMPOSITIONS AND METHODS OF TREATING USHER SYNDROME III

<130>  CWR-023879WO ORD

<160>  13    

<170>  PatentIn version 3.5

<210>  1
<211>  2978
<212>  DNA
<213>  Mus musculus

<400>  1
agtgggtgag gaaggatgct tcacggactg gcgttctgcc tggtggaacc actgtaagga       60

agggcagtgt ttttcagctg ctgtgataaa tgcagccgac ggggcagtcg ctacttgatg      120

ctcacaaagg tctttgtttt caagtttgtc tttaccgaag ccttttctcg tcatgccaag      180

ccagcagaag aagatcatct tttgcatggc tggcgtactg agctttctct gtgctcttgg      240

agtggtgaca gcagtgggca ccccactgtg ggttaaagcc actatcctct gcaaaacagg      300

ggctctgctt gtcaacgcgt cagggaagga gctggacaag ttcatgggcg agatgcagta      360

tggccttttc cacggagaag gcgtaaggca atgtgggtta ggagcaaggc ctttccggtt      420

ctcattcttc ccagatttgg tccaagccat ccccgtaagc atccacatca atattattct      480

cttctccatg attcttgtcg tcttaaccat ggtggggaca gccttcttca tgtacaatgc      540

ttttggcaag ccctttgaaa ctcttcatgg accactgggg ctctatctgg tcagcttcat      600

ttcaggctcc tgtggctgtc ttgtcatgat attgtttgcc tctgaagtga aagtccaccg      660

cctttcagag aaaattgcaa attttaaaga agggacctat gcctacagaa cacaaaacga      720

aaactatacc acctcattct gggttgtttt catttgcttt tttgttcatt ttttgaatgg      780

gctcctgata cgacttgctg gatttcagtt ccctttcaca aaatctaaag aaacagagac      840

cactaatgta gcttcagatt taatgtactg aaaagcaaat atcttcataa tttctcaata      900

aggatatgga cttcctttgg ccacttttaa tatgggtgat ttcatctgtg catttagact      960

tcttaagtac caagccctcc ttatgttatg tttacagagc atgtagtaag gattcaggct     1020

ggaaaataac agaagcagga ggatggtttc actgggaaga cgttcttcct gatgggtaat     1080

ggcctgcata gttagtccaa agcagttggc tagatggacg gatggttact ccatgtcctt     1140

actgaccgat aagatgcacg ttctcccaag cagaactcaa caggcacatg acatacagtt     1200

ttgtaagact ccagggagcc ttaacttacc agggaccccc tgagtggacc acgtggagct     1260

gggatcaatg caaaaagcaa gaggaattta ttgttccagt gcactggggt tgtcccagat     1320

caacagtgct ggcagcgacc cccagcacct tttcagtgag tttttatacg gtttctaggg     1380

gcagaataga gcatcagcaa ctaggcacaa tatgattgat ggaacagtgc accctttaaa     1440

ctgattggtc tttaaggaat gaggtgacaa ggacttccgt tgtctgatgg tggaggtcct     1500

gtggagtgtg tccccacaca caggtcagtt cctgtccttt agtctgagaa atgttaatta     1560

gcctctccct tccagagggg gacgtattcc atgaccttcc caaagttctt gagctgacct     1620

attcagttaa ataaaacaga cgttatttct aattgtccac atagtcacag atcccagaaa     1680

acagaggtga aattggtgtc ttaaactgac agtgcaccga atcattgcaa accttcaagt     1740

tctttgtaag tttgcttaga gcatgatgtc attatgtctg gtggtcaaaa ccagaaaagt     1800

ttataagcaa acaagcaagc tagcaagaaa ggaagaaaaa ggaaaggaag aaaggaagaa     1860

aggaagaaag gaagaaagga aggaaggaag gaaggaagga aggaaggaag gaaggaagac     1920

ggaaagaagc agatcaatgg tttctttcct tatgcatctg agttcataac aatggtactt     1980

acagtggaca gaatccctac tagacaagtt ggtgagagaa acccactggg aactgtttcc     2040

agcttggtgt ctttggcact aatgagctcc aaatcatgaa aattcagaat tgaggtggga     2100

ttgcagtgtg tcatgggaga catgaagcat ggcccaagtc aaatctttct ccttgaatta     2160

ttcaccaaat gaatctgctg gagaccagag gccacaagtg agcctgaaac tgacactcct     2220

taactctcaa tgtgttaccc tcaggaaaga acaaaggaca aagacattat ggtgccctgg     2280

ccacaaacac cagagatcat agagtttgga aatgctccag aaaaccaatc tggaactagg     2340

aagatggctc agttgataaa gggctgcctc aaaagcttga gagcctgagt tcagattccc     2400

cagcacccat gagaaacgca tgggtttcat acatgtctgt gatcccagca ctgggaaggc     2460

agagctaggc aagtcttaaa gctcaccagc aagccaagtc aaacctaatc agtgcactcc     2520

aaggtcagtg agagaccctg actcaaaaca aaaaaacgga ggtgatggag aaaggcacca     2580

tcagcctcca tgaaccccct catgagcaca cacattttca tttgggaaca atttacatac     2640

aaggaaggag agactgcaca cctgaaatat aaccagctct ggtgatggcc tgctggttac     2700

tctcagacat cagaacatac ttgcttttct caggatggag tcctttcacc ttaattcagg     2760

acactggaag tttctagaag cccaccagct agtctgtcca ggagctggtg catgctttgg     2820

tgatgggcta gtagtgccct gacctggagg tcagaccctg aaattctcaa gcacaaaagg     2880

ctgtgttagg agggaaaggg agggagttga aggctggagg atgaatcccc ctcctctggc     2940

ctccatctac ctctttcctc tctgctcaga ggtctgaa                             2978


<210>  2
<211>  2352
<212>  DNA
<213>  Homo sapiens

<400>  2
tgaaggcagt ttgaaagact tgttttacag attcttagtc caaagatttc caattaggga       60

gaagaagcag cagaaaagga gaaaagccaa gtatgagtga tgatgaggcc ttcatctact      120

gacatttaac ctggcgagaa ccgtcgatgg tgaagttgcc ttttcagctg ggagctgtcc      180

gttcagcttc cgtaataaat gcagtcaaag aggcagtccc ttcccattgc tcacaaaggt      240

cttgtttttg aacctcgccc tcacagaagc cgtttctcat catgccaagc caacagaaga      300

aaatcatttt ttgcatggcc ggagtgttca gttttgcatg tgccctcgga gttgtgacag      360

ccttggggac accgttgtgg atcaaagcca ctgtcctctg caaaacggga gctctgctcg      420

tcaatgcctc agggcaggag ctggacaagt ttatgggtga aatgcagtac gggcttttcc      480

acggagaggg tgtgaggcag tgtgggttgg gagcaaggcc ctttcggttc tcattttttc      540

cagatttgct caaagcaatc ccagtgagca tccacgtcaa tgtcattctc ttctctgcca      600

tccttattgt gttaaccatg gtggggacag ccttcttcat gtacaatgct tttggaaaac      660

cttttgaaac tctgcatggt cccctagggc tgtacctttt gagcttcatt tcaggctcct      720

gtggctgtct tgtcatgata ttgtttgcct ctgaagtgaa aatccatcac ctctcagaaa      780

aaattgcaaa ttataaagaa gggacttatg tctacaaaac gcaaagtgaa aaatatacca      840

cctcattctg ggtcattttc ttttgctttt ttgttcattt tctgaatggg ctcctaatac      900

gacttgctgg atttcagttc ccttttgcaa aatctaaaga cgcagaaaca actaatgtag      960

ctgcagatct aatgtactga aaggcaaacc tttctataat tttacaaggg agtagacttg     1020

ctttggtcac ttttagatgt ggttaatttt gcatatcctt ttagtctgca tatattaaag     1080

catcaggacc cttcgtgaca atgtttacaa attacgtact aaggatacag gctggaaagt     1140

aagggaagca gaaggaaggc tttgaaaagt tgttttatct ggtgggaaat tgcttgaccc     1200

aggtagtcaa aggcagttga ctagaatcga caaattgtta ctccatatat atatatgtgt     1260

gtgtgtgtgt gtgtgtgtgt gtgtaagatg tcttcctatc aaaaagatat caaaggcaca     1320

tggaatatat tttaataaaa acaaataata tctctaatat atccacacat ttgttgccag     1380

atttcagaaa actgagctgc aatcgctttc ctaaaacagt agtgtattaa atgaacatct     1440

ataaaatgta tcaacacaca ttttaaaaaa tttgtttaaa gtatactctt aggccaggcg     1500

tggtgactca cacctgtaat tccagcactt caggaggcca aggtgggaag atcatttgag     1560

ttcaggagtt cgagttacag cctgggcaat aaagtgagac cctgtcacta acaaaattaa     1620

aaaataaaat aaatataaaa tataggcttt aaaaaagcat agtcttatta accatgtctg     1680

ttggtcaaaa tctgcaaact ctaaaagaag aaaagaagaa aaaaccaagc ttagggtatt     1740

tttcctcccg tgcctgagtc ccaattacat tcacgacagt actttcaatg aacataattg     1800

ttaggaccac tgaggaatca tgaaaaatga tctctgctta gtacatttga tgcaaaatga     1860

cttattaggg gctgtttttc tagctatagt gtctcgagta ctaatatgca attatgaaaa     1920

ttatattaaa tctgggatta tgacggtatc actgtatcat cttggtcttg ttctggctgt     1980

caccaagcat gacccaggtc aacttttttt ttcccctgaa ttacccatca aattgatctg     2040

cagctgacta aaggccacag ctgagcctgg aactgaccct tccttcatcc tcaacctgct     2100

gtcctccaga aagcaccaag gaaaaagcag agaatgacag caaacagatc actaggcctc     2160

tgaccacagg tgctgagtac tcagcagccc tcatataata ggtttgaaag tactccttaa     2220

aataaaacac tgtttccctt tggaactatt tacaaggatg aaacaaccgt atacctgaga     2280

aataacttgc tctggtgtca attcgctatt cgccagcaga catcagaaca caccgagttt     2340

ccagatgctg aa                                                         2352


<210>  3
<211>  699
<212>  DNA
<213>  Mus musculus

<400>  3
atgccaagcc agcagaagaa gatcatcttt tgcatggctg gcgtactgag ctttctctgt       60

gctcttggag tggtgacagc agtgggcacc ccactgtggg ttaaagccac tatcctctgc      120

aaaacagggg ctctgcttgt caacgcgtca gggaaggagc tggacaagtt catgggcgag      180

atgcagtatg gccttttcca cggagaaggc gtaaggcaat gtgggttagg agcaaggcct      240

ttccggttct cattcttccc agatttggtc caagccatcc ccgtaagcat ccacatcaat      300

attattctct tctccatgat tcttgtcgtc ttaaccatgg tggggacagc cttcttcatg      360

tacaatgctt ttggcaagcc ctttgaaact cttcatggac cactggggct ctatctggtc      420

agcttcattt caggctcctg tggctgtctt gtcatgatat tgtttgcctc tgaagtgaaa      480

gtccaccgcc tttcagagaa aattgcaaat tttaaagaag ggacctatgc ctacagaaca      540

caaaacgaaa actataccac ctcattctgg gttgttttca tttgcttttt tgttcatttt      600

ttgaatgggc tcctgatacg acttgctgga tttcagttcc ctttcacaaa atctaaagaa      660

acagagacca ctaatgtagc ttcagattta atgtactga                             699


<210>  4
<211>  699
<212>  DNA
<213>  Homo sapiens

<400>  4
atgccaagcc aacagaagaa aatcattttt tgcatggccg gagtgttcag ttttgcatgt       60

gccctcggag ttgtgacagc cttggggaca ccgttgtgga tcaaagccac tgtcctctgc      120

aaaacgggag ctctgctcgt caatgcctca gggcaggagc tggacaagtt tatgggtgaa      180

atgcagtacg ggcttttcca cggagagggt gtgaggcagt gtgggttggg agcaaggccc      240

tttcggttct cattttttcc agatttgctc aaagcaatcc cagtgagcat ccacgtcaat      300

gtcattctct tctctgccat ccttattgtg ttaaccatgg tggggacagc cttcttcatg      360

tacaatgctt ttggaaaacc ttttgaaact ctgcatggtc ccctagggct gtaccttttg      420

agcttcattt caggctcctg tggctgtctt gtcatgatat tgtttgcctc tgaagtgaaa      480

atccatcacc tctcagaaaa aattgcaaat tataaagaag ggacttatgt ctacaaaacg      540

caaagtgaaa aatataccac ctcattctgg gtcattttct tttgcttttt tgttcatttt      600

ctgaatgggc tcctaatacg acttgctgga tttcagttcc cttttgcaaa atctaaagac      660

gcagaaacaa ctaatgtagc tgcagatcta atgtactga                             699


<210>  5
<211>  2107
<212>  DNA
<213>  Mus musculus

<400>  5
aaagcaaata tcttcataat ttctcaataa ggatatggac ttcctttggc cacttttaat       60

atgggtgatt tcatctgtgc atttagactt cttaagtacc aagccctcct tatgttatgt      120

ttacagagca tgtagtaagg attcaggctg gaaaataaca gaagcaggag gatggtttca      180

ctgggaagac gttcttcctg atgggtaatg gcctgcatag ttagtccaaa gcagttggct      240

agatggacgg atggttactc catgtcctta ctgaccgata agatgcacgt tctcccaagc      300

agaactcaac aggcacatga catacagttt tgtaagactc cagggagcct taacttacca      360

gggaccccct gagtggacca cgtggagctg ggatcaatgc aaaaagcaag aggaatttat      420

tgttccagtg cactggggtt gtcccagatc aacagtgctg gcagcgaccc ccagcacctt      480

ttcagtgagt ttttatacgg tttctagggg cagaatagag catcagcaac taggcacaat      540

atgattgatg gaacagtgca ccctttaaac tgattggtct ttaaggaatg aggtgacaag      600

gacttccgtt gtctgatggt ggaggtcctg tggagtgtgt ccccacacac aggtcagttc      660

ctgtccttta gtctgagaaa tgttaattag cctctccctt ccagaggggg acgtattcca      720

tgaccttccc aaagttcttg agctgaccta ttcagttaaa taaaacagac gttatttcta      780

attgtccaca tagtcacaga tcccagaaaa cagaggtgaa attggtgtct taaactgaca      840

gtgcaccgaa tcattgcaaa ccttcaagtt ctttgtaagt ttgcttagag catgatgtca      900

ttatgtctgg tggtcaaaac cagaaaagtt tataagcaaa caagcaagct agcaagaaag      960

gaagaaaaag gaaaggaaga aaggaagaaa ggaagaaagg aagaaaggaa ggaaggaagg     1020

aaggaaggaa ggaaggaagg aaggaagacg gaaagaagca gatcaatggt ttctttcctt     1080

atgcatctga gttcataaca atggtactta cagtggacag aatccctact agacaagttg     1140

gtgagagaaa cccactggga actgtttcca gcttggtgtc tttggcacta atgagctcca     1200

aatcatgaaa attcagaatt gaggtgggat tgcagtgtgt catgggagac atgaagcatg     1260

gcccaagtca aatctttctc cttgaattat tcaccaaatg aatctgctgg agaccagagg     1320

ccacaagtga gcctgaaact gacactcctt aactctcaat gtgttaccct caggaaagaa     1380

caaaggacaa agacattatg gtgccctggc cacaaacacc agagatcata gagtttggaa     1440

atgctccaga aaaccaatct ggaactagga agatggctca gttgataaag ggctgcctca     1500

aaagcttgag agcctgagtt cagattcccc agcacccatg agaaacgcat gggtttcata     1560

catgtctgtg atcccagcac tgggaaggca gagctaggca agtcttaaag ctcaccagca     1620

agccaagtca aacctaatca gtgcactcca aggtcagtga gagaccctga ctcaaaacaa     1680

aaaaacggag gtgatggaga aaggcaccat cagcctccat gaaccccctc atgagcacac     1740

acattttcat ttgggaacaa tttacataca aggaaggaga gactgcacac ctgaaatata     1800

accagctctg gtgatggcct gctggttact ctcagacatc agaacatact tgcttttctc     1860

aggatggagt cctttcacct taattcagga cactggaagt ttctagaagc ccaccagcta     1920

gtctgtccag gagctggtgc atgctttggt gatgggctag tagtgccctg acctggaggt     1980

cagaccctga aattctcaag cacaaaaggc tgtgttagga gggaaaggga gggagttgaa     2040

ggctggagga tgaatccccc tcctctggcc tccatctacc tctttcctct ctgctcagag     2100

gtctgaa                                                               2107


<210>  6
<211>  1372
<212>  DNA
<213>  Homo sapiens

<400>  6
aaggcaaacc tttctataat tttacaaggg agtagacttg ctttggtcac ttttagatgt       60

ggttaatttt gcatatcctt ttagtctgca tatattaaag catcaggacc cttcgtgaca      120

atgtttacaa attacgtact aaggatacag gctggaaagt aagggaagca gaaggaaggc      180

tttgaaaagt tgttttatct ggtgggaaat tgcttgaccc aggtagtcaa aggcagttga      240

ctagaatcga caaattgtta ctccatatat atatatgtgt gtgtgtgtgt gtgtgtgtgt      300

gtgtaagatg tcttcctatc aaaaagatat caaaggcaca tggaatatat tttaataaaa      360

acaaataata tctctaatat atccacacat ttgttgccag atttcagaaa actgagctgc      420

aatcgctttc ctaaaacagt agtgtattaa atgaacatct ataaaatgta tcaacacaca      480

ttttaaaaaa tttgtttaaa gtatactctt aggccaggcg tggtgactca cacctgtaat      540

tccagcactt caggaggcca aggtgggaag atcatttgag ttcaggagtt cgagttacag      600

cctgggcaat aaagtgagac cctgtcacta acaaaattaa aaaataaaat aaatataaaa      660

tataggcttt aaaaaagcat agtcttatta accatgtctg ttggtcaaaa tctgcaaact      720

ctaaaagaag aaaagaagaa aaaaccaagc ttagggtatt tttcctcccg tgcctgagtc      780

ccaattacat tcacgacagt actttcaatg aacataattg ttaggaccac tgaggaatca      840

tgaaaaatga tctctgctta gtacatttga tgcaaaatga cttattaggg gctgtttttc      900

tagctatagt gtctcgagta ctaatatgca attatgaaaa ttatattaaa tctgggatta      960

tgacggtatc actgtatcat cttggtcttg ttctggctgt caccaagcat gacccaggtc     1020

aacttttttt ttcccctgaa ttacccatca aattgatctg cagctgacta aaggccacag     1080

ctgagcctgg aactgaccct tccttcatcc tcaacctgct gtcctccaga aagcaccaag     1140

gaaaaagcag agaatgacag caaacagatc actaggcctc tgaccacagg tgctgagtac     1200

tcagcagccc tcatataata ggtttgaaag tactccttaa aataaaacac tgtttccctt     1260

tggaactatt tacaaggatg aaacaaccgt atacctgaga aataacttgc tctggtgtca     1320

attcgctatt cgccagcaga catcagaaca caccgagttt ccagatgctg aa             1372


<210>  7
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Construct

<400>  7
ccctctctca caccccatta                                                   20


<210>  8
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Construct

<400>  8
tgagaaccgg aaaggccttg c                                                 21


<210>  9
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Construct

<400>  9
tttaccgaag ccttttctcg                                                   20


<210>  10
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Construct

<400>  10
gtggccaaag gaagtccata                                                   20


<210>  11
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Construct

<400>  11
cggcgccatg gcatatgagg cc                                                22


<210>  12
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Construct

<400>  12
caagggcgag gagctgtt                                                     18


<210>  13
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic Construct

<400>  13
cttgtacagc tcgtccatgc                                                   20


