                         SEQUENCE LISTING

<110>  Sarepta Therapeutics, Inc.
 
<120>  FUNCTIONALLY-MODIFIED OLIGONUCLEOTIDES AND SUBUNITS THEREOF

<130>  120178.498WO

<150>  US 61/561,806
<151>  2011-11-18

<160>  35    

<170>  PatentIn version 3.5

<210>  1
<211>  11
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  beta-Alanine

<400>  1

Arg Phe Phe Arg Phe Phe Arg Phe Phe Xaa Ala 
1               5                   10      


<210>  2
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  beta-Alanine

<400>  2

Arg Thr Arg Thr Arg Phe Leu Arg Arg Thr Xaa Ala 
1               5                   10          


<210>  3
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  beta-Alanine

<400>  3

Arg Phe Phe Arg Phe Phe Arg Phe Phe Arg Xaa Ala 
1               5                   10          


<210>  4
<211>  12
<212>  PRT
<213>  Artificial Seqeunce

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  beta-Alanine

<400>  4

Lys Thr Arg Thr Lys Phe Leu Lys Lys Thr Xaa Ala 
1               5                   10          


<210>  5
<211>  11
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  beta-Alanine

<400>  5

Lys Phe Phe Lys Phe Phe Lys Phe Phe Xaa Ala 
1               5                   10      


<210>  6
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synethetic transport peptide


<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  beta-Alanine

<400>  6

Lys Phe Phe Lys Phe Phe Lys Phe Phe Lys Xaa Ala 
1               5                   10          


<210>  7
<211>  8
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (7)..(7)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  beta-Alanine

<400>  7

Arg Phe Phe Arg Phe Phe Xaa Ala 
1               5               


<210>  8
<211>  9
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (9)..(9)
<223>  beta-Alanine

<400>  8

Arg Phe Phe Arg Phe Phe Arg Xaa Ala 
1               5                   


<210>  9
<211>  10
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(3)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (5)..(6)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(9)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  beta-Alanine

<400>  9

Arg Xaa Xaa Arg Xaa Xaa Arg Xaa Xaa Ala 
1               5                   10  


<210>  10
<211>  14
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  beta-Alanine

<400>  10

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Xaa Ala 
1               5                   10                  


<210>  11
<211>  10
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  11

Arg Arg Arg Gln Arg Arg Lys Lys Arg Cys 
1               5                   10  


<210>  12
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  12

Arg Arg Arg Arg Arg Arg Arg Arg Arg Phe Phe Cys 
1               5                   10          


<210>  13
<211>  13
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (3)..(3)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (9)..(9)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  beta-Alanine

<400>  13

Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Ala 
1               5                   10              


<210>  14
<211>  14
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  beta-Alanine

<400>  14

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Xaa Ala 
1               5                   10                  


<210>  15
<211>  14
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (1)..(1)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (4)..(4)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (7)..(7)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  beta-Alanine

<400>  15

Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Ala 
1               5                   10                  


<210>  16
<211>  13
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (4)..(4)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  beta-Alanine

<400>  16

Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Ala 
1               5                   10              


<210>  17
<211>  15
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (4)..(4)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (10)..(10)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (12)..(12)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (15)..(15)
<223>  beta-Alanine

<400>  17

Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Arg Xaa Ala 
1               5                   10                  15  


<210>  18
<211>  17
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (16)..(16)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (17)..(17)
<223>  beta-Alanine

<400>  18

Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Arg Xaa Arg Xaa 
1               5                   10                  15      


Ala 
    


<210>  19
<211>  14
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (5)..(5)
<223>  beta-Alanine

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (11)..(11)
<223>  beta-Alanine

<220>
<221>  misc_feature
<222>  (13)..(13)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (14)..(14)
<223>  beta-Alanine

<400>  19

Arg Xaa Arg Arg Ala Arg Arg Xaa Arg Arg Ala Arg Xaa Ala 
1               5                   10                  


<210>  20
<211>  5
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  20

Arg Arg Arg Arg Gly 
1               5   


<210>  21
<211>  6
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  21

Arg Arg Arg Arg Arg Gly 
1               5       


<210>  22
<211>  7
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  22

Arg Arg Arg Arg Arg Arg Gly 
1               5           


<210>  23
<211>  8
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  23

Arg Arg Arg Arg Arg Arg Arg Gly 
1               5               


<210>  24
<211>  9
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  24

Arg Arg Arg Arg Arg Arg Arg Arg Gly 
1               5                   


<210>  25
<211>  11
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  25

Arg Arg Arg Arg Arg Gly Arg Arg Arg Arg Gly 
1               5                   10      


<210>  26
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  26

Arg Arg Arg Arg Arg Phe Phe Arg Arg Arg Arg Gly 
1               5                   10          


<210>  27
<211>  10
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  27

Arg Lys Lys Arg Arg Gln Arg Arg Arg Gly 
1               5                   10  


<210>  28
<211>  10
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  28

Arg Arg Arg Gln Arg Arg Lys Lys Arg Gly 
1               5                   10  


<210>  29
<211>  11
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<400>  29

Arg Xaa Arg Arg Gly Gly Arg Xaa Arg Gly Gly 
1               5                   10      


<210>  30
<211>  12
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide


<220>
<221>  misc_feature
<222>  (2)..(2)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (6)..(6)
<223>  6-aminohexanoic acid

<220>
<221>  misc_feature
<222>  (8)..(8)
<223>  6-aminohexanoic acid

<400>  30

Arg Xaa Arg Arg Arg Xaa Arg Xaa Arg Arg Arg Gly 
1               5                   10          


<210>  31
<211>  5
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  31

Arg Arg Arg Arg Pro 
1               5   


<210>  32
<211>  6
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  32

Arg Arg Arg Arg Arg Pro 
1               5       


<210>  33
<211>  7
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  33

Arg Arg Arg Arg Arg Arg Pro 
1               5           


<210>  34
<211>  8
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  34

Arg Arg Arg Arg Arg Arg Arg Pro 
1               5               


<210>  35
<211>  9
<212>  PRT
<213>  Artificial Sequence

<220>
<223>  Synthetic transport peptide

<400>  35

Arg Arg Arg Arg Arg Arg Arg Arg Pro 
1               5                   


