                         SEQUENCE LISTING

<110>  Amsterdam Molecular Therapeutics (AMT) IP B.V.
       BOZZONI, Irene
       DE ANGELIS, Fernanda
       INCITTI, Tania
       MARTONE, Julie
       CAZZELLA, Valentina
       PINNARO', Chiara
 
<120>  MODIFIED snRNAs FOR USE IN THERAPY

<130>  PCT 113843

<150>  RM2010A000310
<151>  2010-06-08

<160>  74    

<170>  PatentIn version 3.5

<210>  1
<211>  20
<212>  DNA
<213>  Homo sapiens

<400>  1
catcaagcag aaggtatgag                                                   20


<210>  2
<211>  16
<212>  DNA
<213>  Homo sapiens

<400>  2
tagctcctac tcagac                                                       16


<210>  3
<211>  21
<212>  DNA
<213>  Homo sapiens

<400>  3
ccatcttcct tgatgttgga g                                                 21


<210>  4
<211>  56
<212>  DNA
<213>  Homo sapiens

<400>  4
ctcatacctt ctgcttgatg ctccaacatc aaggaagatg ggtctgagta ggagct           56


<210>  5
<211>  212
<212>  DNA
<213>  Homo sapiens

<400>  5
atctcatacc ttctgcttga tgctccaaca tcaaggaaga tgggtctgag taggagctgg       60

caggggagat accatgatca cgaaggtggt tttcccaggg cgaggcttat ccattgcact      120

ccggatgtgc tgacccctgc gatttcccca aatgtgggaa actcgactgc ataatttgtg      180

gtagtggggg actgcgttcg cgctttcccc tg                                    212


<210>  6
<211>  18
<212>  DNA
<213>  Homo sapiens

<400>  6
gaaaaaagag gtagggcg                                                     18


<210>  7
<211>  17
<212>  DNA
<213>  Homo sapiens

<400>  7
cttacaggaa ctccagg                                                      17


<210>  8
<211>  20
<212>  DNA
<213>  Homo sapiens

<400>  8
cagcaatcct caaaaacaga                                                   20


<210>  9
<211>  55
<212>  DNA
<213>  Homo sapiens

<400>  9
cgccctacct cttttttctc tgtttttgag gattgctgcc tggagttcct gtaag            55


<210>  10
<211>  211
<212>  DNA
<213>  Homo sapiens

<400>  10
atcgccctac ctcttttttc tctgtttttg aggattgctg cctggagttc ctgtaagggc       60

aggggagata ccatgatcac gaaggtggtt ttcccagggc gaggcttatc cattgcactc      120

cggatgtgct gacccctgcg atttccccaa atgtgggaaa ctcgactgca taatttgtgg      180

tagtggggga ctgcgttcgc gctttcccct g                                     211


<210>  11
<211>  9
<212>  DNA
<213>  Homo sapiens

<400>  11
gaggtaggg                                                                9


<210>  12
<211>  8
<212>  DNA
<213>  Homo sapiens

<400>  12
caggaact                                                                 8


<210>  13
<211>  20
<212>  DNA
<213>  Homo sapiens

<400>  13
ccaggatggc attgggcagc                                                   20


<210>  14
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  14
cagcaatcct caaaaacaga tgc                                               23


<210>  15
<211>  60
<212>  DNA
<213>  Homo sapiens

<400>  15
ccctacctcg catctgtttt tgaggattgc tggctgccca atgccatcct ggagttcctg       60


<210>  16
<211>  216
<212>  DNA
<213>  Homo sapiens

<400>  16
atccctacct cgcatctgtt tttgaggatt gctggctgcc caatgccatc ctggagttcc       60

tgggcagggg agataccatg atcacgaagg tggttttccc agggcgaggc ttatccattg      120

cactccggat gtgctgaccc ctgcgatttc cccaaatgtg ggaaactcga ctgcataatt      180

tgtggtagtg ggggactgcg ttcgcgcttt cccctg                                216


<210>  17
<211>  28
<212>  DNA
<213>  Homo sapiens

<400>  17
cccaaaatat tttagctcct actcagac                                          28


<210>  18
<211>  24
<212>  DNA
<213>  Homo sapiens

<400>  18
atcaagcaga aggtatgaga aaaa                                              24


<210>  19
<211>  20
<212>  DNA
<213>  Homo sapiens

<400>  19
agaaatgcca tcttccttga                                                   20


<210>  20
<211>  30
<212>  DNA
<213>  Homo sapiens

<400>  20
ctagaaatgc catcttcctt gatgttggag                                        30


<210>  21
<211>  23
<212>  DNA
<213>  Homo sapiens

<400>  21
atcaagttat aaaatcacag agg                                               23


<210>  22
<211>  30
<212>  DNA
<213>  Homo sapiens

<400>  22
gcctttttgg tatcttacag gaactccagg                                        30


<210>  23
<211>  24
<212>  DNA
<213>  Homo sapiens

<400>  23
cagaaaaaag aggtagggcg acag                                              24


<210>  24
<211>  8
<212>  DNA
<213>  Homo sapiens

<400>  24
caggaact                                                                 8


<210>  25
<211>  17
<212>  DNA
<213>  Homo sapiens

<400>  25
ccaggatggc attgggc                                                      17


<210>  26
<211>  20
<212>  DNA
<213>  Homo sapiens

<400>  26
tcctcaaaaa cagatgccag                                                   20


<210>  27
<211>  13
<212>  DNA
<213>  Homo sapiens

<400>  27
aagaggtagg gcg                                                          13


<210>  28
<211>  9
<212>  DNA
<213>  Homo sapiens

<400>  28
acaggaact                                                                9


<210>  29
<211>  15
<212>  DNA
<213>  Homo sapiens

<400>  29
ccaggatggc attgg                                                        15


<210>  30
<211>  18
<212>  DNA
<213>  Homo sapiens

<400>  30
gcaatcctca aaaacaga                                                     18


<210>  31
<211>  16
<212>  DNA
<213>  Homo sapiens

<400>  31
gaaaaaagag gtaggg                                                       16


<210>  32
<211>  12
<212>  DNA
<213>  Homo sapiens

<400>  32
cttacaggaa ct                                                           12


<210>  33
<211>  25
<212>  DNA
<213>  Homo sapiens

<400>  33
gcctttttgg tatcttacag gaact                                             25


<210>  34
<211>  40
<212>  DNA
<213>  Homo sapiens

<400>  34
agaaatgcca tcttccttga atgagatctt gggcctctgc                             40


<210>  35
<211>  21
<212>  DNA
<213>  Homo sapiens

<400>  35
ggcaggggag ataccatgat c                                                 21


<210>  36
<211>  36
<212>  DNA
<213>  Homo sapiens

<400>  36
agatggcatt tctagggcag gggagatacc atgatc                                 36


<210>  37
<211>  35
<212>  DNA
<213>  Homo sapiens

<400>  37
tccttgatgt tggagatgag atcttgggcc tctgc                                  35


<210>  38
<211>  41
<212>  DNA
<213>  Homo sapiens

<400>  38
tcaaggaaga tggcatttct ggcaggggag ataccatgat c                           41


<210>  39
<211>  43
<212>  DNA
<213>  Homo sapiens

<400>  39
atcaagttat aaaatcacag aggatgagat cttgggcctc tgc                         43


<210>  40
<211>  49
<212>  DNA
<213>  Homo sapiens

<400>  40
gtctgagtag gagctaaaat attttggggg caggggagat accatgatc                   49


<210>  41
<211>  40
<212>  DNA
<213>  Homo sapiens

<400>  41
agaaatgcca tcttccttga atgagatctt gggcctctgc                             40


<210>  42
<211>  44
<212>  DNA
<213>  Homo sapiens

<400>  42
cctctgtgat tttataactt gatggcaggg gagataccat gatc                        44


<210>  43
<211>  44
<212>  DNA
<213>  Homo sapiens

<400>  43
atcaagcaga aggtatgaga aaaaatgaga tcttgggcct ctgc                        44


<210>  44
<211>  49
<212>  DNA
<213>  Homo sapiens

<400>  44
tcaaggaaga tgggtctgag taggagctgg caggggagat accatgatc                   49


<210>  45
<211>  48
<212>  DNA
<213>  Homo sapiens

<400>  45
tgttggagca tcaagcagaa ggtatgagat gagatcttgg gcctctgc                    48


<210>  46
<211>  21
<212>  DNA
<213>  Homo sapiens

<400>  46
gctagaagaa caaaagaata t                                                 21


<210>  47
<211>  20
<212>  DNA
<213>  Homo sapiens

<400>  47
ctacaacaaa gctcaggtcg                                                   20


<210>  48
<211>  22
<212>  DNA
<213>  Homo sapiens

<400>  48
cttttatgaa tgcttctcca ag                                                22


<210>  49
<211>  20
<212>  DNA
<213>  Homo sapiens

<400>  49
ttactggtgg aagagttgcc                                                   20


<210>  50
<211>  26
<212>  DNA
<213>  Homo sapiens

<400>  50
ttcgatccgt aatgattgtt ctagcc                                            26


<210>  51
<211>  28
<212>  DNA
<213>  Homo sapiens

<400>  51
caggggaaag cgcgaacgca gtccccca                                          28


<210>  52
<211>  38
<212>  DNA
<213>  Homo sapiens

<400>  52
aaggaaaaaa gcggccgcat gagaatgagc aaaatcgt                               38


<210>  53
<211>  30
<212>  DNA
<213>  Homo sapiens

<400>  53
ccttaattaa gagacaacta ttcttgtaag                                        30


<210>  54
<211>  45
<212>  DNA
<213>  Homo sapiens

<400>  54
cagaaaaaag aggtagggcg acagggcagg ggagatacca tgatc                       45


<210>  55
<211>  50
<212>  DNA
<213>  Homo sapiens

<400>  55
cctggagttc ctgtaagata ccaaaaaggc atgagatctt gggcctctgc                  50


<210>  56
<211>  46
<212>  DNA
<213>  Homo sapiens

<400>  56
gcccaatgcc atcctggagt tcctgggcag gggagatacc atgatc                      46


<210>  57
<211>  53
<212>  DNA
<213>  Homo sapiens

<400>  57
tcctcaaaaa cagatgccag aagaggtagg gcgatgagat cttgggcctc tgc              53


<210>  58
<211>  49
<212>  DNA
<213>  Homo sapiens

<400>  58
gctgcccaat gccatcctgg agttcctggg caggggagat accatgatc                   49


<210>  59
<211>  52
<212>  DNA
<213>  Homo sapiens

<400>  59
cagcaatcct caaaaacaga tgcgaggtag ggatgagatc ttgggcctct gc               52


<210>  60
<211>  49
<212>  DNA
<213>  Homo sapiens

<400>  60
gaggattgct gcctggagtt cctgtaaggg caggggagat accatgatc                   49


<210>  61
<211>  47
<212>  DNA
<213>  Homo sapiens

<400>  61
aaaaacagag aaaaaagagg tagggcgatg agatcttggg cctctgc                     47


<210>  62
<211>  50
<212>  DNA
<213>  Homo sapiens

<400>  62
attgcccaat gccatcctgg agttcctgtg gcaggggaga taccatgatc                  50


<210>  63
<211>  49
<212>  DNA
<213>  Homo sapiens

<400>  63
cctcaaaaac agagaaaaaa gaggtaggga tgagatcttg ggcctctgc                   49


<210>  64
<211>  53
<212>  DNA
<213>  Homo sapiens

<400>  64
gctgcccaat gccatcctgg agttcctgta agggcagggg agataccatg atc              53


<210>  65
<211>  43
<212>  DNA
<213>  Homo sapiens

<400>  65
cagcaatcct caaaaacaga tgcatgagat cttgggcctc tgc                         43


<210>  66
<211>  44
<212>  DNA
<213>  Homo sapiens

<400>  66
cagaaaaaag aggtagggcg acagatgaga tcttgggcct ctgc                        44


<210>  67
<211>  51
<212>  DNA
<213>  Homo sapiens

<400>  67
cctggagttc ctgtaagata ccaaaaaggc ggcaggggag ataccatgat c                51


<210>  68
<211>  35
<212>  DNA
<213>  Homo sapiens

<400>  68
atggcattgg gcagcatgag atcttgggcc tctgc                                  35


<210>  69
<211>  24
<212>  DNA
<213>  Homo sapiens

<400>  69
gaagacatgc ctttggaaat ttct                                              24


<210>  70
<211>  21
<212>  DNA
<213>  Homo sapiens

<400>  70
ctgaacgtca aatggtcctt c                                                 21


<210>  71
<211>  21
<212>  DNA
<213>  Homo sapiens

<400>  71
ctcttttcca ggttcaagtg g                                                 21


<210>  72
<211>  13
<212>  DNA
<213>  Homo sapiens

<400>  72
caggaactcc agg                                                          13


<210>  73
<211>  342
<212>  DNA
<213>  Homo sapiens

<400>  73
gtttctaatt tttctttttc ttcttttttc ctttttgcaa aaacccaaaa tattttagct       60

cctactcaga ctgttactct ggtgacacaa cctgtggtta ctaaggaaac tgccatctcc      120

aaactagaaa tgccatcttc cttgatgttg gaggtacctg ctctggcaga tttcaaccgg      180

gcttggacag aacttaccga ctggctttct ctgcttgatc aagttataaa atcacagagg      240

gtgatggtgg gtgaccttga ggatatcaac gagatgatca tcaagcagaa ggtatgagaa      300

aaaatgataa aagttggcag aagtttttct ttaaaatgaa ga                         342


<210>  74
<211>  376
<212>  DNA
<213>  Homo sapiens

<400>  74
tttgccagta caactgcatg tggtagcaca ctgtttaatc ttttctcaaa taaaaagaca       60

tggggcttca tttttgtttt gcctttttgg tatcttacag gaactccagg atggcattgg      120

gcagcggcaa actgttgtca gaacattgaa tgcaactggg gaagaaataa ttcagcaatc      180

ctcaaaaaca gatgccagta ttctacagga aaaattggga agcctgaatc tgcggtggca      240

ggaggtctgc aaacagctgt cagacagaaa aaagaggtag ggcgacagat ctaataggaa      300

tgaaaacatt ttagcagact ttttaagctt tctttagaag aatatttcat gagagattat      360

aagcagggtg aaaggc                                                      376


