                         SEQUENCE LISTING

<110>  RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL
       Kaspar, Brian
 
<120>  MICROALGAE AS A NOVEL PLATFORM FOR PRODUCTION OF GENE THERAPY 
       VECTORS

<130>  28335/49063PCT

<150>  62/075,408
<151>  2014-11-05

<160>  4     

<170>  PatentIn version 3.5

<210>  1
<211>  1866
<212>  DNA
<213>  Adeno-Associated Virus 9

<400>  1
atgcccggct tctacgagat cgtgatcaag gtgcccagcg acctggacga gcacctgccc       60

ggcatcagcg acagcttcgt gaactgggtg gccgagaagg agtgggagct gccccccgac      120

agcgacatgg acctgaacct gatcgagcag gcccccctga ccgtggccga gaagctgcag      180

cgcgacttcc tgaccgagtg gcgccgcgtg agcaaggccc ccgaggccct gttcttcgtg      240

cagttcgaga agggcgagag ctacttccac atgcacgtgc tggtggagac caccggcgtg      300

aagagcatgg tgctgggccg cttcctgagc cagatccgcg agaagctgat ccagcgcatc      360

taccgcggca tcgagcccac cctgcccaac tggttcgccg tgaccaagac ccgcaacggc      420

gccggcggcg gcaacaaggt ggtggacgag tgctacatcc ccaactacct gctgcccaag      480

acccagcccg agctgcagtg ggcctggacc aacatggagc agtacctgag cgcctgcctg      540

aacctgaccg agcgcaagcg cctggtggcc cagcacctga cccacgtgag ccagacccag      600

gagcagaaca aggagaacca gaaccccaac agcgacgccc ccgtgatccg cagcaagacc      660

agcgcccgct acatggagct ggtgggctgg ctggtggaca agggcatcac cagcgagaag      720

cagtggatcc aggaggacca ggccagctac atcagcttca acgccgccag caacagccgc      780

agccagatca aggccgccct ggacaacgcc ggcaagatca tgagcctgac caagaccgcc      840

cccgactacc tggtgggcca gcagcccgtg gaggacatca gcagcaaccg catctacaag      900

atcctggagc tgaacggcta cgacccccag tacgccgcca gcgtgttcct gggctgggcc      960

accaagaagt tcggcaagcg caacaccatc tggctgttcg gccccgccac caccggcaag     1020

accaacatcg ccgaggccat cgcccacacc gtgcccttct acggctgcgt gaactggacc     1080

aacgagaact tccccttcaa cgactgcgtg gacaagatgg tgatctggtg ggaggagggc     1140

aagatgaccg ccaaggtggt ggagagcgcc aaggccatcc tgggcggcag caaggtgcgc     1200

gtggaccaga agtgcaagag cagcgcccag atcgacccca cccccgtgat cgtgaccagc     1260

aacaccaaca tgtgcgccgt gatcgacggc aacagcacca ccttcgagca ccagcagccc     1320

ctgcaggacc gcatgttcaa gttcgagctg acccgccgcc tggaccacga cttcggcaag     1380

gtgaccaagc aggaggtgaa ggacttcttc cgctgggcca aggaccacgt ggtggaggtg     1440

gagcacgagt tctacgtgaa gaagggcggc gccaagaagc gccccgcccc cagcgacgcc     1500

gacatcagcg agcccaagcg cgtgcgcgag agcgtggccc agcccagcac cagcgacgcc     1560

gaggccagca tcaactacgc cgaccgctac cagaacaagt gcagccgcca cgtgggcatg     1620

aacctgatgc tgttcccctg ccgccagtgc gagcgcatga accagaacag caacatctgc     1680

ttcacccacg gccagaagga ctgcctggag tgcttccccg tgagcgagag ccagcccgtg     1740

agcgtggtga agaaggccta ccagaagctg tgctacatcc accacatcat gggcaaggtg     1800

cccgacgcct gcaccgcctg cgacctggtg aacgtggacc tggacgactg catcttcgag     1860

cagtaa                                                                1866


<210>  2
<211>  1194
<212>  DNA
<213>  Adeno-Associated Virus 9

<400>  2
atggagctgg tgggctggct ggtggacaag ggcatcacca gcgagaagca gtggatccag       60

gaggaccagg ccagctacat cagcttcaac gccgccagca acagccgcag ccagatcaag      120

gccgccctgg acaacgccgg caagatcatg agcctgacca agaccgcccc cgactacctg      180

gtgggccagc agcccgtgga ggacatcagc agcaaccgca tctacaagat cctggagctg      240

aacggctacg acccccagta cgccgccagc gtgttcctgg gctgggccac caagaagttc      300

ggcaagcgca acaccatctg gctgttcggc cccgccacca ccggcaagac caacatcgcc      360

gaggccatcg cccacaccgt gcccttctac ggctgcgtga actggaccaa cgagaacttc      420

cccttcaacg actgcgtgga caagatggtg atctggtggg aggagggcaa gatgaccgcc      480

aaggtggtgg agagcgccaa ggccatcctg ggcggcagca aggtgcgcgt ggaccagaag      540

tgcaagagca gcgcccagat cgaccccacc cccgtgatcg tgaccagcaa caccaacatg      600

tgcgccgtga tcgacggcaa cagcaccacc ttcgagcacc agcagcccct gcaggaccgc      660

atgttcaagt tcgagctgac ccgccgcctg gaccacgact tcggcaaggt gaccaagcag      720

gaggtgaagg acttcttccg ctgggccaag gaccacgtgg tggaggtgga gcacgagttc      780

tacgtgaaga agggcggcgc caagaagcgc cccgccccca gcgacgccga catcagcgag      840

cccaagcgcg tgcgcgagag cgtggcccag cccagcacca gcgacgccga ggccagcatc      900

aactacgccg accgctacca gaacaagtgc agccgccacg tgggcatgaa cctgatgctg      960

ttcccctgcc gccagtgcga gcgcatgaac cagaacagca acatctgctt cacccacggc     1020

cagaaggact gcctggagtg cttccccgtg agcgagagcc agcccgtgag cgtggtgaag     1080

aaggcctacc agaagctgtg ctacatccac cacatcatgg gcaaggtgcc cgacgcctgc     1140

accgcctgcg acctggtgaa cgtggacctg gacgactgca tcttcgagca gtaa           1194


<210>  3
<211>  2211
<212>  DNA
<213>  Adeno-Associated Virus 9

<400>  3
atggccgccg acggctacct gcccgactgg ctggaggaca acctgagcga gggcatccgc       60

gagtggtggg ccctgaagcc cggcgccccc cagcccaagg ccaaccagca gcaccaggac      120

aacgcccgcg gcctggtgct gcccggctac aagtacctgg gccccggcaa cggcctggac      180

aagggcgagc ccgtgaacgc cgccgacgcc gccgccctgg agcacgacaa ggcctacgac      240

cagcagctga aggccggcga caacccctac ctgaagtaca accacgccga cgccgagttc      300

caggagcgcc tgaaggagga caccagcttc ggcggcaacc tgggccgcgc cgtgttccag      360

gccaagaagc gcctgctgga gcccctgggc ctggtggagg aggccgccaa gaccgccccc      420

ggcaagaagc gccccgtgga gcagagcccc caggagcccg acagcagcgc cggcatcggc      480

aagagcggcg cccagcccgc caagaagcgc ctgaacttcg gccagaccgg cgacaccgag      540

agcgtgcccg acccccagcc catcggcgag ccccccgccg cccccagcgg cgtgggcagc      600

ctgaccatgg ccagcggcgg cggcgccccc gtggccgaca acaacgaggg cgccgacggc      660

gtgggcagca gcagcggcaa ctggcactgc gacagccagt ggctgggcga ccgcgtgatc      720

accaccagca cccgcacctg ggccctgccc acctacaaca accacctgta caagcagatc      780

agcaacagca ccagcggcgg cagcagcaac gacaacgcct acttcggcta cagcaccccc      840

tggggctact tcgacttcaa ccgcttccac tgccacttca gcccccgcga ctggcagcgc      900

ctgatcaaca acaactgggg cttccgcccc aagcgcctga acttcaagct gttcaacatc      960

caggtgaagg aggtgaccga caacaacggc gtgaagacca tcgccaacaa cctgaccagc     1020

accgtgcagg tgttcaccga cagcgactac cagctgccct acgtgctggg cagcgcccac     1080

gagggctgcc tgcccccctt ccccgccgac gtgttcatga tcccccagta cggctacctg     1140

accctgaacg acggcagcca ggccgtgggc cgcagcagct tctactgcct ggagtacttc     1200

cccagccaga tgctgcgcac cggcaacaac ttccagttca gctacgagtt cgagaacgtg     1260

cccttccaca gcagctacgc ccacagccag agcctggacc gcctgatgaa ccccctgatc     1320

gaccagtacc tgtactacct gagcaagacc atcaacggca gcggccagaa ccagcagacc     1380

ctgaagttca gcgtggccgg ccccagcaac atggccgtgc agggccgcaa ctacatcccc     1440

ggccccagct accgccagca gcgcgtgagc accaccgtga cccagaacaa caacagcgag     1500

ttcgcctggc ccggcgccag cagctgggcc ctgaacggcc gcaacagcct gatgaacccc     1560

ggccccgcca tggccagcca caaggagggc gaggaccgct tcttccccct gagcggcagc     1620

ctgatcttcg gcaagcaggg caccggccgc gacaacgtgg acgccgacaa ggtgatgatc     1680

accaacgagg aggagatcaa gaccaccaac cccgtggcca ccgagagcta cggccaggtg     1740

gccaccaacc accagagcgc ccaggcccag gcccagaccg gctgggtgca gaaccagggc     1800

atcctgcccg gcatggtgtg gcaggaccgc gacgtgtacc tgcagggccc catctgggcc     1860

aagatccccc acaccgacgg caacttccac cccagccccc tgatgggcgg cttcggcatg     1920

aagcaccccc ccccccagat cctgatcaag aacacccccg tgcccgccga cccccccacc     1980

gccttcaaca aggacaagct gaacagcttc atcacccagt acagcaccgg ccaggtgagc     2040

gtggagatcg agtgggagct gcagaaggag aacagcaagc gctggaaccc cgagatccag     2100

tacaccagca actactacaa gagcaacaac gtggagttcg ccgtgaacac cgagggcgtg     2160

tacagcgagc cccgccccat cggcacccgc tacctgaccc gcaacctgta a              2211


<210>  4
<211>  1800
<212>  DNA
<213>  Adeno-Associated Virus 9

<400>  4
acggcccccg gcaagaagcg ccccgtggag cagagccccc aggagcccga cagcagcgcc       60

ggcatcggca agagcggcgc ccagcccgcc aagaagcgcc tgaacttcgg ccagaccggc      120

gacaccgaga gcgtgcccga cccccagccc atcggcgagc cccccgccgc ccccagcggc      180

gtgggcagcc tgaccatggc cagcggcggc ggcgcccccg tggccgacaa caacgagggc      240

gccgacggcg tgggcagcag cagcggcaac tggcactgcg acagccagtg gctgggcgac      300

cgcgtgatca ccaccagcac ccgcacctgg gccctgccca cctacaacaa ccacctgtac      360

aagcagatca gcaacagcac cagcggcggc agcagcaacg acaacgccta cttcggctac      420

agcaccccct ggggctactt cgacttcaac cgcttccact gccacttcag cccccgcgac      480

tggcagcgcc tgatcaacaa caactggggc ttccgcccca agcgcctgaa cttcaagctg      540

ttcaacatcc aggtgaagga ggtgaccgac aacaacggcg tgaagaccat cgccaacaac      600

ctgaccagca ccgtgcaggt gttcaccgac agcgactacc agctgcccta cgtgctgggc      660

agcgcccacg agggctgcct gccccccttc cccgccgacg tgttcatgat cccccagtac      720

ggctacctga ccctgaacga cggcagccag gccgtgggcc gcagcagctt ctactgcctg      780

gagtacttcc ccagccagat gctgcgcacc ggcaacaact tccagttcag ctacgagttc      840

gagaacgtgc ccttccacag cagctacgcc cacagccaga gcctggaccg cctgatgaac      900

cccctgatcg accagtacct gtactacctg agcaagacca tcaacggcag cggccagaac      960

cagcagaccc tgaagttcag cgtggccggc cccagcaaca tggccgtgca gggccgcaac     1020

tacatccccg gccccagcta ccgccagcag cgcgtgagca ccaccgtgac ccagaacaac     1080

aacagcgagt tcgcctggcc cggcgccagc agctgggccc tgaacggccg caacagcctg     1140

atgaaccccg gccccgccat ggccagccac aaggagggcg aggaccgctt cttccccctg     1200

agcggcagcc tgatcttcgg caagcagggc accggccgcg acaacgtgga cgccgacaag     1260

gtgatgatca ccaacgagga ggagatcaag accaccaacc ccgtggccac cgagagctac     1320

ggccaggtgg ccaccaacca ccagagcgcc caggcccagg cccagaccgg ctgggtgcag     1380

aaccagggca tcctgcccgg catggtgtgg caggaccgcg acgtgtacct gcagggcccc     1440

atctgggcca agatccccca caccgacggc aacttccacc ccagccccct gatgggcggc     1500

ttcggcatga agcacccccc cccccagatc ctgatcaaga acacccccgt gcccgccgac     1560

ccccccaccg ccttcaacaa ggacaagctg aacagcttca tcacccagta cagcaccggc     1620

caggtgagcg tggagatcga gtgggagctg cagaaggaga acagcaagcg ctggaacccc     1680

gagatccagt acaccagcaa ctactacaag agcaacaacg tggagttcgc cgtgaacacc     1740

gagggcgtgt acagcgagcc ccgccccatc ggcacccgct acctgacccg caacctgtaa     1800


