                         SEQUENCE LISTING

<110>  ASSOCIATION INSTITUT DE MYOLOGIE ET AL.
 
<120>  TREATMENT OF MYOTONIC DYSTROPHY

<130>  B1798PC00

<160>  3     

<170>  PatentIn version 3.5

<210>  1
<211>  130
<212>  PRT
<213>  homo sapiens

<400>  1

Thr Gln Ser Ala Val Lys Ser Leu Lys Arg Pro Leu Glu Ala Thr Phe 
1               5                   10                  15      


Asp Leu Gly Ile Pro Gln Ala Val Leu Pro Pro Leu Pro Lys Arg Pro 
            20                  25                  30          


Ala Leu Glu Lys Thr Asn Gly Ala Thr Ala Val Phe Asn Thr Gly Ile 
        35                  40                  45              


Phe Gln Tyr Gln Gln Ala Leu Ala Asn Met Gln Leu Gln Gln His Thr 
    50                  55                  60                  


Ala Phe Leu Pro Pro Gly Ser Ile Leu Cys Met Thr Pro Ala Thr Ser 
65                  70                  75                  80  


Val Val Pro Met Val His Gly Ala Thr Pro Ala Thr Val Ser Ala Ala 
                85                  90                  95      


Thr Thr Ser Ala Thr Ser Val Pro Phe Ala Ala Thr Thr Ala Asn Gln 
            100                 105                 110         


Ile Pro Ile Ile Ser Ala Glu His Leu Thr Ser His Lys Tyr Val Thr 
        115                 120                 125             


Gln Met 
    130 


<210>  2
<211>  268
<212>  PRT
<213>  artificial

<220>
<223>  delta-CT3 MBNL1-derived polypeptide

<400>  2

Ala Val Ser Val Thr Pro Ile Arg Asp Thr Lys Trp Leu Thr Leu Glu 
1               5                   10                  15      


Val Cys Arg Glu Phe Gln Arg Gly Thr Cys Ser Arg Pro Asp Thr Glu 
            20                  25                  30          


Cys Lys Phe Ala His Pro Ser Lys Ser Cys Gln Val Glu Asn Gly Arg 
        35                  40                  45              


Val Ile Ala Cys Phe Asp Ser Leu Lys Gly Arg Cys Ser Arg Glu Asn 
    50                  55                  60                  


Cys Lys Tyr Leu His Pro Pro Pro His Leu Lys Thr Gln Leu Glu Ile 
65                  70                  75                  80  


Asn Gly Arg Asn Asn Leu Ile Gln Gln Lys Asn Met Ala Met Leu Ala 
                85                  90                  95      


Gln Gln Met Gln Leu Ala Asn Ala Met Met Pro Gly Ala Pro Leu Gln 
            100                 105                 110         


Pro Val Pro Met Phe Ser Val Ala Pro Ser Leu Ala Thr Asn Ala Ser 
        115                 120                 125             


Ala Ala Ala Phe Asn Pro Tyr Leu Gly Pro Val Ser Pro Ser Leu Val 
    130                 135                 140                 


Pro Ala Glu Ile Leu Pro Thr Ala Pro Met Leu Val Thr Gly Asn Pro 
145                 150                 155                 160 


Gly Val Pro Val Pro Ala Ala Ala Ala Ala Ala Ala Gln Lys Leu Met 
                165                 170                 175     


Arg Thr Asp Arg Leu Glu Val Cys Arg Glu Tyr Gln Arg Gly Asn Cys 
            180                 185                 190         


Asn Arg Gly Glu Asn Asp Cys Arg Phe Ala His Pro Ala Asp Ser Thr 
        195                 200                 205             


Met Ile Asp Thr Asn Asp Asn Thr Val Thr Val Cys Met Asp Tyr Ile 
    210                 215                 220                 


Lys Gly Arg Cys Ser Arg Glu Lys Cys Lys Tyr Phe His Pro Pro Ala 
225                 230                 235                 240 


His Leu Gln Ala Lys Ile Lys Ala Ala Gln Tyr Gln Val Asn Gln Ala 
                245                 250                 255     


Ala Ala Ala Gln Ala Ala Ala Thr Ala Ala Ala Met 
            260                 265             


<210>  3
<211>  568
<212>  DNA
<213>  artificial

<220>
<223>  mutated MBNL minigene

<400>  3
cctttcaccc aggagcaaac gcacatcacc tgtgtcctca tctgatggcc ctggtgtggg       60

gcacagtcgt gttggcaggg agggaggtgg ggttggtccc ctttgtgggt ttgttgcgag      120

gccgtgttcc agctgtttcc acagggagcg attttcagct ccacaggaca cagctcccca      180

gttcctcctg agaacaaaag ggggttctgg ggagaggcca ccgttctgag ggctcactgt      240

atgtgttcca gaatctcccc tgcagacccc cactgaggac ggatctgagg aaccgggctc      300

tgaaacctct gaccgtaaga gcactccaac agcggaaggt gggcccccct tcagacgccc      360

cctccagcct ccagcctgta cttagcctac tttgagcctc cctcctggct gcatctacgc      420

tccccctggc tgagagatgt cactccttcg gtactcagga cagcgtggtg ggagctgagc      480

cttcgattac ttactggttg agtgtgggca ccttcatccc gtgtggctct ggaggcagcc      540

acccttggac agtcccgcgc acagctcc                                         568


