                         SEQUENCE LISTING

<110>  ASSOCIATION INSTITUT DE MYOLOGIE
 
<120>  NEW MODIFIED U7 SNRNAS FOR TREATMENT OF NEUROMUSCULAR DISEASES

<130>  D26819

<150>  US 61/314,830
<151>  2010-03-17

<160>  42    

<170>  PatentIn version 3.3

<210>  1
<211>  32
<212>  RNA
<213>  homo sapiens


<220>
<221>  misc_feature
<223>  huU7 snRNA stem/loop

<400>  1
uaggcuuucu ggcuuuuuac cggaaagccc cu                                   32


<210>  2
<211>  11
<212>  RNA
<213>  homo sapiens


<220>
<221>  misc_feature
<223>  smOPT

<400>  2
aauuuuugga g                                                          11


<210>  3
<211>  363
<212>  DNA
<213>  homo sapiens


<220>
<221>  misc_feature
<223>  huU7 promoter

<400>  3
gggcattagg ctccatcgct catcaataga caaggccttt aggaaactgc gacaacggct     60

tttgctctgg gcctttactg ccgaatccag gtctccgggc ttaacaacaa cgaaggggct    120

gtgactggct gctttctcaa ccaatcagca ccgaactcat ttgcatgggc tgagaacaaa    180

tgttcgcgaa ctctagaaat gaatgactta agtaagttcc ttagaatatt atttttccta    240

ctgaaagtta ccacatgcgt cgttgtttat acagtaatag gaacaagaaa aaagtcacct    300

aagctcaccc tcatcaattg tggagttcct ttatatccca tcttctctcc aaacacatac    360

gca                                                                  363


<210>  4
<211>  233
<212>  DNA
<213>  homo sapiens


<220>
<221>  misc_feature
<223>  huU7 downstream elements

<400>  4
cttatgatgt ttgttgccaa tgatagattg ttttcactgt gcaaaaatta tgggtagttt     60

tggtggtctt gatgcagttg taagcttggg gtatgaaggt ttgggccacg cctgggcgct    120

tccggctgcg ccggatgctg tttcctttcc gctcccaggg gcgttgggaa cggttgtagg    180

acgtggctct ttattcgtga gttttccatt tacctccgct gaacctagag ctt           233


<210>  5
<211>  26
<212>  DNA
<213>  artificial

<220>
<223>  GAPDH-F oligo

<400>  5
tgaaggtcgg agtcaacgga tttggt                                          26


<210>  6
<211>  25
<212>  DNA
<213>  artificial

<220>
<223>  GAPDH-R oligo

<400>  6
gatgacaagc ttcccgttct cagcc                                           25


<210>  7
<211>  17
<212>  DNA
<213>  artificial

<220>
<223>  U6snRNA-F oligo

<400>  7
ctcgcttcgg cagcaca                                                    17


<210>  8
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  U6snRNA-R oligo

<400>  8
aacgcttcac gaatttgcgt                                                 20


<210>  9
<211>  25
<212>  DNA
<213>  artificial

<220>
<223>  DMPK exon 9-exon 10-F oligo

<400>  9
cactgtcgga cattcgggaa ggtgc                                           25


<210>  10
<211>  26
<212>  DNA
<213>  artificial

<220>
<223>  DMPK exon 9-exon 10-R oligo

<400>  10
gcttgcacgt gtggctcaag cagctg                                          26


<210>  11
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  DMPK intron 9-intron 10-F oligo

<400>  11
ctacccacag gccagaagtt                                                 20


<210>  12
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  DMPK intron 9-intron 10-R oligo

<400>  12
ggaagccctc accttttctc                                                 20


<210>  13
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  DMPK splice junction exon 14/16-exon 16-F oligo

<400>  13
ctgctccctg ccagggctga                                                 20


<210>  14
<211>  22
<212>  DNA
<213>  artificial

<220>
<223>  DMPK splice junction exon 14/16-exon 16-R oligo

<400>  14
tgtcggggtc tcagtgcatc ca                                              22


<210>  15
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  CPA6-F oligo

<400>  15
actgatgtcc atatccccca                                                 20


<210>  16
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  CPA6-R oligo

<400>  16
tttgagtcgt gatcgtctgc                                                 20


<210>  17
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  LTBP3-F oligo

<400>  17
gagaagagcc tgtgtttccg                                                 20


<210>  18
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  LTBP3-R oligo

<400>  18
gaaaagtcac tctcgccctg                                                 20


<210>  19
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  LRP8-F oligo

<400>  19
ctccactgac ttcctgagcc                                                 20


<210>  20
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  LRP8-R oligo

<400>  20
gtgctcggta gcacctcttc                                                 20


<210>  21
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  TMCC1-F oligo

<400>  21
gagcaaaggt gactggcttc                                                 20


<210>  22
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  TMCC1-R oligo

<400>  22
cgctcctcct gtaaggtctg                                                 20


<210>  23
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  CASK-F oligo

<400>  23
cagagttcgg ctggtacagt                                                 20


<210>  24
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  CASK-R oligo

<400>  24
acaggacgaa gactgagtgc                                                 20


<210>  25
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  MAP3K4-F oligo

<400>  25
aagggcacgt atagcattgg                                                 20


<210>  26
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  MAP3K4-R oligo

<400>  26
tggttctcca gcaggtctct                                                 20


<210>  27
<211>  21
<212>  DNA
<213>  artificial

<220>
<223>  BIN1-exon 11-F oligo

<400>  27
agaacctcaa tgatgtgctg g                                               21


<210>  28
<211>  22
<212>  DNA
<213>  artificial

<220>
<223>  BIN1-exon 11-R oligo

<400>  28
tcgtggttga ctctgatctc gg                                              22


<210>  29
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  DMD-exon 78-F oligo

<400>  29
ttagaggagg tgatggagca                                                 20


<210>  30
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  DMD-exon 78-R oligo

<400>  30
gatactaagg actccatcgc                                                 20


<210>  31
<211>  23
<212>  DNA
<213>  artificial

<220>
<223>  LDB3-exon 7-F oligo

<400>  31
gcaagaccct gatgaagaag ctc                                             23


<210>  32
<211>  19
<212>  DNA
<213>  artificial

<220>
<223>  LDB3-exon 7-R oligo

<400>  32
gacagaaggc cggatgctg                                                  19


<210>  33
<211>  22
<212>  DNA
<213>  artificial

<220>
<223>  Ex20ext oligo

<400>  33
cagaattctg ccaattgctg ag                                              22


<210>  34
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  Ex26ext oligo

<400>  34
ttcttcagct tgtgtcatcc                                                 20


<210>  35
<211>  24
<212>  DNA
<213>  artificial

<220>
<223>  Ex20int oligo

<400>  35
cccagtctac caccctatca gagc                                            24


<210>  36
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  Ex26int oligo

<400>  36
cctgccttta aggcttcctt                                                 20


<210>  37
<211>  24
<212>  DNA
<213>  artificial

<220>
<223>  BP22 oligo

<400>  37
aaatagaagt tcatttacac taac                                            24


<210>  38
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  SD23 oligo

<400>  38
ggccaaacct cggcttacct                                                 20


<210>  39
<211>  20
<212>  DNA
<213>  artificial

<220>
<223>  SD23 modif oligo

<400>  39
ggcgaaacct cggcttacct                                                 20


<210>  40
<211>  39
<212>  DNA
<213>  artificial

<220>
<223>  Smopt-loop oligo

<400>  40
aatttttgga gcaggttttc tgacttgggt cggaaaacc                            39


<210>  41
<211>  38
<212>  DNA
<213>  artificial

<220>
<223>  Smopt-loop modif oligo

<400>  41
aatttttgga gcaggttttc tgacggcgtc ggaaaacc                             38


<210>  42
<211>  38
<212>  DNA
<213>  artificial

<220>
<223>  Smopt-loop modif2 oligo

<400>  42
aatttttgga gcaggttttc tgcaggcgtc ggaaaacc                             38


