                         SEQUENCE LISTING

<110>  Synthena AG
 
<120>  NUCLEIC ACIDS AND METHODS FOR THE TREATMENT OF POMPE DISEASE

<130>  P3266PC00

<150>  EP 13184013.4
<151>  2013-09-11

<160>  18    

<170>  PatentIn version 3.5

<210>  1
<211>  578
<212>  DNA
<213>  homo sapiens

<400>  1
gcctgtagga gctgtccagg ccatctccaa ccatgggagt gaggcacccg ccctgctccc       60

accggctcct ggccgtctgc gccctcgtgt ccttggcaac cgctgcactc ctggggcaca      120

tcctactcca tgatttcctg ctggttcccc gagagctgag tggctcctcc ccagtcctgg      180

aggagactca cccagctcac cagcagggag ccagcagacc agggccccgg gatgcccagg      240

cacaccccgg ccgtcccaga gcagtgccca cacagtgcga cgtccccccc aacagccgct      300

tcgattgcgc ccctgacaag gccatcaccc aggaacagtg cgaggcccgc ggctgttgct      360

acatccctgc aaagcagggg ctgcagggag cccagatggg gcagccctgg tgcttcttcc      420

cacccagcta ccccagctac aagctggaga acctgagctc ctctgaaatg ggctacacgg      480

ccaccctgac ccgtaccacc cccaccttct tccccaagga catcctgacc ctgcggctgg      540

acgtgatgat ggagactgag aaccgcctcc acttcacg                              578


<210>  2
<211>  15
<212>  RNA
<213>  artificial

<220>
<223>  target sequence

<400>  2
cuguaggagc ugucc                                                        15


<210>  3
<211>  15
<212>  RNA
<213>  artificial

<220>
<223>  target sequence

<400>  3
aggagcuguc caggc                                                        15


<210>  4
<211>  15
<212>  RNA
<213>  artificial

<220>
<223>  target sequence

<400>  4
caggccaucu ccaac                                                        15


<210>  5
<211>  44
<212>  RNA
<213>  artificial

<220>
<223>  target sequence

<400>  5
cuguaggagc uguccaggcc aucuccaacc augggaguga ggca                        44


<210>  6
<211>  57
<212>  RNA
<213>  artificial

<220>
<223>  U7-modified antisense oligonucleotide

<400>  6
guuggagaug gccuggacag cuccuacagg uuuucugacu ucggucggaa aaccccu          57


<210>  7
<211>  19
<212>  DNA
<213>  artificial

<220>
<223>  primer

<400>  7
agctgacggg gaaactgag                                                    19


<210>  8
<211>  18
<212>  DNA
<213>  artificial

<220>
<223>  primer

<400>  8
aaggtcccgg ttccacag                                                     18


<210>  9
<211>  19
<212>  DNA
<213>  artificial

<220>
<223>  primer

<400>  9
gctcctcgga gaactccac                                                    19


<210>  10
<211>  18
<212>  DNA
<213>  artificial

<220>
<223>  primer

<400>  10
ctgtccaggc catctcca                                                     18


<210>  11
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  primer

<400>  11
agtctccatc atcacgtcca                                                   20


<210>  12
<211>  29
<212>  RNA
<213>  artificial

<220>
<223>  target sequence

<400>  12
cuguaggagc uguccaggcc aucuccaac                                         29


<210>  13
<211>  43
<212>  RNA
<213>  artificial

<220>
<223>  target sequence

<400>  13
cuguaggagc uguccaggcc aucuccaacc augggaguga ggc                         43


<210>  14
<211>  15
<212>  DNA
<213>  artificial

<220>
<223>  antisense oligonucleotide AON1

<400>  14
ggacagctcc tacag                                                        15


<210>  15
<211>  15
<212>  DNA
<213>  artificial

<220>
<223>  antisense oligonucleotide AON2

<400>  15
gcctggacag ctcct                                                        15


<210>  16
<211>  15
<212>  DNA
<213>  artificial

<220>
<223>  antisense oligonucleotide AON3

<400>  16
gttggagatg gcctg                                                        15


<210>  17
<211>  29
<212>  DNA
<213>  artificial

<220>
<223>  antisense oligonucleotide

<400>  17
gttggagatg gcctggacag ctcctacag                                         29


<210>  18
<211>  71
<212>  RNA
<213>  artificial

<220>
<223>  U7opt-AS[+3;+31]

<400>  18
guuggagaug gccuggacag cuccuacaga auuuuuggag cagguuuucu gacuucgguc       60

ggaaaacccc u                                                            71


