
                                SEQUENCE LISTING

<110> bluebird bio, Inc.
      Denaro, Maria Joann
      Finer, Mitchell Howard
      Veres, Gabor

<120> GENE THERAPY VECTORS FOR
  ADRENOLEUKODYSTROPHY AND ADRENOMYELONEUROPATHY
  

<130> BLBD-003/01WO

<150> US 61/495,857                  
<151> 2011-06-09 

<160> 3

<170> FastSEQ for Windows Version 4.0

<210> 1
<211> 2297
<212> DNA
<213> Homo sapiens

<400> 1
ccagccccag tccctacgcg gcagccagcc caggtgacat gccggtgctc tccaggcccc 60
ggccctggcg ggggaacacg ctgaagcgca cggccgtgct cctggccctc gcggcctatg 120
gagcccacaa agtctacccc ttggtgcgcc agtgcctggc cccggccagg ggtcttcagg 180
cgcccgccgg ggagcccacg caggaggcct ccggggtcgc ggcggccaaa gctggcatga 240
accgggtatt cctgcagcgg ctcctgtggc tcctgcggct gctgttcccc cgggtcctgt 300
gccgggagac ggggctgctg gccctgcact cggccgcctt ggtgagccgc accttcctgt 360
cggtgtatgt ggcccgcctg gacggaaggc tggcccgctg catcgtccgc aaggacccgc 420
gggcttttgg ctggcagctg ctgcagtggc tcctcatcgc cctccctgct accttcgtca 480
acagtgccat ccgttacctg gagggccaac tggccctgtc gttccgcagc cgtctggtgg 540
cccacgccta ccgcctctac ttctcccagc agacctacta ccgggtcagc aacatggacg 600
ggcggcttcg caaccctgac cagtctctga cggaggacgt ggtggccttt gcggcctctg 660
tggcccacct ctactccaac ctgaccaagc cactcctgga cgtggctgtg acttcctaca 720
ccctgcttcg ggcggcccgc tcccgtggag ccggcacagc ctggccctcg gccatcgccg 780
gcctcgtggt gttcctcacg gccaacgtgc tgcgggcctt ctcgcccaag ttcggggagc 840
tggtggcaga ggaggcgcgg cggaaggggg agctgcgcta catgcactcg cgtgtggtgg 900
ccaactcgga ggagatcgcc ttctatgggg gccatgaggt ggagctggcc ctgctacagc 960
gctcctacca ggacctggcc tcgcagatca acctcatcct tctggaacgc ctgtggtatg 1020
ttatgctgga gcagttcctc atgaagtatg tgtggagcgc ctcgggcctg ctcatggtgg 1080
ctgtccccat catcactgcc actggctact cagagtcaga tgcagaggcc gtgaagaagg 1140
cagccttgga aaagaaggag gaggagctgg tgagcgagcg cacagaagcc ttcactattg 1200
cccgcaacct cctgacagcg gctgcagatg ccattgagcg gatcatgtcg tcgtacaagg 1260
aggtgacgga gctggctggc tacacagccc gggtgcacga gatgttccag gtatttgaag 1320
atgttcagcg ctgtcacttc aagaggccca gggagctaga ggacgctcag gcggggtctg 1380
ggaccatagg ccggtctggt gtccgtgtgg agggccccct gaagatccga ggccaggtgg 1440
tggatgtgga acaggggatc atctgcgaga acatccccat cgtcacgccc tcaggagagg 1500
tggtggtggc cagcctcaac atcagggtgg aggaaggcat gcatctgctc atcacaggcc 1560
ccaatggctg cggcaagagc tccctgttcc ggatcctggg tgggctctgg cccacgtacg 1620
gtggtgtgct ctacaagccc ccaccccagc gcatgttcta catcccgcag aggccctaca 1680
tgtctgtggg ctccctgcgt gaccaggtga tctacccgga ctcagtggag gacatgcaaa 1740
ggaagggcta ctcggagcag gacctggaag ccatcctgga cgtcgtgcac ctgcaccaca 1800
tcctgcagcg ggagggaggt tgggaggcta tgtgtgactg gaaggacgtc ctgtcgggtg 1860
gcgagaagca gagaatcggc atggcccgca tgttctacca caggcccaag tacgccctcc 1920
tggatgaatg caccagcgcc gtgagcatcg acgtggaagg caagatcttc caggcggcca 1980
aggacgcggg cattgccctg ctctccatca cccaccggcc ctccctgtgg aaataccaca 2040
cacacttgct acagttcgat ggggagggcg gctggaagtt cgagaagctg gactcagctg 2100
cccgcctgag cctgacggag gagaagcagc ggctggagca gcagctggcg ggcattccca 2160
agatgcagcg gcgcctccag gagctctgcc agatcctggg cgaggccgtg gccccagcgc 2220
atgtgccggc acctagcccg caaggccctg gtggcctcca gggtgcctcc acctgactcg 2280
agggggggcc cggtacc                                                2297

<210> 2
<211> 2238
<212> DNA
<213> Homo sapiens

<400> 2
atgccggtgc tctccaggcc ccggccctgg cgggggaaca cgctgaagcg cacggccgtg 60
ctcctggccc tcgcggccta tggagcccac aaagtctacc ccttggtgcg ccagtgcctg 120
gccccggcca ggggtcttca ggcgcccgcc ggggagccca cgcaggaggc ctccggggtc 180
gcggcggcca aagctggcat gaaccgggta ttcctgcagc ggctcctgtg gctcctgcgg 240
ctgctgttcc cccgggtcct gtgccgggag acggggctgc tggccctgca ctcggccgcc 300
ttggtgagcc gcaccttcct gtcggtgtat gtggcccgcc tggacggaag gctggcccgc 360
tgcatcgtcc gcaaggaccc gcgggctttt ggctggcagc tgctgcagtg gctcctcatc 420
gccctccctg ctaccttcgt caacagtgcc atccgttacc tggagggcca actggccctg 480
tcgttccgca gccgtctggt ggcccacgcc taccgcctct acttctccca gcagacctac 540
taccgggtca gcaacatgga cgggcggctt cgcaaccctg accagtctct gacggaggac 600
gtggtggcct ttgcggcctc tgtggcccac ctctactcca acctgaccaa gccactcctg 660
gacgtggctg tgacttccta caccctgctt cgggcggccc gctcccgtgg agccggcaca 720
gcctggccct cggccatcgc cggcctcgtg gtgttcctca cggccaacgt gctgcgggcc 780
ttctcgccca agttcgggga gctggtggca gaggaggcgc ggcggaaggg ggagctgcgc 840
tacatgcact cgcgtgtggt ggccaactcg gaggagatcg ccttctatgg gggccatgag 900
gtggagctgg ccctgctaca gcgctcctac caggacctgg cctcgcagat caacctcatc 960
cttctggaac gcctgtggta tgttatgctg gagcagttcc tcatgaagta tgtgtggagc 1020
gcctcgggcc tgctcatggt ggctgtcccc atcatcactg ccactggcta ctcagagtca 1080
gatgcagagg ccgtgaagaa ggcagccttg gaaaagaagg aggaggagct ggtgagcgag 1140
cgcacagaag ccttcactat tgcccgcaac ctcctgacag cggctgcaga tgccattgag 1200
cggatcatgt cgtcgtacaa ggaggtgacg gagctggctg gctacacagc ccgggtgcac 1260
gagatgttcc aggtatttga agatgttcag cgctgtcact tcaagaggcc cagggagcta 1320
gaggacgctc aggcggggtc tgggaccata ggccggtctg gtgtccgtgt ggagggcccc 1380
ctgaagatcc gaggccaggt ggtggatgtg gaacagggga tcatctgcga gaacatcccc 1440
atcgtcacgc cctcaggaga ggtggtggtg gccagcctca acatcagggt ggaggaaggc 1500
atgcatctgc tcatcacagg ccccaatggc tgcggcaaga gctccctgtt ccggatcctg 1560
ggtgggctct ggcccacgta cggtggtgtg ctctacaagc ccccacccca gcgcatgttc 1620
tacatcccgc agaggcccta catgtctgtg ggctccctgc gtgaccaggt gatctacccg 1680
gactcagtgg aggacatgca aaggaagggc tactcggagc aggacctgga agccatcctg 1740
gacgtcgtgc acctgcacca catcctgcag cgggagggag gttgggaggc tatgtgtgac 1800
tggaaggacg tcctgtcggg tggcgagaag cagagaatcg gcatggcccg catgttctac 1860
cacaggccca agtacgccct cctggatgaa tgcaccagcg ccgtgagcat cgacgtggaa 1920
ggcaagatct tccaggcggc caaggacgcg ggcattgccc tgctctccat cacccaccgg 1980
ccctccctgt ggaaatacca cacacacttg ctacagttcg atggggaggg cggctggaag 2040
ttcgagaagc tggactcagc tgcccgcctg agcctgacgg aggagaagca gcggctggag 2100
cagcagctgg cgggcattcc caagatgcag cggcgcctcc aggagctctg ccagatcctg 2160
ggcgaggccg tggccccagc gcatgtgccg gcacctagcc cgcaaggccc tggtggcctc 2220
cagggtgcct ccacctga                                               2238

<210> 3
<211> 399
<212> DNA
<213> Artificial Sequence

<220> 
<223> a MND promoter sequence

<400> 3
tttatttagt ctccagaaaa aggggggaat gaaagacccc acctgtaggt ttggcaagct 60
aggatcaagg ttaggaacag agagacagca gaatatgggc caaacaggat atctgtggta 120
agcagttcct gccccggctc agggccaaga acagttggaa cagcagaata tgggccaaac 180
aggatatctg tggtaagcag ttcctgcccc ggctcagggc caagaacaga tggtccccag 240
atgcggtccc gccctcagca gtttctagag aaccatcaga tgtttccagg gtgccccaag 300
gacctgaaat gaccctgtgc cttatttgaa ctaaccaatc agttcgcttc tcgcttctgt 360
tcgcgcgctt ctgctccccg agctcaataa aagagccca                        399
