                         SEQUENCE LISTING

<110>  RaNA Therapeutics, Inc.
 
<120>  COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF FRATAXIN

<130>  R0693.70024WO00

<140>  Not yet available
<141>  Concurrently herewith

<150>  US 61/866790
<151>  2013-08-16

<160>  109   

<170>  PatentIn version 3.5

<210>  1
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  1
cggcgcccga gagtccacat                                                   20


<210>  2
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  2
ccaggaggcc ggctactgcg                                                   20


<210>  3
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  3
ctgggctggg ctgggtgacg                                                   20


<210>  4
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  4
acccgggtga gggtctgggc                                                   20


<210>  5
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  5
ccaactctgc cggccgcggg                                                   20


<210>  6
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  6
acggcggccg cagagtgggg                                                   20


<210>  7
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  7
tcgatgtcgg tgcgcaggcc                                                   20


<210>  8
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  8
ggcggggcgt gcaggtcgca                                                   20


<210>  9
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  9
acgttggttc gaacttgcgc                                                   20


<210>  10
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  10
ttccaaatct ggttgaggcc                                                   20


<210>  11
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  11
agacactctg ctttttgaca                                                   20


<210>  12
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  12
tttcctcaaa ttcatcaaat                                                   20


<210>  13
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  13
gggtggccca aagttccaga                                                   20


<210>  14
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  14
tggtctcatc tagagagcct                                                   20


<210>  15
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  15
ctctgctagt ctttcatagg                                                   20


<210>  16
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  16
gctaaagagt ccagcgtttc                                                   20


<210>  17
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  17
gcaaggtctt caaaaaactc t                                                 21


<210>  18
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  18
ctcaaacgtg tatggcttgt ct                                                22


<210>  19
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  19
cccaaaggag acatcatagt c                                                 21


<210>  20
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  20
cagtttgaca gttaagacac cact                                              24


<210>  21
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  21
ataggttcct agatctccac c                                                 21


<210>  22
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  22
ggcgtctgct tgttgatcac                                                   20


<210>  23
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  23
aagatagcca gatttgcttg ttt                                               23


<210>  24
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  24
ggtccactac atacctggat ggag                                              24


<210>  25
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  25
cccagtccag tcataacgct t                                                 21


<210>  26
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  26
cgtgggagta cacccagttt tt                                                22


<210>  27
<211>  18
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  27
catggaggga cacgccgt                                                     18


<210>  28
<211>  22
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  28
gtgagctctg cggccagcag ct                                                22


<210>  29
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  29
agtttggttt ttaaggcttt a                                                 21


<210>  30
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  30
taggccaagg aagacaagtc c                                                 21


<210>  31
<211>  19
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  31
tcaagcatct tttccggaa                                                    19


<210>  32
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  32
tccttaaaac ggggctgggc a                                                 21


<210>  33
<211>  21
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  33
ttggcctgat agcttttaat g                                                 21


<210>  34
<211>  27
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  34
cctcagctgc ataatgaagc tggggtc                                           27


<210>  35
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  35
aacaacaaca acaacaaaaa acaga                                             25


<210>  36
<211>  26
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  36
cctcaaaagc aggaataaaa aaaata                                            26


<210>  37
<211>  23
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  37
gctgtgacac atagcccaac tgt                                               23


<210>  38
<211>  25
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  38
ggaggcaaca cattctttct acaga                                             25


<210>  39
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  39
ctattaatat tactg                                                        15


<210>  40
<211>  16
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  40
cattatgtgt atgtat                                                       16


<210>  41
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  41
tttatctatg ttatt                                                        15


<210>  42
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  42
ctaatttgaa gttct                                                        15


<210>  43
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  43
ttcgaacttg cgcgg                                                        15


<210>  44
<211>  14
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  44
tagagagcct gggt                                                         14


<210>  45
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  45
acaccactcc caaag                                                        15


<210>  46
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  46
aggtccacta catac                                                        15


<210>  47
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  47
cgttaacctg gatgg                                                        15


<210>  48
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  48
tgacccaagg gagac                                                        15


<210>  49
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  49
tggccactgg ccgca                                                        15


<210>  50
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  50
cggcgacccc tggtg                                                        15


<210>  51
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  51
cgccctccag cgctg                                                        15


<210>  52
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  52
cgctccgccc tccag                                                        15


<210>  53
<211>  17
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  53
tgacccaagg gagaccc                                                      17


<210>  54
<211>  17
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  54
tggccactgg ccgcacc                                                      17


<210>  55
<211>  17
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  55
cggcgacccc tggtgcc                                                      17


<210>  56
<211>  17
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  56
cgccctccag cgctgcc                                                      17


<210>  57
<211>  17
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  57
cgctccgccc tccagcc                                                      17


<210>  58
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  58
tgacccaagg gagacggaaa ccac                                              24


<210>  59
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  59
tggccactgg ccgcaggaaa ccac                                              24


<210>  60
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  60
cggcgacccc tggtgggaaa cctc                                              24


<210>  61
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  61
cgccctccag cgctgggaaa cctc                                              24


<210>  62
<211>  24
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  62
cgctccgccc tccagccaaa ggtc                                              24


<210>  63
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  63
ggtttttaag gcttt                                                        15


<210>  64
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  64
ggggtcttgg cctga                                                        15


<210>  65
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  65
cataatgaag ctggg                                                        15


<210>  66
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  66
aggaggcaac acatt                                                        15


<210>  67
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  67
attattttgc ttttt                                                        15


<210>  68
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  68
cattttccct cctgg                                                        15


<210>  69
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  69
gtaggctacc cttta                                                        15


<210>  70
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  70
gaggcttgtt gcttt                                                        15


<210>  71
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  71
catgtatgat gttat                                                        15


<210>  72
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  72
tttttggttt ttaaggcttt                                                   20


<210>  73
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  73
tttttggggt cttggcctga                                                   20


<210>  74
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  74
tttttcataa tgaagctggg                                                   20


<210>  75
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  75
tttttaggag gcaacacatt                                                   20


<210>  76
<211>  20
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  76
tttttattat tttgcttttt                                                   20


<210>  77
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  77
atgggggacg gggca                                                        15


<210>  78
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  78
ggttgagact gggtg                                                        15


<210>  79
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  79
atgggggacg gggca                                                        15


<210>  80
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  80
aaagccttaa aaacc                                                        15


<210>  81
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  81
tcaggccaag acccc                                                        15


<210>  82
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  82
cccagcttca ttatg                                                        15


<210>  83
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  83
aatgtgttgc ctcct                                                        15


<210>  84
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  84
aaaaagcaaa ataat                                                        15


<210>  85
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  85
ccaggaggga aaatg                                                        15


<210>  86
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  86
taaagggtag cctac                                                        15


<210>  87
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  87
aaagcaacaa gcctc                                                        15


<210>  88
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  88
ataacatcat acatg                                                        15


<210>  89
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  89
gatactatct tcctc                                                        15


<210>  90
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  90
agactgaaga ggtgc                                                        15


<210>  91
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  91
cgggacggct gtgtt                                                        15


<210>  92
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  92
tctgtgtggg cagca                                                        15


<210>  93
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  93
aaagccttaa aaacc                                                        15


<210>  94
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  94
tcaggccaag acccc                                                        15


<210>  95
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  95
cccagcttca ttatg                                                        15


<210>  96
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  96
aatgtgttgc ctcct                                                        15


<210>  97
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  97
aaaaagcaaa ataat                                                        15


<210>  98
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  98
ccaggaggga aaatg                                                        15


<210>  99
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  99
taaagggtag cctac                                                        15


<210>  100
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  100
aaagcaacaa gcctc                                                        15


<210>  101
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  101
ataacatcat acatg                                                        15


<210>  102
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  102
gatactatct tcctc                                                        15


<210>  103
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  103
atgggggacg gggca                                                        15


<210>  104
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  104
ggttgagact gggtg                                                        15


<210>  105
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  105
agactgaaga ggtgc                                                        15


<210>  106
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  106
cgggacggct gtgtt                                                        15


<210>  107
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  107
tctgtgtggg cagca                                                        15


<210>  108
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  108
gaagaagaag aagaa                                                        15


<210>  109
<211>  15
<212>  DNA
<213>  Artificial Sequence

<220>
<223>  Synthetic oligonucleotides

<400>  109
ttcttcttct tcttc                                                        15


