                         SEQUENCE LISTING

<110>  AVRYGEN CORPORATION
       GOOMER, Randy
 
<120>  Nanoparticles for Targeted Gene Therapy and Methods of Use 
       Thereof

<130>  AVGN-001WO

<140>  PCT/US15/27389
<141>  2015-04-23

<150>  US 61/983,218
<151>  2014-04-23

<160>  78    

<170>  PatentIn version 3.5

<210>  1
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  1
acctcgaact ggtgtcccgg atattcaaga gatatccggg acaccagttc tt               52


<210>  2
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  2
caaaaagaac tggtgtcccg gatatctctt gaatatccgg gacaccagtt cg               52


<210>  3
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  3
acctcgaaca gcgagctaaa tatatcaaga gtatatttag ctcgctgttc tt               52


<210>  4
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  4
caaaaagaac agcgagctaa atatactctt gatatattta gctcgctgtt cg               52


<210>  5
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  5
gtacctcgaa ctggtgtccc ggatattcaa gagatatccg ggacaccagt tctttttgga       60

aa                                                                      62


<210>  6
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  6
agcttttcca aaaagaactg gtgtcccgga tatctcttga atatccggga caccagttcg       60

ag                                                                      62


<210>  7
<211>  64
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  7
gtacctcgaa cagcgagcta aatatattca agagatatat ttagctcgct gttctttttg       60

gaaa                                                                    64


<210>  8
<211>  64
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  8
agcttttcca aaaagaacag cgagctaaat atatctcttg aatatattta gctcgctgtt       60

cgag                                                                    64


<210>  9
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  9
acctcgagcc agcctgaatg atgatcaaga gtcatcattc aggctggctc tt               52


<210>  10
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  10
caaaaagagc cagcctgaat gatgactctt gatcatcatt caggctggct cg               52


<210>  11
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  11
acctcgtaag tgcccgaagt gtaatcaaga gttacacttc gggcacttac tt               52


<210>  12
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  12
caaaaagtaa gtgcccgaag tgtaactctt gattacactt cgggcactta cg               52


<210>  13
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  13
gtacctcgag ccagcctgaa tgatgatcaa gagtcatcat tcaggctggc tctttttgga       60

aa                                                                      62


<210>  14
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  14
agcttttcca aaaagagcca gcctgaatga tgactcttga tcatcattca ggctggctcg       60

ag                                                                      62


<210>  15
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  15
gtacctcgta agtgcccgaa gtgtaatcaa gagttacact tcgggcactt actttttgga       60

aa                                                                      62


<210>  16
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  16
agcttttcca aaaagtaagt gcccgaagtg taactcttga ttacacttcg ggcacttacg       60

ag                                                                      62


<210>  17
<211>  66
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  17
gtacctcgca ggtaaacgtg ctgctctatc aagagtagag cagcacgttt acctgctttt       60

tggaaa                                                                  66


<210>  18
<211>  66
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  18
agcttttcca aaaagcaggt aaacgtgctg ctctactctt gatagagcag cacgtttacc       60

tgcgag                                                                  66


<210>  19
<211>  56
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  19
acctcgcagg taaacgtgct gctctatcaa gagtagagca gcacgtttac ctgctt           56


<210>  20
<211>  56
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  20
caaaaagcag gtaaacgtgc tgctctactc ttgatagagc agcacgttta cctgcg           56


<210>  21
<211>  65
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  21
gtacctccct actagtcacc agagacttct cgagaagtct ctggtgacta gtaggttttt       60

ggaaa                                                                   65


<210>  22
<211>  65
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  22
agcttttcca aaaacctact agtcaccaga gacttctcga gaagtctctg gtgactagta       60

gggag                                                                   65


<210>  23
<211>  55
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  23
acctccctac tagtcaccag agacttctcg agaagtctct ggtgactagt aggtt            55


<210>  24
<211>  55
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  24
caaaaaccta ctagtcacca gagacttctc gagaagtctc tggtgactag taggg            55


<210>  25
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  25
acctcgcgca gatcgatttg aatatcaaga gtattcaaat cgatctgcgc tt               52


<210>  26
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  26
caaaaagcgc agatcgattt gaatactctt gatattcaaa tcgatctgcg cg               52


<210>  27
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  27
gtacctcgcg cagatcgatt tgaatatcaa gagtattcaa atcgatctgc gctttttgga       60

aa                                                                      62


<210>  28
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  28
agcttttcca aaaagcgcag atcgatttga atactcttga tattcaaatc gatctgcgcg       60

ag                                                                      62


<210>  29
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  29
acctcgcaac tcctagtagt acaatcaaga gttgtactac taggagttgc tt               52


<210>  30
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  30
caaaaagcaa ctcctagtag tacaactctt gattgtacta ctaggagttg cg               52


<210>  31
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  31
gtacctcgca actcctagta gtacaatcaa gagttgtact actaggagtt gctttttgga       60

aa                                                                      62


<210>  32
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  32
agcttttcca aaaagcaact cctagtagta caactcttga ttgtactact aggagttgcg       60

ag                                                                      62


<210>  33
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  33
acctctgagg gatatcgcca aacatcaaga gtgtttggcg atatccctca tt               52


<210>  34
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  34
caaaaatgag ggatatcgcc aaacactctt gatgtttggc gatatccctc ag               52


<210>  35
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  35
gtacctctga gggatatcgc caaacatcaa gagtgtttgg cgatatccct catttttgga       60

aa                                                                      62


<210>  36
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  36
agcttttcca aaaatgaggg atatcgccaa acactcttga tgtttggcga tatccctcag       60

ag                                                                      62


<210>  37
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  37
acctcggcgc agatcgattt gaattcaaga gattcaaatc gatctgcgcc tt               52


<210>  38
<211>  52
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  38
caaaaaggcg cagatcgatt tgaatctctt gaattcaaat cgatctgcgc cg               52


<210>  39
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  39
gtacctcggc gcagatcgat ttgaattcaa gagattcaaa tcgatctgcg cctttttgga       60

aa                                                                      62


<210>  40
<211>  62
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  40
agcttttcca aaaaggcgca gatcgatttg aatctcttga attcaaatcg atctgcgccg       60

ag                                                                      62


<210>  41
<211>  72
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  41
acctcactca gcttagccag gtggaaatcc tacatcaaga gtgtaggatt tccacctggc       60

taagctgagt tt                                                           72


<210>  42
<211>  72
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  42
caaaaaactc agcttagcca ggtggaaatc ctacactctt gatgtaggat ttccacctgg       60

ctaagctgag tg                                                           72


<210>  43
<211>  82
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  43
gtacctcact cagcttagcc aggtggaaat cctacatcaa gagtgtagga tttccacctg       60

gctaagctga gttttttgga aa                                                82


<210>  44
<211>  82
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  44
agcttttcca aaaaactcag cttagccagg tggaaatcct acactcttga tgtaggattt       60

ccacctggct aagctgagtg ag                                                82


<210>  45
<211>  72
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  45
acctcatcga ctacattctc gacctgcagg tagttcaaga gactacctgc aggtcgagaa       60

tgtagtcgat tt                                                           72


<210>  46
<211>  72
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  46
caaaaaatcg actacattct cgacctgcag gtagtctctt gaactacctg caggtcgaga       60

atgtagtcga tg                                                           72


<210>  47
<211>  82
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  47
gtacctcatc gactacattc tcgacctgca ggtagttcaa gagactacct gcaggtcgag       60

aatgtagtcg attttttgga aa                                                82


<210>  48
<211>  82
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  48
agcttttcca aaaaatcgac tacattctcg acctgcaggt agtctcttga actacctgca       60

ggtcgagaat gtagtcgatg ag                                                82


<210>  49
<211>  72
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  49
acctcacctt cccatccaga cagccgagct cacttcaaga gagtgagctc ggctgtctgg       60

atgggaaggt tt                                                           72


<210>  50
<211>  72
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  50
caaaaaacct tcccatccag acagccgagc tcactctctt gaagtgagct cggctgtctg       60

gatgggaagg tg                                                           72


<210>  51
<211>  82
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  51
gtacctcacc ttcccatcca gacagccgag ctcacttcaa gagagtgagc tcggctgtct       60

ggatgggaag gttttttgga aa                                                82


<210>  52
<211>  82
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  52
agcttttcca aaaaaccttc ccatccagac agccgagctc actctcttga agtgagctcg       60

gctgtctgga tgggaaggtg ag                                                82


<210>  53
<211>  72
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  53
acctcccgga acttgtcatc tccaacgaca aaagtcaaga gcttttgtcg ttggagatga       60

caagttccgg tt                                                           72


<210>  54
<211>  72
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  54
caaaaaccgg aacttgtcat ctccaacgac aaaagctctt gacttttgtc gttggagatg       60

acaagttccg gg                                                           72


<210>  55
<211>  82
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  55
gtacctcccg gaacttgtca tctccaacga caaaagtcaa gagcttttgt cgttggagat       60

gacaagttcc ggtttttgga aa                                                82


<210>  56
<211>  82
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  56
agcttttcca aaaaccggaa cttgtcatct ccaacgacaa aagctcttga cttttgtcgt       60

tggagatgac aagttccggg ag                                                82


<210>  57
<211>  56
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  57
acctcgcagt ctattcgtcc tccatatcaa gagtatggag gacgaataga ctgctt           56


<210>  58
<211>  56
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  58
caaaaagcag tctattcgtc ctccatactc ttgatatgga ggacgaatag actgcg           56


<210>  59
<211>  66
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  59
gtacctcgca gtctattcgt cctccatatc aagagtatgg aggacgaata gactgctttt       60

tggaaa                                                                  66


<210>  60
<211>  66
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  60
agcttttcca aaaagcagtc tattcgtcct ccatactctt gatatggagg acgaatagac       60

tgcgag                                                                  66


<210>  61
<211>  36
<212>  PRT
<213>  Leiurus quinquestriatus quinquestriatus

<400>  61

Met Cys Met Pro Cys Phe Thr Thr Asp His Gln Met Ala Arg Lys Cys 
1               5                   10                  15      


Asp Asp Cys Cys Gly Gly Lys Gly Arg Gly Lys Cys Tyr Gly Pro Gln 
            20                  25                  30          


Cys Leu Cys Arg 
        35      


<210>  62
<211>  27
<212>  PRT
<213>  Artificial sequence

<220>
<223>  synthetic amino acid sequence

<400>  62

Gly Ile Gly Ala Val Leu Lys Val Leu Thr Thr Gly Leu Pro Ala Leu 
1               5                   10                  15      


Ile Ser Trp Ile Lys Arg Lys Arg His His Cys 
            20                  25          


<210>  63
<211>  25
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  63
cauaauaucg ucuuuguacu cuaaa                                             25


<210>  64
<211>  25
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  64
agaguacaaa gacgauauua ugaaa                                             25


<210>  65
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence


<220>
<221>  misc_feature
<222>  (1)..(21)
<223>  DNA/RNA hybrid

<400>  65
gcgcagaucg auuugaauat t                                                 21


<210>  66
<211>  21
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  66
uauucaaauc gaucugcgcc a                                                 21


<210>  67
<211>  21
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  67
uggucaugga guucuacugc a                                                 21


<210>  68
<211>  21
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  68
caguacaacu ccaugaccac g                                                 21


<210>  69
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence


<220>
<221>  misc_feature
<222>  (1)..(21)
<223>  DNA/RNA hybrid

<400>  69
uucauguagg ucugcgagct g                                                 21


<210>  70
<211>  21
<212>  DNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence


<220>
<221>  misc_feature
<222>  (1)..(21)
<223>  DNA/RNA hybrid

<400>  70
gcucgcagac ctacatgaac g                                                 21


<210>  71
<211>  21
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  71
uacuuauccu ucuucaugag c                                                 21


<210>  72
<211>  21
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  72
ucaugaagaa ggauaaguac a                                                 21


<210>  73
<211>  21
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  73
aacccaugga gccaagagcc a                                                 21


<210>  74
<211>  21
<212>  RNA
<213>  Artificial sequence

<220>
<223>  synthetic nucleic acid sequence

<400>  74
gcucuuggcu ccauggguuc g                                                 21


<210>  75
<211>  22
<212>  RNA
<213>  Homo sapiens

<400>  75
uggcaguguc uuagcugguu gu                                                22


<210>  76
<211>  110
<212>  RNA
<213>  Homo sapiens

<400>  76
ggccagcugu gaguguuucu uuggcagugu cuuagcuggu uguugugagc aauaguaagg       60

aagcaaucag caaguauacu gcccuagaag ugcugcacgu uguggggccc                 110


<210>  77
<211>  23
<212>  RNA
<213>  Homo sapiens

<400>  77
gggggccgau acacuguacg aga                                               23


<210>  78
<211>  84
<212>  RNA
<213>  Homo sapiens

<400>  78
ugugcagugg gaaggggggc cgauacacug uacgagagug aguagcaggu cucacaguga       60

accggucucu uucccuacug uguc                                              84


